Dendrimer‐Based Lipid Nanoparticles Deliver Therapeutic FAH mRNA to Normalize Liver Function and Extend Survival in a Mouse Model of Hepatorenal Tyrosinemia Type I

Cheng, Qiang, Wei, Tuo, Jia, Yuemeng, Farbiak, Lukas, Zhou, Kejin, Zhang, Shuyuan, Wei, Yonglong, Zhu, Hao +1 more·2018·Advanced Materials
DOI 10.1002/adma.201805308

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