Snyder, Richard O.

Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors

Snyder, R. O., Miao, C., Meuse, L., Tubb, J., Donahue, B. A., Lin, H.-F., Stafford, D. W., Patel, S., Thompson, A. R., Nichols, T., et al. (1999) · Nature Medicine

Hemophilia Treatment and ResearchVirus-based gene therapy research

Cited by 409

Epitope Mapping of Human Anti-Adeno-Associated Virus Type 2 Neutralizing Antibodies: Implications for Gene Therapy and Virus Structure

Moskalenko, M., Chen, L., van Roey, M., Donahue, B. A., Snyder, R. O., McArthur, J. G., & Patel, S. D. (2000) · Journal of Virology

Virus-based gene therapy researchRNA Interference and Gene Delivery

Cited by 253

Gene Therapy for Aromatic l -Amino Acid Decarboxylase Deficiency

Hwu, W.-L., Muramatsu, S.-I., Tseng, S.-H., Tzen, K.-Y., Lee, N.-C., Chien, Y.-H., Snyder, R. O., Byrne, B. J., Tai, C.-H., & Wu, R.-M. (2012) · Science Translational Medicine

Virus-based gene therapy researchLysosomal Storage Disorders Research

Cited by 246

Characterization of a recombinant adeno-associated virus type 2 Reference Standard Material

Lock, M., McGorray, S., Auricchio, A., Ayuso, E., Beecham, E. J., Blouin-Tavel, V., Bosch, F., Bose, M., Byrne, B. J., Caton, T., et al. (2010) · Human Gene Therapy

Virus-based gene therapy researchViral Infectious Diseases and Gene Expression in Insects

Cited by 131

Viral Gene Delivery Selectively Restores Feeding and Prevents Lethality of Dopamine-Deficient Mice

Szczypka, M. S., Mandel, R. J., Donahue, B. A., Snyder, R. O., Leff, S. E., & Palmiter, R. D. (1999) · Neuron

Virus-based gene therapy researchParkinson's Disease Mechanisms and Treatments

Cited by 129

Manufacturing and characterization of a recombinant adeno-associated virus type 8 reference standard material

Ayuso, E., Blouin, V., Lock, M., McGorray, S., Leon, X., Alvira, M. R., Auricchio, A., Bucher, S., Chtarto, A., Clark, K. R., et al. (2014) · Human Gene Therapy

Virus-based gene therapy researchViral Infectious Diseases and Gene Expression in Insects

Cited by 94

Practical utilization of recombinant AAV vector reference standards: focus on vector genomes titration by free ITR qPCR

D'Costa, S., Blouin, V., Broucque, F., Penaud-Budloo, M., Fçranois, A., Perez, I. C., Le Bec, C., Moullier, P., Snyder, R. O., & Ayuso, E. (2016) · Molecular Therapy - Methods & Clinical Development

Virus-based gene therapy researchRNA Interference and Gene Delivery

Cited by 89

Manufacturing Clinical Grade Recombinant Adeno-Associated Virus Using Invertebrate Cell Lines

Kotin, R. M., & Snyder, R. O. (2017) · Human Gene Therapy

Virus-based gene therapy researchViral Infectious Diseases and Gene Expression in Insects

Cited by 59

Immune Responses to Gene Product of Inducible Promoters

Guiner, C., Stieger, K., Snyder, R., Rolling, F., & Moullier, P. (2007) · Current Gene Therapy

Virus-based gene therapy researchRNA Interference and Gene Delivery

Cited by 46

Stability of the adeno-associated virus 8 reference standard material

Penaud-Budloo, M., Broucque, F., Harrouet, K., Bouzelha, M., Saleun, S., Douthe, S., D’Costa, S., Ogram, S., Adjali, O., Blouin, V., et al. (2019) · Gene Therapy

Virus-based gene therapy researchRNA Interference and Gene Delivery

Cited by 14