Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia

An, Ding, Schneller, Jessica L., Frassetto, Andrea, Liang, Shi, Zhu, Xuling, Park, Ji-Sun, Theisen, Matt, Hong, Sue-Jean +16 more·2017·Cell Reports
DOI 10.1016/j.celrep.2017.11.081

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