Falk, Darin J.

Pompe disease gene therapy

Byrne, B. J., Falk, D. J., Pacak, C. A., Nayak, S., Herzog, R. W., Elder, M. E., Collins, S. W., Conlon, T. J., Clement, N., Cleaver, B. D., et al. (2011) · Human Molecular Genetics

Lysosomal Storage Disorders ResearchGlycogen Storage Diseases and Myoclonus

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Pompe disease gene therapy: neural manifestations require consideration of CNS directed therapy

Byrne, B. J., Fuller, D. D., Smith, B. K., Clement, N., Coleman, K., Cleaver, B., Vaught, L., Falk, D. J., McCall, A., & Corti, M. (2019) · Annals of Translational Medicine

Lysosomal Storage Disorders ResearchGlycogen Storage Diseases and Myoclonus

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Correcting Neuromuscular Deficits With Gene Therapy in Pompe Disease

Todd, A. G., McElroy, J. A., Grange, R. W., Fuller, D. D., Walter, G. A., Byrne, B. J., & Falk, D. J. (2015) · Annals of Neurology

Lysosomal Storage Disorders ResearchGlycogen Storage Diseases and Myoclonus

Cited by 51

Altered activation of the tibialis anterior in individuals with Pompe disease: Implications for motor unit dysfunction: Neuromuscular Activation in Pompe

Corti, M., Smith, B. K., Falk, D. J., Lawson, L. A., Fuller, D. D., Subramony, S. H., Byrne, B. J., & Christou, E. A. (2015) · Muscle & Nerve

Lysosomal Storage Disorders ResearchMuscle Physiology and Disorders

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