Long, Chengzu

Prevention of muscular dystrophy in mice by CRISPR/Cas9–mediated editing of germline DNA

Long, C., McAnally, J. R., Shelton, J. M., Mireault, A. A., Bassel-Duby, R., & Olson, E. N. (2014) · Science

CRISPR and Genetic EngineeringMuscle Physiology and Disorders

Cited by 720

Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy

Amoasii, L., Long, C., Li, H., Mireault, A. A., Shelton, J. M., Sanchez-Ortiz, E., McAnally, J. R., Bhattacharyya, S., Schmidt, F., Grimm, D., et al. (2017) · Science Translational Medicine

CRISPR and Genetic EngineeringMuscle Physiology and Disorders

Cited by 247

KLHL40 deficiency destabilizes thin filament proteins and promotes nemaline myopathy

Garg, A., O’Rourke, J., Long, C., Doering, J., Ravenscroft, G., Bezprozvannaya, S., Nelson, B. R., Beetz, N., Li, L., Chen, S., et al. (2014) · Journal of Clinical Investigation

Muscle Physiology and DisordersCardiomyopathy and Myosin Studies

Cited by 127