Several log increase in therapeutic transgene delivery by distinct adeno-associated viral serotype vectors

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7. Enhancement of Muscle Gene Delivery with Pseudotyped Adeno-Associated Virus Type 5 Correlates with Myoblast Differentiation
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8. Differential Myocardial Gene Delivery by Recombinant Serotype-Specific Adeno-associated Viral Vectors
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23. Optimal Design of a Single Recombinant Adeno-associated Virus Derived from Serotypes 1 and 2 to Achieve More Tightly Regulated Transgene Expression from Nonhuman Primate Muscle
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33. Gene Therapy with Helper-Dependent Adenoviral Vectors: Current Advances and Future Perspectives
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34. Successful Gene Transfer Using Adeno-Associated Virus Vectors into the Kidney: Comparison among Adeno-Associated Virus Serotype 1–5 Vectors in vitro and in vivo
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36. Transient Immunomodulation Allows Repeated Injections of AAV1 and Correction of Muscular Dystrophy in Multiple Muscles
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44. Adeno-associated viral serotypes produce differing titers and differentially transduce neurons within the rat basal and lateral amygdala
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45. Designing Heart Performance by Gene Transfer
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48. Gene Transfer as an Approach to Treating Hemophilia
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52. Intravenous administration of an AAV-2 vector for the expression of factor IX in mice and a dog model of hemophilia B
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53. Intrathecal Long-Term Gene Expression by Self-Complementary Adeno-Associated Virus type 1 Suitable for Chronic Pain Studies in Rats
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54. Viral Vectors: A Wide Range of Choices and High Levels of Service
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55. Chimeric Adeno-Associated Virus/Antisense U1 Small Nuclear RNA Effectively Rescues Dystrophin Synthesis and Muscle Function by Local Treatment of mdx Mice
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