Viral vectors for therapy of neurologic diseases

Choudhury, Sourav R., Hudry, Eloise, Maguire, Casey A., Sena-Esteves, Miguel, Breakefield, Xandra O., Grandi, Paola·2017·Neuropharmacology
DOI 10.1016/j.neuropharm.2016.02.013

Cites (234)

Items 201–234 of 234

  1. Intracerebroventricular Viral Injection of the Neonatal Mouse Brain for Persistent and Widespread Neuronal Transduction
    Ji‐Yoen Kim, Stacy D. Grunke, Yona Levites · 2014 · Journal of Visualized Experiments
  2. HLA-A*0201-restricted cytolytic responses to the rtTA transactivator dominant and cryptic epitopes compromise transgene expression induced by the tetracycline on system
    Ginhoux, F., Turbant, S., Gross, D.A., Poupiot, J., Marais, T., Lone, Y., Lemonnier, F.A., Firat, H., Perez, N., Danos, O. et al. · 2004 · Molecular Therapy
  3. Expression of β-galactosidase in mouse brain: utilization of a novel nonreplicative Sindbis virus vector as a neuronal gene delivery system
    Sanja Altman-Hamamdzic, Chad H. Groseclose, J-X Ma · 1997 · Gene Therapy
  4. Efficient central nervous system AAVrh10-mediated intrathecal gene transfer in adult and neonate rats
    Juliette Hordeaux, Laurence Dubreil, Johan Deniaud, Fabien Iacobelli, Stéphanie Moreau, Mireille Ledevin, Caroline Le Guiner, Véronique Blouin, Johanne Le Duff, Alexandra Mendes-Madeira et al. · 2015 · Gene Therapy
  5. Adeno-associated virus-mediated expression of β-hexosaminidase prevents neuronal loss in the Sandhoff mouse brain
    Timothy J. Sargeant, Susan Siyu Wang, Josephine M. Bradley, Nicolas J.C. Smith, Animesh Alexander Raha, Rosamund McNair, Robin J. Ziegler, Seng H. Cheng, Timothy Martin Cox, María Begoña Cachón-González · 2011 · Human Molecular Genetics
  6. Role of the Vector Genome and Underlying Factor IX Mutation in Immune Responses to AAV Gene Therapy for Hemophilia B
    Rogers, Geoffrey L, Martino, Ashley T, Zolotukhin, Irene, Ertl, Hildegund CJ, Herzog, Roland W · 2014 · Journal of Translational Medicine
  7. The RB tumor suppressor at the intersection of proliferation and immunity: relevance to disease immune evasion and immunotherapy
    Jack Hutcheson, Agnieszka Katarzyna Witkiewicz, Erik S. Knudsen · 2015 · Cell Cycle
  8. Efficacy of a Combined Intracerebral and Systemic Gene Delivery Approach for the Treatment of a Severe Lysosomal Storage Disorder
    Carmine Spampanato, Elvira De Leonibus, Paola Dama, Annagiusi Gargiulo, Alessandro Fraldi, Nicolina Cristina Sorrentino, Fabio Russo, Edoardo Nusco, Alberto Auricchio, Enrico Maria Surace et al. · 2011 · Molecular Therapy
  9. Enhanced neurotrophic distribution, cell signaling and neuroprotection following substantia nigral versus striatal delivery of AAV2-NRTN (CERE-120)
    Christopher D. Herzog, Lamar Brown, Brian R. Kruegel, Alistair Wilson, Malú G. Tansey, Fred H. Gage, Eugene M. Johnson, Raymond T. Bartus · 2013 · Neurobiology of Disease
  10. The Neurofibromatoses. Part 1: NF1.
    Christine Lu‐Emerson, Scott Randall Plotkin · 2009 · PubMed
  11. T-cell response to adenovirus hexon and DNA-binding protein in mice
    Troy W. McKelvey, A Tang, Andrew J. Bett · 2004 · Gene Therapy
  12. AAV2/1 CD74 Gene Transfer Reduces β-amyloidosis and Improves Learning and Memory in a Mouse Model of Alzheimer's Disease
    Tomomi Kiyota, Gang Zhang, Christine M. Morrison, Megan E. Bosch, Robert A. Weir, Yaman Lu, Weiguo Dong, Howard Eliot Gendelman · 2015 · Molecular Therapy
  13. Inhibiting AIDS in the central nervous system: gene delivery to protect neurons from HIV
    Pierre Cordelier, Elisabeth Van Bockstaele, Sandra A. Calarota · 2003 · Molecular Therapy
  14. Targeting BACE with small inhibitory nucleic acids - a future for Alzheimer's disease therapy?
    Barbara Nawrot · 2004 · Acta Biochimica Polonica
  15. Cytokine production in motor neurons by poliovirus replicon vector gene delivery
    Andrea Bledsoe, Cheryl A. Jackson, Sylvia A. McPherson, Casey D. Morrow · 2000 · Nature Biotechnology
  16. Targeted Integration of Functional Human ATM cDNA Into Genome Mediated by HSV/AAV Hybrid Amplicon Vector
    Cortés, Maria L, Oehmig, Angelika, Saydam, Okay, Sanford, Jocelyn D, Perry, Katherine F, Fraefel, Cornel, Breakefield, Xandra O · 2008 · Molecular Therapy
  17. Long-term correction of biochemical and neurological abnormalities in MLD mice model by neonatal systemic injection of an AAV serotype 9 vector
    Noriko Miyake, K Miyake, Nagisa Asakawa, M Yamamoto, Takashi Shimada · 2014 · Gene Therapy
  18. Mechanisms of distribution of mouse β-galactosidase in the adult GM1-gangliosidosis brain
    Marike L. D. Broekman, Laryssa A. Tierney, Caroline Benn, P Chawla, J H, Miguel Sena‐Esteves · 2008 · Gene Therapy
  19. FIRST-IN-HUMAN PHASE I CLINICAL TRIAL OF ONCOLYTIC DELTA-24-RGD (DNX-2401) WITH BIOLOGICAL ENDPOINTS: IMPLICATIONS FOR VIRO- IMMUNOTHERAPY
    F. Lang, C. Conrad, Candelaria Gomez‐Manzano et al. · 2014 · Neuro-Oncology
  20. Chemical Modulation of Endocytic Sorting Augments Adeno-associated Viral Transduction
    Garrett E. Berry, Aravind Asokan · 2015 · Journal of Biological Chemistry
  21. Neprilysin gene transfer: A promising therapeutic approach for A lzheimer's disease
    Yuanli Li, Junqing Wang, Shenghao Zhang, Zhaohui Liu · 2015 · Journal of Neuroscience Research
  22. Repetitive Intrathecal Injections of Poliovirus Replicons Result in Gene Expression in Neurons of the Central Nervous System Without Pathogenesis
    Cheryl A. Jackson, Charles Cobbs, Jean D. Peduzzi · 2001 · Human Gene Therapy
  23. An integration-defective lentivirus-based resource for site-specific targeting of an edited safe-harbour locus in the human genome
    Raúl Torres-Ruiz, Angie Fernanda Rodriguez Garcia, M Jimenez, S Rodriguez, Juan Carlos Ramı́rez · 2014 · Gene Therapy
  24. A Human Monoclonal IgG That Binds Aβ Assemblies and Diverse Amyloids Exhibits Anti-Amyloid ActivitiesIn VitroandIn Vivo
    Yona Levites, Brian O’Nuallain, Rama Devudu Puligedda, Tomáš Ondrejčák, Sharad P. Adekar, Cindy Si Chen, Pedro E. Cruz, Awilda M. Rosario, Sallie D. Macy, Alexandra J. Mably et al. · 2015 · Journal of Neuroscience
  25. AAV8 capsid variable regions at the two-fold symmetry axis contribute to high liver transduction by mediating nuclear entry and capsid uncoating
    Rebeca M Tenney, Christie L. Bell, James M. Wilson · 2014 · Virology
  26. Immune-mediated Loss of Transgene Expression From Virally Transduced Brain Cells Is Irreversible, Mediated by IFNγ, Perforin, and TNFα, and due to the Elimination of Transduced Cells
    Jeffrey M. Zirger, Mariana Puntel, Josee Bergeron et al. · 2012 · Molecular Therapy
  27. Stochastic Model of Tsc1 Lesions in Mouse Brain
    Shilpa Prabhakar, June Goto, Xuan Zuang, Miguel Sena‐Esteves, Roderick Terry Bronson, Jillian Brockmann, Davide Gianni, Gregory R. Wojtkiewicz, John W. Chen, Anat O Stemmer-Rachamimov et al. · 2013 · PLoS ONE
  28. Survival benefit and phenotypic improvement by hamartin gene therapy in a tuberous sclerosis mouse brain model
    Shilpa Prabhakar, Xuan Zhang, June Goto, Sangyeul Han, Charles Pin‐Kuang Lai, Roderick Terry Bronson, Miguel Sena‐Esteves, Vijaya Ramesh, Anat O Stemmer-Rachamimov, David J. Kwiatkowski et al. · 2015 · Neurobiology of Disease
  29. RNA-Based Vaccination: Sending a Strong Message
    David B. Weiner · 2013 · Molecular Therapy
  30. Lentivirus-Based Genetic Manipulations in Neurons In Vivo
    Tanjew Dittgen, Pawel Licznerski, Pavel Osten · 2006 · Frontiers in neuroscience
  31. (Re-)Engineering tumor cell-selective replicating adenoviruses: A step in the right direction toward systemic therapy for metastatic disease
    Thomas Walter Dubensky · 2002 · Cancer Cell
  32. Lentivirus-based genetic manipulations in neurons in vivo
    Osten, P., Dittgen, T., Licznerski, P. · 2006 · Max Planck Digital Library
  33. Clinical trials of viral therapy for malignant gliomas
    David Eric Piccioni, Santosh Kesari · 2013 · Expert Review of Anticancer Therapy
  34. Healing Genes in the Nervous System
    Xandra O. Breakefield, Miguel Sena‐Esteves · 2010 · Neuron