Douar, Anne-Marie

Putative X-linked adrenoleukodystrophy gene shares unexpected homology with ABC transporters

Mosser, J., Douar, A.-M., Sarde, C.-O., Kioschis, P., Feil, R., Moser, H., Poustka, A.-M., Mandel, J.-L., & Aubourg, P. (1993) · Nature

Metabolism and Genetic DisordersHereditary Neurological Disorders

Cited by 1,202

Intravenous administration of self-complementary AAV9 enables transgene delivery to adult motor neurons

Duque, S., Joussemet, B., Riviere, C., Marais, T., Dubreil, L., Douar, A.-M., Fyfe, J., Moullier, P., Colle, M.-A., & Barkats, M. (2009) · Molecular Therapy

Virus-based gene therapy researchNeurogenetic and Muscular Disorders Research

Cited by 511

Intracellular trafficking of adeno-associated virus vectors: routing to the late endosomal compartment and proteasome degradation

Douar, A.-M., Poulard, K., Stockholm, D., & Danos, O. (2001) · Journal of Virology

Virus-based gene therapy researchCellular transport and secretion

Cited by 282

The gene responsible for adrenoleukodystrophy encodes a peroxisomal membrane protein

Mosser, J., Lutz, Y., Stoeckel, M. E., Sarde, C. O., Kretz, C., Douar, A. M., Lopez, J., Aubourg, P., & Mandel, J. L. (1994) · Human Molecular Genetics

Metabolism and Genetic DisordersHereditary Neurological Disorders

Cited by 281

Long-term expression and repeated administration of AAV type 1, 2 and 5 vectors in skeletal muscle of immunocompetent adult mice

Rivière, C., Danos, O., & Douar, A. M. (2006) · Gene Therapy

Virus-based gene therapy researchRNA Interference and Gene Delivery

Cited by 192

Characterization of a recombinant adeno-associated virus type 2 Reference Standard Material

Lock, M., McGorray, S., Auricchio, A., Ayuso, E., Beecham, E. J., Blouin-Tavel, V., Bosch, F., Bose, M., Byrne, B. J., Caton, T., et al. (2010) · Human Gene Therapy

Virus-based gene therapy researchViral Infectious Diseases and Gene Expression in Insects

Cited by 131

Abnormal messenger RNA expression and a missense mutation in patients with X-linked adrenoleukodystrophy

Cartier, N., Sarde, C.-O., Douar, A.-M., Mosser, J., Mandel, J.-L., & Aubourg, P. (1993) · Human Molecular Genetics

Metabolism and Genetic DisordersLysosomal Storage Disorders Research

Cited by 55

Deleterious effect of peptide insertions in a permissive site of the AAV2 capsid

Douar, A. M., Poulard, K., & Danos, O. (2003) · Virology

Virus-based gene therapy researchRNA Interference and Gene Delivery

Cited by 17

268. Optogenetic Engineering of Retinal Ganglion Cells with AAV2.7m8-ChrimsonR-tdTomato (GS030-DP) Is Well Tolerated and Induces Functional Responses to Light in Non-Human Primates

Douar, A. M., Bouquet, C., Pruneau, D., Chavas, J., Dalkara, D., Duebel, J., Benosman, R., Chenegros, G., Picaud, S., Sahel, J., et al. (2016) · Molecular Therapy

Retinal Development and DisordersPhotoreceptor and optogenetics research

Cited by 11