Reversion of FMR1 methylation and silencing by editing the triplet repeats in Fragile X iPSC-derived neurons

Park, Chul-Yong, Halevy, Tomer, Lee, Dongjin R., Sung, Jin Jea, Lee, Jae Souk, Yanuka, Ofra, Benvenisty, Nissim, Kim, Dong-Wook·2015·Cell Reports
DOI 10.1016/j.celrep.2015.08.084

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