Park, Ji-Sun

Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia

An, D., Schneller, J. L., Frassetto, A., Liang, S., Zhu, X., Park, J.-S., Theisen, M., Hong, S.-J., Zhou, J., Rajendran, R., et al. (2017) · Cell Reports

RNA Interference and Gene DeliveryMetabolism and Genetic Disorders

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Systemic messenger RNA as an etiological treatment for acute intermittent porphyria

Jiang, L., Berraondo, P., Jericó, D., Guey, L. T., Sampedro, A., Frassetto, A., Benenato, K. E., Burke, K., Santamaría, E., Alegre, M., et al. (2018) · Nature Medicine

Porphyrin Metabolism and DisordersRNA Interference and Gene Delivery

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