Simon, Amy
University of Modena and Reggio Emilia · Karolinska University Hospital · Alnylam Pharmaceuticals (United States) · Karolinska Institutet · Hospital Clínic de Barcelona · Universitat de Barcelona · Icahn School of Medicine at Mount Sinai
3 papers on CoChat
Most cited papers
- Verified
A highly durable RNAi therapeutic inhibitor of PCSK9
Fitzgerald, K., White, S., Borodovsky, A., Bettencourt, B. R., Strahs, A., Clausen, V., Wijngaard, P., Horton, J. D., Taubel, J., Brooks, A., et al. (2017) · New England Journal of Medicine
Lipoproteins and Cardiovascular HealthRNA Interference and Gene Delivery
Cited by 768
- Verified
Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria
Balwani, M., Sardh, E., Ventura, P., Peiró, P. A., Rees, D. C., Stölzel, U., Bissell, D. M., Bonkovsky, H. L., Windyga, J., Anderson, K. E., et al. (2020) · New England Journal of Medicine
Porphyrin Metabolism and DisordersNeonatal Health and Biochemistry
Cited by 608
- Verified
Preclinical development of a subcutaneous ALAS1 RNAi therapeutic for treatment of hepatic porphyrias using circulating RNA quantification
Chan, A., Liebow, A., Yasuda, M., Gan, L., Racie, T., Maier, M., Kuchimanchi, S., Foster, D., Milstein, S., Charisse, K., et al. (2015) · Molecular Therapy — Nucleic Acids
Porphyrin Metabolism and DisordersRNA Interference and Gene Delivery
Cited by 128
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