Adeno-associated virus integration: virus versus vector

Smith, R H·2008·Gene Therapy

Cited by (178)

Items 101–178 of 178

  1. A Changing World in Gene Therapy Research: Exciting Opportunities for Medical Advancement and Biosafety Challenges
    Daniel Eisenman, Shaun Debold, James Riddle · 2021 · Applied Biosafety
  2. Functional Intercellular Transmission of miHTT via Extracellular Vesicles: An In Vitro Proof-of-Mechanism Study
    Roberto D.V.S. Morais, Marina Sogorb-González, Citlali Bar, Nikki C Timmer, M. Leontien van der Bent, Morgane Wartel, Astrid Vallès · 2022 · Cells
  3. Streamlined, single-step non-viral CRISPR-Cas9 knockout strategy enhances gene editing efficiency in primary human chondrocyte populations
    Simone Ponta, Angela Bonato, Philipp Neidenbach, Valentino F. Bruhin, Alexis E. Laurent, Lee Ann Applegate, Marcy Zenobi‐Wong, Gonçalo Barreto · 2024 · Arthritis Research & Therapy
  4. Transduction of Human Adipose-Derived Mesenchymal Stem Cells by Recombinant Adeno-Associated Virus Vectors
    Michelle Locke, James E. Ussher, Raakhi M. Mistry, John A. Taylor, P. Rod Dunbar · 2011 · Tissue Engineering Part C Methods
  5. Foamy Virus Vectors Transduce Visceral Organs and Hippocampal Structures following In Vivo Delivery to Neonatal Mice
    John Robert Counsell, Rajvinder Karda, Juan F. Antinao Diaz, Louise Carey, Tatiana Wiktorowicz, Suzanne M. K. Buckley, Shima Ameri, Joanne Ng, Julien Baruteau, Filipa Almeida et al. · 2018 · Molecular Therapy — Nucleic Acids
  6. Gene therapy approval for Duchenne muscular dystrophy: a European perspective
    Hannah Jolly, Annemieke M Aartsma-Rus, Enrico Bertini, Liesbeth De Waele, Jana Haberlová, Andrea Klein, Erik Harmen Niks, Laurent Servais · 2025 · The Lancet
  7. Microhomology‐mediated repair machinery and its relationship with HPV‐mediated oncogenesis
    Subhajit Chatterjee, Gabriel J. Starrett · 2024 · Journal of Medical Virology
  8. Mutagenesis and Carcinogenesis Risk Evaluation for AAV and Lentiviral Gene Therapies
    Toufan Parman, Daniella M. Pizzurro, Jacquelynn Lucas, Zhechu Peng · 2025 · International Journal of Toxicology
  9. Structural basis for nuclear import of bat adeno-associated virus capsid protein
    Mikayla Hoad, Justin A. Roby, Jade Kenneth Forwood · 2024 · Journal of General Virology
  10. Design of Lentivirally Expressed siRNAs
    Ying Poi Liu, Ben Berkhout · 2012 · Methods in molecular biology
  11. Isling: A Tool for Detecting Integration of Wild-Type Viruses and Clinical Vectors
    Suzanne Scott, Claus V. Hallwirth, Felix Hartkopf, Susanna R. Grigson, Yatish Jain, Ian E. Alexander, Denis C. Bauer, Laurence O.W. Wilson · 2021 · Journal of Molecular Biology
  12. Genome defense against exogenous nucleic acids in eukaryotes by non-coding DNA occurs through CRISPR-like mechanisms in the cytosol and the bodyguard protection in the nucleus
    Guo‐Hua Qiu · 2016 · Mutation Research/Reviews in Mutation Research
  13. Gene therapy for the heart: encapsulated viruses to the rescue
    Uma Maheswari Deshetty, Susmita Sil, Shilpa J. Buch · 2024 · Extracellular Vesicles and Circulating Nucleic Acids
  14. Genersatztherapie bei genetisch bedingter Zapfenblindheit
    Regine Mühlfriedel, Naoyuki Tanimoto, M. W. Seeliger · 2014 · Klinische Monatsblätter für Augenheilkunde
  15. Gene Therapy in Pediatric Liver Disease
    Andrés Fernando Muro, Lorenzo D’Antiga, Federico Mingozzi · 2019 · Springer eBooks
  16. Herpes Simplex Virus Type 1/Adeno-Associated Virus Hybrid Vectors
    Anna Oliveira · 2010 · The Open Virology Journal
  17. Substitution of adeno-associated virus Rep protein binding and nicking sites with human chromosome 19 sequences
    McAlister, Victor J, Owens, Roland A · 2010 · Virology Journal
  18. Safer Vectors for Gene Therapy of Primary Immunodeficiencies
    Zulema G. Romero, Miguel G. Toscano, Juan Diego Unciti-Broceta, Ignacio J. Molina, Francisco Martı́n · 2009 · Current Gene Therapy
  19. AAV Vector-Based Gene Therapy, Progress and Current Challenges
    Klaudia Kuranda, Federico Mingozzi · 2017 · Springer eBooks
  20. Genetically Encoded SpyTag Enables Modular AAV Retargeting via SpyCatcher-Fused Ligands for Targeted Gene Delivery
    Anja Armbruster, Maximilian Hörner, Hanna J. Wagner, Claudia Fink‐Straube, Wilfried Weber · 2025 · ACS Synthetic Biology
  21. Recombinant Adeno-Associated Virus Serotype 6 Efficiently Transduces Primary Human Melanocytes
    Hilary M. Sheppard, James E. Ussher, Daniel J. Verdon, Jennifer Hechao Chen, John A. Taylor, P. Rod Dunbar · 2013 · PLoS ONE
  22. Production and use of adeno-associated virus vectors as tools for cancer immunotherapy
    Myriam Fernández-Sendin, Shirley Tenesaca, Marcos Vásquez, Fernando Aranda, Pedro Berraondo · 2019 · Methods in enzymology on CD-ROM/Methods in enzymology
  23. Elucidation of the binding interaction interface between AAV serotype 11 capsid protein and host nuclear import proteins
    Mikayla Hoad, Sepehr Nematollahzadeh, Justin A. Roby, Gualtiero Alvisi, Jade Kenneth Forwood · 2025 · Molecular Therapy — Methods & Clinical Development
  24. New Vectors for Stable and Safe Gene Modification
    Francisco Martı́n, Karim Benabdellah, Marién Cobo, Pilar Munoz, Per O. Anderson, Miguel G. · 2011 · InTech eBooks
  25. Efficiency and Specificity of Targeted Integration Mediated by the Adeno-Associated Virus Serotype 2 Rep 78 Protein
    Pingjuan Li, Michael P. Marino, Jizhong Zou, Takele Argaw, Michael T. Morreale, Brian J. Iaffaldano, Jakob Reiser · 2018 · Human Gene Therapy Methods
  26. High-efficiency HDR in immortalized cell lines by crude rAAV mediated donor template delivery
    Stuti Mehta, Altantsetseg Buyanbat, Ge Zheng, Nan Liu, Stuart H. Orkin · 2022 · bioRxiv (Cold Spring Harbor Laboratory)
  27. Modified AAV5 capsid for improved brain biodistribution following direct injection in preclinical models
    Sebastian N. Kieper, Elisabeth A. Spronck, Meriem Bourajjaj, Roberto D.V.S. Morais, M. Leontien van der Bent, Şeyda Acar Broekmans, Charlot van Rooijen, Rhodé van Westen, Giorgia Squeri, Giso Brasser et al. · 2025 · Molecular Therapy — Methods & Clinical Development
  28. Exploration of the potential of genomic editing in the treatment of congenital adrenal hyperplasia
    Lara E. Graves, Sharntie Christina, Kathryn Mullany, Ian E. Alexander, Henrik Falhammar · 2025 · Frontiers in Endocrinology
  29. Lentiviral vectors as the delivery vehicles for transduction into iPSCs
    Boris Kantor, Ornit Chiba‐Falek · 2021 · Elsevier eBooks
  30. Preclinical Assessment of Antibody Responses to Adeno-Associated Virus (AAV) Vector-Based Capsids of AAV2, AAV5, AAV8, or AAV9 in Laboratory Cynomolgus Macaques ( Macaca fascicularis ) of Asian or Mauritian Origin
    Betina Pajaziti, Ulf Michgehl, Dragica Blazevic, Franziska Fimm-Todt, A. Dütting, Birgit Korbmacher, Stephanie Grote-Wessels, Stefan Michelfelder, Lars Mecklenburg · 2025 · Human Gene Therapy
  31. Recent Advances and Improvements in the Biosafety of Gene Therapy
    Jaichandran Sivalingam, Oi Lian · 2011 · InTech eBooks
  32. A method mediated AAVS1 recombination with Rep mRNA and homologous arms
    Qiantong Xiang, Linian Huang, Sijia Guo, Fang Chen, Xiaojun Zha, Bing Chen, Liangdan Sun, Haisheng Zhou, De‐Pei Liu · 2012 · Acta Biochimica et Biophysica Sinica
  33. Genersatztherapie bei hereditären Netzhauterkrankungen
    Regine Mühlfriedel, Vithiyanjali Sothilingam, Naoyuki Tanimoto, Mathias W. Seeliger · 2017 · Klinische Monatsblätter für Augenheilkunde
  34. Systemic Gene Delivery by Single-Dose Intracardiac Administration of scAAV2/9 and scAAV2/rh10 Variants in Newborn Rats
    Lucie Chansel‐Debordeaux, Mathieu Bourdenx, Nathalie Dutheil, Sandra Doveró, Marie‐Hélène Canron, Clément Jimenez, Erwan Bézard, Benjamin Dehay · 2018 · Human Gene Therapy Methods
  35. Riding the gene therapy wave: challenges and opportunities for rare disease patients and clinicians
    Matthew S. Alexander, Nathaniel H. Robin · 2024 · Current Opinion in Pediatrics
  36. Breast Cancer Gene Therapy
    Gülay Büyükköroğlu, Duygu Abbasoğlu, Candan Hızel · 2014 · Springer eBooks
  37. Optogenetic stimulation of the cochlea
    David López de la Morena · 2019 · eDiss (Georg-August-Universität Göttingen)
  38. Recombinant AAV gene transfer: Emerging applications in immune modulation and cancer therapy
    Yixuan Yang, Rongtao Chen, Yuchen Bao, Heqiao Han, Kai Ma, Xiaolei Pei, Lei Zhang, Wenwei Shao · 2025 · Biochemical Pharmacology
  39. Viral Manipulation of Neural Stem/Precursor Cells
    Nunzio Iraci, Giulia E. Tyzack, Chiara Cossetti, Clara Alfaro‐Cervelló, Stefano Pluchino · 2013 · Neuromethods
  40. Modeling Cancer Using CRISPR-Cas9 Technology
    Sandra Rodríguez, Marta Martínez-Lage, Raúl Torres-Ruiz · 2017 · Elsevier eBooks
  41. Gene therapy approaches in central nervous system regenerative medicine
    Assumpció Bosch, Miguel Chillón · 2020 · Elsevier eBooks
  42. Genetically Engineered Mesenchymal Stem Cells for Cell and Gene Therapy
    Yunjoon Jung, Jan A. Nolta · 2012 · Humana Press eBooks
  43. Uso de vectores derivados de virus adenoasociados para el tratamiento de la enfermedad de Morquio A
    Carlos Javier Alméciga-Díaz, María Andrea Rueda-Páramo, Olga Yaneth Echeverri-Peña, Adriana M. Montaño, Shunji Tomatsu, Luis Alejandro Barrera · 2009 · DOAJ (DOAJ: Directory of Open Access Journals)
  44. Viral Vectors for Studying Drug-Seeking Behavior
    Arlene Martínez-Rivera, Caitlin E. Burgdorf, Anjali M. Rajadhyaksha · 2020 · Neuromethods
  45. Nanoparticles as Cell Tracking Agents in Human Ocular Cell Transplantation Therapy
    David C Mundy, Jeffrey Louis Goldberg · 2021 · Current Ophthalmology Reports
  46. Gene Silencing Methods Using Vector‐Encoded siRNAs or miRNAs
    Ying Poi Liu, Ben Berkhout · 2014 · Wiley eBooks
  47. Adeno-Associated Virus Vectors for Gene Therapy: From Scalable Production Systems via Serotype-Specific Glycan Interaction Patterns to Gene Transfer Applications
    Mario Mietzsch · 2014
  48. Mutations and Genomic Alterations in Liver Cancer
    Jessica Zucman‐Rossi, Jean‐Charles Nault · 2020 · Wiley eBooks
  49. Targeted local combination therapy with checkpoint inhibitors and CAR-NK cells in glioblastoma using DARPin-linked AAV vectors
    Maja Strecker · 2022 · Publication Server of Goethe University Frankfurt am Main (Goethe University Frankfurt)
  50. Biomarker and Bioanalytical Readouts for the Development of AAV Gene Therapy
    Yanmei Lu, Wibke Lembke · 2024 · Wiley eBooks
  51. Microhomology-mediated repair machinery and its relationship with HPV-mediated oncogenesis
    Gabriel J. Starrett, Subhajit Chatterjee · 2024
  52. Expanding AAV cargo capacity for gene therapy of Stargardt disease
    Ivana Trapani · 2014
  53. Investigation and application of novel adeno-associated viral vectors for cystic fibrosis gene therapy
    Benjamin R. Steines, Joseph Zabner, Jeffery L. Meier, Christopher M. Adams, Paul B. McCray, Charles A. Yeaman · 2015
  54. Immune modulation in gene therapy studies
    Fatima Aerts‐Kaya, Leonie C. M. Kaptein, Gerard Wagemaker · 2010 · RePub (Erasmus University Rotterdam)
  55. Uso de vectores lentivirales para mediar la transfección del gen de la enzima n-acetil-galactosamina -6-sulfato-sulfatasa en células en cultivo
    Herrera Mejía · 2020 · Repositorio Institucional (Pontificia Universidad Javeriana)
  56. Aus dem Institut für Experimentelle und Klinische Pharmakologie und Toxikologie Universitätsklinikum Hamburg-Eppendorf
    Thomas Eschenhagen · 2009
  57. Ermittlung und Entstehung der Umsatzsteuer
    Jörg Grune, Reinhard Elvers · 2008 · Gabler eBooks
  58. Towards therapeutic gene delivery to human cancer cells : targeting and entry of baculovirus
    Anna R. Mäkelä · 2008 · Jyväskylä University Digital Archive (University of Jyväskylä)
  59. Increased transgene expression mediated by recombinant adeno- associated virus in human neuroglia cells under microgravity conditions
    Feiyi Sun, Jiewen Zhang, Chengwei Ma, Yaxi Zhang, Yali Li, Lan Zhang, Yulin Deng, Hong Ma · 2016
  60. Development of Helper-Dependent Adenoviral Vectors for Gene Therapy for Inherited Retinal Diseases
    Simon Lam · 2015 · TSpace (University of Toronto)
  61. Evaluation of immune responses to novel Adeno-Associated Viruses for vaccine and gene therapy applications
    Allan Chand · 2012 · Mspace (University of Manitoba)
  62. Stem Cells in the Liver Cancer and the Organ Size Control
    Amita Tiyaboonchai, Yulong Su, Bin Li · 2018 · Elsevier eBooks
  63. Therapy and mechanism of Mendelian eye diseases
    Tsai, Yi-Ting · 2018
  64. Editorial
    Bidyut Baran Saha, Kyaw Thu, Agung Tri Wijayanta · 2018 · Evergreen
  65. Thérapie génique de la dystrophie musculaire de duchenne : utilisation de transgènes de la dystrophine chez le modèle canin
    Christophe Pichavant · 2010
  66. Gene Therapy
    Arianna Malgieri, Paola Spitalieri, Giuseppe Novelli, Federica Carla Sangiuolo · 2010 · Springer eBooks
  67. 遺伝子治療の最前線―AAVベクター遺伝子治療の躍進と課題―
    世志幸 宮川 · 2022 · Nihon Ika Daigaku Igakkai Zasshi
  68. Liver Cancer and the Curative Potential of Nanomedicine
    Adrian Kuzmanović, Cheng Lin, Matthias Bartneck · 2023 · Interdisciplinary cancer research
  69. Biomanufacturing Aspects of Gene Therapy
    James N. Warnock · 2023 · Cell engineering
  70. Effective Transduction of Human Adipose Stromal Cells by a Recombinant Adeno-Associated Virus
    Е.К. Шевченко, П. И. Макаревич, З. И. Цоколаева, Elizaveta I. Ratner, Е. В. Парфёнова · 2010 · Genes and Cells
  71. Even a Worm Will Turn: Immunity Following AAV Vector Administration
    Kruti Patel, Arpana Khatri, Suryanarayan Somanathan · 2024 · Springer eBooks
  72. Analyse des réponses cellulaires induites par l’intégration d’un ADN étranger au sein du génome
    Virginie Gay · 2010 · theses.fr (ABES)
  73. Développement de nouveaux modèles expérimentaux de la Sclérose Latérale Amyotrophique
    Karine Langou · 2010 · theses.fr (ABES)
  74. Gene therapy approach on Charcot-Marie-Tooth type 1A rats
    Hélène Hajjar · 2018 · theses.fr (ABES)
  75. Thérapie génique pour l’amyotrophie spinale à l’aide de vecteur AAV
    Aurore Besse · 2019 · theses.fr (ABES)
  76. Adeno-associated virus in the liver : natural history of the infection and consequences in tumor development
    Tiziana La Bella · 2018 · theses.fr (ABES)
  77. Immunogenicity of recombinant Associated Virus-derived Vectors (rAAV) : how rAAV interact with the innate immune system ?
    Samer Masri · 2022 · theses.fr (ABES)
  78. Alternative bipartite arrangements of VP1 BR1-3 drive efficient nuclear import of AAV2 capsids
    Mikayla Hoad, Sepehr Nematollahzadeh, Davide Cimichella, Silvia Pavan, Ciro Leonardo Pierri, Justin A. Roby, Gualtiero Alvisi, Jade Kenneth Forwood · 2026 · Journal of Biological Chemistry