Ciuculescu, Marioara F.
Boston Children's Hospital
2 papers on CoChat
Most cited papers
- Verified
Post-Transcriptional Genetic Silencing of BCL11A to Treat Sickle Cell Disease
Esrick, E. B., Lehmann, L. E., Biffi, A., Achebe, M., Brendel, C., Ciuculescu, M. F., Daley, H., MacKinnon, B., Morris, E., Federico, A., et al. (2021) · New England Journal of Medicine
Hemoglobinopathies and Related DisordersVirus-based gene therapy research
Cited by 449
- Verified
Clonal selection of hematopoietic stem cells after gene therapy for sickle cell disease
Spencer Chapman, M., Cull, A. H., Ciuculescu, M. F., Esrick, E. B., Mitchell, E., Jung, H., O’Neill, L., Roberts, K., Fabre, M. A., Williams, N., et al. (2023) · Nature Medicine
Virus-based gene therapy researchHematopoietic Stem Cell Transplantation
Cited by 67
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