Harmatz, Paul

Efficacy of sapropterin dihydrochloride in increasing phenylalanine tolerance in children with phenylketonuria: a phase III, randomized, double-blind, placebo-controlled study

Trefz, F. K., Burton, B. K., Longo, N., Casanova, M. M.-P., Gruskin, D. J., Dorenbaum, A., Kakkis, E. D., Crombez, E. A., Grange, D. K., Harmatz, P., et al. (2009) · The Journal of Pediatrics

Metabolism and Genetic DisordersAmino Acid Enzymes and Metabolism

Cited by 196

Inflammation and oxidant-stress in -thalassemia patients treated with iron chelators deferasirox (ICL670) or deferoxamine: an ancillary study of the Novartis CICL670A0107 trial

Walter, P. B., Macklin, E. A., Porter, J., Evans, P., Kwiatkowski, J. L., Neufeld, E. J., Coates, T., Giardina, P. J., Vichinsky, E., Olivieri, N., et al. (2008) · Haematologica

Hemoglobinopathies and Related DisordersIron Metabolism and Disorders

Cited by 87

Iron chelation therapy in thalassemia major: A systematic review with meta-analyses of 1520 patients included on randomized clinical trials

Maggio, A., Filosa, A., Vitrano, A., Aloj, G., Kattamis, A., Ceci, A., Fucharoen, S., Cianciulli, P., Grady, R. W., Prossomariti, L., et al. (2011) · Blood Cells, Molecules, and Diseases

Hemoglobinopathies and Related DisordersIron Metabolism and Disorders

Cited by 65

Caregiving time in sickle cell disease: psychological effects in maternal caregivers

Moskowitz, J. T., Butensky, E., Harmatz, P., Vichinsky, E., Heyman, M. B., Acree, M., Wrubel, J., Wilson, L., & Folkman, S. (2007) · Pediatric Blood & Cancer

Hemoglobinopathies and Related DisordersFamily and Disability Support Research

Cited by 62

ALTERED IRON METABOLISM IN CHILDREN WITH HUMAN IMMUNODEFICIENCY VIRUS DISEASE

James, E. B., Harmatz, P., Lee, M., Kennedy, C., Petru, A., Wara, D., & Miaskowski, C. (2009) · Pediatric Hematology and Oncology

Iron Metabolism and DisordersHIV Research and Treatment

Cited by 17