Adeno-associated virus integration: virus versus vector
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Items 101–178 of 178
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- Transduction of Human Adipose-Derived Mesenchymal Stem Cells by Recombinant Adeno-Associated Virus VectorsMichelle Locke, James E. Ussher, Raakhi M. Mistry, John A. Taylor, P. Rod Dunbar · 2011 · Tissue Engineering Part C Methods
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- Isling: A Tool for Detecting Integration of Wild-Type Viruses and Clinical VectorsSuzanne Scott, Claus V. Hallwirth, Felix Hartkopf, Susanna R. Grigson, Yatish Jain, Ian E. Alexander, Denis C. Bauer, Laurence O.W. Wilson · 2021 · Journal of Molecular Biology
- Genome defense against exogenous nucleic acids in eukaryotes by non-coding DNA occurs through CRISPR-like mechanisms in the cytosol and the bodyguard protection in the nucleusGuo‐Hua Qiu · 2016 · Mutation Research/Reviews in Mutation Research
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- Genersatztherapie bei genetisch bedingter ZapfenblindheitRegine Mühlfriedel, Naoyuki Tanimoto, M. W. Seeliger · 2014 · Klinische Monatsblätter für Augenheilkunde
- Gene Therapy in Pediatric Liver DiseaseAndrés Fernando Muro, Lorenzo D’Antiga, Federico Mingozzi · 2019 · Springer eBooks
- Herpes Simplex Virus Type 1/Adeno-Associated Virus Hybrid VectorsAnna Oliveira · 2010 · The Open Virology Journal
- Substitution of adeno-associated virus Rep protein binding and nicking sites with human chromosome 19 sequencesMcAlister, Victor J, Owens, Roland A · 2010 · Virology Journal
- Safer Vectors for Gene Therapy of Primary ImmunodeficienciesZulema G. Romero, Miguel G. Toscano, Juan Diego Unciti-Broceta, Ignacio J. Molina, Francisco Martı́n · 2009 · Current Gene Therapy
- AAV Vector-Based Gene Therapy, Progress and Current ChallengesKlaudia Kuranda, Federico Mingozzi · 2017 · Springer eBooks
- Genetically Encoded SpyTag Enables Modular AAV Retargeting via SpyCatcher-Fused Ligands for Targeted Gene DeliveryAnja Armbruster, Maximilian Hörner, Hanna J. Wagner, Claudia Fink‐Straube, Wilfried Weber · 2025 · ACS Synthetic Biology
- Recombinant Adeno-Associated Virus Serotype 6 Efficiently Transduces Primary Human MelanocytesHilary M. Sheppard, James E. Ussher, Daniel J. Verdon, Jennifer Hechao Chen, John A. Taylor, P. Rod Dunbar · 2013 · PLoS ONE
- Production and use of adeno-associated virus vectors as tools for cancer immunotherapyMyriam Fernández-Sendin, Shirley Tenesaca, Marcos Vásquez, Fernando Aranda, Pedro Berraondo · 2019 · Methods in enzymology on CD-ROM/Methods in enzymology
- Elucidation of the binding interaction interface between AAV serotype 11 capsid protein and host nuclear import proteinsMikayla Hoad, Sepehr Nematollahzadeh, Justin A. Roby, Gualtiero Alvisi, Jade Kenneth Forwood · 2025 · Molecular Therapy — Methods & Clinical Development
- New Vectors for Stable and Safe Gene ModificationFrancisco Martı́n, Karim Benabdellah, Marién Cobo, Pilar Munoz, Per O. Anderson, Miguel G. · 2011 · InTech eBooks
- Efficiency and Specificity of Targeted Integration Mediated by the Adeno-Associated Virus Serotype 2 Rep 78 ProteinPingjuan Li, Michael P. Marino, Jizhong Zou, Takele Argaw, Michael T. Morreale, Brian J. Iaffaldano, Jakob Reiser · 2018 · Human Gene Therapy Methods
- High-efficiency HDR in immortalized cell lines by crude rAAV mediated donor template deliveryStuti Mehta, Altantsetseg Buyanbat, Ge Zheng, Nan Liu, Stuart H. Orkin · 2022 · bioRxiv (Cold Spring Harbor Laboratory)
- Modified AAV5 capsid for improved brain biodistribution following direct injection in preclinical modelsSebastian N. Kieper, Elisabeth A. Spronck, Meriem Bourajjaj, Roberto D.V.S. Morais, M. Leontien van der Bent, Şeyda Acar Broekmans, Charlot van Rooijen, Rhodé van Westen, Giorgia Squeri, Giso Brasser et al. · 2025 · Molecular Therapy — Methods & Clinical Development
- Exploration of the potential of genomic editing in the treatment of congenital adrenal hyperplasiaLara E. Graves, Sharntie Christina, Kathryn Mullany, Ian E. Alexander, Henrik Falhammar · 2025 · Frontiers in Endocrinology
- Lentiviral vectors as the delivery vehicles for transduction into iPSCsBoris Kantor, Ornit Chiba‐Falek · 2021 · Elsevier eBooks
- Preclinical Assessment of Antibody Responses to Adeno-Associated Virus (AAV) Vector-Based Capsids of AAV2, AAV5, AAV8, or AAV9 in Laboratory Cynomolgus Macaques ( Macaca fascicularis ) of Asian or Mauritian OriginBetina Pajaziti, Ulf Michgehl, Dragica Blazevic, Franziska Fimm-Todt, A. Dütting, Birgit Korbmacher, Stephanie Grote-Wessels, Stefan Michelfelder, Lars Mecklenburg · 2025 · Human Gene Therapy
- Recent Advances and Improvements in the Biosafety of Gene TherapyJaichandran Sivalingam, Oi Lian · 2011 · InTech eBooks
- A method mediated AAVS1 recombination with Rep mRNA and homologous armsQiantong Xiang, Linian Huang, Sijia Guo, Fang Chen, Xiaojun Zha, Bing Chen, Liangdan Sun, Haisheng Zhou, De‐Pei Liu · 2012 · Acta Biochimica et Biophysica Sinica
- Genersatztherapie bei hereditären NetzhauterkrankungenRegine Mühlfriedel, Vithiyanjali Sothilingam, Naoyuki Tanimoto, Mathias W. Seeliger · 2017 · Klinische Monatsblätter für Augenheilkunde
- Systemic Gene Delivery by Single-Dose Intracardiac Administration of scAAV2/9 and scAAV2/rh10 Variants in Newborn RatsLucie Chansel‐Debordeaux, Mathieu Bourdenx, Nathalie Dutheil, Sandra Doveró, Marie‐Hélène Canron, Clément Jimenez, Erwan Bézard, Benjamin Dehay · 2018 · Human Gene Therapy Methods
- Riding the gene therapy wave: challenges and opportunities for rare disease patients and cliniciansMatthew S. Alexander, Nathaniel H. Robin · 2024 · Current Opinion in Pediatrics
- Breast Cancer Gene TherapyGülay Büyükköroğlu, Duygu Abbasoğlu, Candan Hızel · 2014 · Springer eBooks
- Optogenetic stimulation of the cochleaDavid López de la Morena · 2019 · eDiss (Georg-August-Universität Göttingen)
- Recombinant AAV gene transfer: Emerging applications in immune modulation and cancer therapyYixuan Yang, Rongtao Chen, Yuchen Bao, Heqiao Han, Kai Ma, Xiaolei Pei, Lei Zhang, Wenwei Shao · 2025 · Biochemical Pharmacology
- Viral Manipulation of Neural Stem/Precursor CellsNunzio Iraci, Giulia E. Tyzack, Chiara Cossetti, Clara Alfaro‐Cervelló, Stefano Pluchino · 2013 · Neuromethods
- Modeling Cancer Using CRISPR-Cas9 TechnologySandra Rodríguez, Marta Martínez-Lage, Raúl Torres-Ruiz · 2017 · Elsevier eBooks
- Gene therapy approaches in central nervous system regenerative medicineAssumpció Bosch, Miguel Chillón · 2020 · Elsevier eBooks
- Genetically Engineered Mesenchymal Stem Cells for Cell and Gene TherapyYunjoon Jung, Jan A. Nolta · 2012 · Humana Press eBooks
- Uso de vectores derivados de virus adenoasociados para el tratamiento de la enfermedad de Morquio ACarlos Javier Alméciga-Díaz, María Andrea Rueda-Páramo, Olga Yaneth Echeverri-Peña, Adriana M. Montaño, Shunji Tomatsu, Luis Alejandro Barrera · 2009 · DOAJ (DOAJ: Directory of Open Access Journals)
- Viral Vectors for Studying Drug-Seeking BehaviorArlene Martínez-Rivera, Caitlin E. Burgdorf, Anjali M. Rajadhyaksha · 2020 · Neuromethods
- Nanoparticles as Cell Tracking Agents in Human Ocular Cell Transplantation TherapyDavid C Mundy, Jeffrey Louis Goldberg · 2021 · Current Ophthalmology Reports
- Gene Silencing Methods Using Vector‐Encoded siRNAs or miRNAsYing Poi Liu, Ben Berkhout · 2014 · Wiley eBooks
- Adeno-Associated Virus Vectors for Gene Therapy: From Scalable Production Systems via Serotype-Specific Glycan Interaction Patterns to Gene Transfer ApplicationsMario Mietzsch · 2014
- Mutations and Genomic Alterations in Liver CancerJessica Zucman‐Rossi, Jean‐Charles Nault · 2020 · Wiley eBooks
- Targeted local combination therapy with checkpoint inhibitors and CAR-NK cells in glioblastoma using DARPin-linked AAV vectorsMaja Strecker · 2022 · Publication Server of Goethe University Frankfurt am Main (Goethe University Frankfurt)
- Biomarker and Bioanalytical Readouts for the Development of AAV Gene TherapyYanmei Lu, Wibke Lembke · 2024 · Wiley eBooks
- Microhomology-mediated repair machinery and its relationship with HPV-mediated oncogenesisGabriel J. Starrett, Subhajit Chatterjee · 2024
- Expanding AAV cargo capacity for gene therapy of Stargardt diseaseIvana Trapani · 2014
- Investigation and application of novel adeno-associated viral vectors for cystic fibrosis gene therapyBenjamin R. Steines, Joseph Zabner, Jeffery L. Meier, Christopher M. Adams, Paul B. McCray, Charles A. Yeaman · 2015
- Immune modulation in gene therapy studiesFatima Aerts‐Kaya, Leonie C. M. Kaptein, Gerard Wagemaker · 2010 · RePub (Erasmus University Rotterdam)
- Uso de vectores lentivirales para mediar la transfección del gen de la enzima n-acetil-galactosamina -6-sulfato-sulfatasa en células en cultivoHerrera Mejía · 2020 · Repositorio Institucional (Pontificia Universidad Javeriana)
- Aus dem Institut für Experimentelle und Klinische Pharmakologie und Toxikologie Universitätsklinikum Hamburg-EppendorfThomas Eschenhagen · 2009
- Ermittlung und Entstehung der UmsatzsteuerJörg Grune, Reinhard Elvers · 2008 · Gabler eBooks
- Towards therapeutic gene delivery to human cancer cells : targeting and entry of baculovirusAnna R. Mäkelä · 2008 · Jyväskylä University Digital Archive (University of Jyväskylä)
- Increased transgene expression mediated by recombinant adeno- associated virus in human neuroglia cells under microgravity conditionsFeiyi Sun, Jiewen Zhang, Chengwei Ma, Yaxi Zhang, Yali Li, Lan Zhang, Yulin Deng, Hong Ma · 2016
- Development of Helper-Dependent Adenoviral Vectors for Gene Therapy for Inherited Retinal DiseasesSimon Lam · 2015 · TSpace (University of Toronto)
- Evaluation of immune responses to novel Adeno-Associated Viruses for vaccine and gene therapy applicationsAllan Chand · 2012 · Mspace (University of Manitoba)
- Stem Cells in the Liver Cancer and the Organ Size ControlAmita Tiyaboonchai, Yulong Su, Bin Li · 2018 · Elsevier eBooks
- Therapy and mechanism of Mendelian eye diseasesTsai, Yi-Ting · 2018
- EditorialBidyut Baran Saha, Kyaw Thu, Agung Tri Wijayanta · 2018 · Evergreen
- Thérapie génique de la dystrophie musculaire de duchenne : utilisation de transgènes de la dystrophine chez le modèle caninChristophe Pichavant · 2010
- Gene TherapyArianna Malgieri, Paola Spitalieri, Giuseppe Novelli, Federica Carla Sangiuolo · 2010 · Springer eBooks
- 遺伝子治療の最前線―AAVベクター遺伝子治療の躍進と課題―世志幸 宮川 · 2022 · Nihon Ika Daigaku Igakkai Zasshi
- Liver Cancer and the Curative Potential of NanomedicineAdrian Kuzmanović, Cheng Lin, Matthias Bartneck · 2023 · Interdisciplinary cancer research
- Biomanufacturing Aspects of Gene TherapyJames N. Warnock · 2023 · Cell engineering
- Effective Transduction of Human Adipose Stromal Cells by a Recombinant Adeno-Associated VirusЕ.К. Шевченко, П. И. Макаревич, З. И. Цоколаева, Elizaveta I. Ratner, Е. В. Парфёнова · 2010 · Genes and Cells
- Even a Worm Will Turn: Immunity Following AAV Vector AdministrationKruti Patel, Arpana Khatri, Suryanarayan Somanathan · 2024 · Springer eBooks
- Analyse des réponses cellulaires induites par l’intégration d’un ADN étranger au sein du génomeVirginie Gay · 2010 · theses.fr (ABES)
- Développement de nouveaux modèles expérimentaux de la Sclérose Latérale AmyotrophiqueKarine Langou · 2010 · theses.fr (ABES)
- Gene therapy approach on Charcot-Marie-Tooth type 1A ratsHélène Hajjar · 2018 · theses.fr (ABES)
- Thérapie génique pour l’amyotrophie spinale à l’aide de vecteur AAVAurore Besse · 2019 · theses.fr (ABES)
- Adeno-associated virus in the liver : natural history of the infection and consequences in tumor developmentTiziana La Bella · 2018 · theses.fr (ABES)
- Immunogenicity of recombinant Associated Virus-derived Vectors (rAAV) : how rAAV interact with the innate immune system ?Samer Masri · 2022 · theses.fr (ABES)
- Alternative bipartite arrangements of VP1 BR1-3 drive efficient nuclear import of AAV2 capsidsMikayla Hoad, Sepehr Nematollahzadeh, Davide Cimichella, Silvia Pavan, Ciro Leonardo Pierri, Justin A. Roby, Gualtiero Alvisi, Jade Kenneth Forwood · 2026 · Journal of Biological Chemistry