Weber, Michel

Recombinant adeno-associated virus serotype 4 mediates unique and exclusive long-term transduction of retinal pigmented epithelium in rat, dog, and nonhuman primate after subretinal delivery

Weber, M., Rabinowitz, J., Provost, N., Conrath, H., Folliot, S., Briot, D., Chérel, Y., Chenuaud, P., Samulski, J., Moullier, P., et al. (2003) · Molecular Therapy

Virus-based gene therapy researchRetinal Development and Disorders

Cited by 203

Safety and long-term efficacy of AAV4 gene therapy in patients with RPE65 leber congenital amaurosis

Le Meur, G., Lebranchu, P., Billaud, F., Adjali, O., Schmitt, S., Bézieau, S., Péréon, Y., Valabregue, R., Ivan, C., Darmon, C., et al. (2018) · Molecular Therapy

Retinal Development and DisordersVirus-based gene therapy research

Cited by 137

Long-term doxycycline-regulated transgene expression in the retina of nonhuman primates following subretinal injection of recombinant AAV vectors

Stieger, K., Le Meur, G., Lasne, F., Weber, M., Deschamps, J.-Y., Nivard, D., Mendes-Madeira, A., Provost, N., Martin, L., Moullier, P., et al. (2006) · Molecular Therapy

Virus-based gene therapy researchRetinal Development and Disorders

Cited by 110

Detection of intact rAAV particles up to 6 years after successful gene transfer in the retina of dogs and primates

Stieger, K., Schroeder, J., Provost, N., Mendes-Madeira, A., Belbellaa, B., Meur, G. L., Weber, M., Deschamps, J.-Y., Lorenz, B., Moullier, P., et al. (2009) · Molecular Therapy

Virus-based gene therapy researchRetinal Development and Disorders

Cited by 88

Biodistribution of rAAV vectors following intraocular administration: Evidence for the presence and persistence of vector DNA in the optic nerve and in the brain

Provost, N., Le Meur, G., Weber, M., Mendes-Madeira, A., Podevin, G., Cherel, Y., Colle, M.-A., Deschamps, J.-Y., Moullier, P., & Rolling, F. (2005) · Molecular Therapy

Virus-based gene therapy researchRetinal Development and Disorders

Cited by 87

Six-month safety and efficacy of the intelligent retinal implant system II device in retinitis pigmentosa

Muqit, M. M. K., Velikay-Parel, M., Weber, M., Dupeyron, G., Audemard, D., Corcostegui, B., Sahel, J., & Le Mer, Y. (2019) · Ophthalmology

Neuroscience and Neural EngineeringRetinal Development and Disorders

Cited by 46