Vettermann, Christian

AAV5–Factor VIII Gene Transfer in Severe Hemophilia A

Rangarajan, S., Walsh, L., Lester, W., Perry, D., Madan, B., Laffan, M., Yu, H., Vettermann, C., Pierce, G. F., Wong, W. Y., et al. (2017) · New England Journal of Medicine

Hemophilia Treatment and ResearchVirus-based gene therapy research

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Strategy to detect pre-existing immunity to AAV gene therapy

Falese, L., Sandza, K., Yates, B., Triffault, S., Gangar, S., Long, B., Tsuruda, L., Carter, B., Vettermann, C., Zoog, S. J., et al. (2017) · Gene Therapy

Virus-based gene therapy researchHemophilia Treatment and Research

Cited by 101

The impact of pre-existing immunity on the non-clinical pharmacodynamics of AAV5-based gene therapy

Long, B. R., Sandza, K., Holcomb, J., Crockett, L., Hayes, G. M., Arens, J., Fonck, C., Tsuruda, L. S., Schweighardt, B., O’Neill, C. A., et al. (2019) · Molecular Therapy - Methods & Clinical Development

Virus-based gene therapy researchHemophilia Treatment and Research

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Evaluation of the Humoral Response to Adeno-Associated Virus-Based Gene Therapy Modalities Using Total Antibody Assays

Gorovits, B., Azadeh, M., Buchlis, G., Harrison, T., Havert, M., Jawa, V., Long, B., McNally, J., Milton, M., Nelson, R., et al. (2021) · The AAPS Journal

Virus-based gene therapy researchRNA Interference and Gene Delivery

Cited by 53