Mahlaoui, Nizar

Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy

Cartier, N., Hacein-Bey-Abina, S., Bartholomae, C. C., Veres, G., Schmidt, M., Kutschera, I., Vidaud, M., Abel, U., Dal-Cortivo, L., Caccavelli, L., et al. (2009) · Science

Virus-based gene therapy researchLysosomal Storage Disorders Research

Cited by 1,508

The European society for immunodeficiencies (ESID) registry working definitions for the clinical diagnosis of inborn errors of immunity

Seidel, M. G., Kindle, G., Gathmann, B., Quinti, I., Buckland, M., van Montfrans, J., Scheible, R., Rusch, S., Gasteiger, L. M., Grimbacher, B., et al. (2019) · The Journal of Allergy and Clinical Immunology In Practice

Immunodeficiency and Autoimmune DisordersBlood disorders and treatments

Cited by 647

Evaluating Continuity During Transfer to Adult Care: A Systematic Review

Rachas, A., Lefeuvre, D., Meyer, L., Faye, A., Mahlaoui, N., de La Rochebrochard, E., Warszawski, J., & Durieux, P. (2016) · Pediatrics

Adolescent and Pediatric HealthcareHospital Admissions and Outcomes

Cited by 38

Excess mortality and hospitalizations in transitional-age youths with a long-term disease: a national population-based cohort study

Rachas, A., Tuppin, P., Meyer, L., Falissard, B., Faye, A., Mahlaoui, N., de La Rochebrochard, E., Frank, M., Durieux, P., & Warszawski, J. (2018) · PLoS ONE

Adolescent and Pediatric HealthcareHealth and Medical Studies

Cited by 28