Hollis, Roger P.

Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells

Hoban, M. D., Cost, G. J., Mendel, M. C., Romero, Z., Kaufman, M. L., Joglekar, A. V., Ho, M., Lumaquin, D., Gray, D., Lill, G. R., et al. (2015) · Blood

Hemoglobinopathies and Related DisordersCRISPR and Genetic Engineering

Cited by 320

CRISPR/Cas9-Mediated Correction of the Sickle Mutation in Human CD34+ cells

Hoban, M. D., Lumaquin, D., Kuo, C. Y., Romero, Z., Long, J., Ho, M., Young, C. S., Mojadidi, M., Fitz-Gibbon, S., Cooper, A. R., et al. (2016) · Molecular Therapy

CRISPR and Genetic EngineeringHemoglobinopathies and Related Disorders

Cited by 220

Transient Gene Expression by Nonintegrating Lentiviral Vectors

Nightingale, S. J., Hollis, R. P., Pepper, K. A., Petersen, D., Yu, X.-J., Yang, C., Bahner, I., & Kohn, D. B. (2006) · Molecular Therapy

Virus-based gene therapy researchRNA Interference and Gene Delivery

Cited by 192

Integrase-defective Lentiviral Vectors as a Delivery Platform for Targeted Modification of Adenosine Deaminase Locus

Joglekar, A. V., Hollis, R. P., Kuftinec, G., Senadheera, S., Chan, R., & Kohn, D. B. (2013) · Molecular Therapy

Virus-based gene therapy researchCRISPR and Genetic Engineering

Cited by 65

Zinc Finger Nucleases Targeting The β-Globin Locus Drive Efficient Correction Of The Sickle Mutation In CD34+ Cells

Hoban, M. D., Joglekar, A. V., Gray, D., Kaufman, M. L., Urbinati, F., Senadheera, S., Cost, G., Reik, A., Holmes, M. C., Gregory, P. D., et al. (2013) · Blood

Hemoglobinopathies and Related DisordersCRISPR and Genetic Engineering

Cited by 2