Several rAAV Vectors Efficiently Cross the Blood–brain Barrier and Transduce Neurons and Astrocytes in the Neonatal Mouse Central Nervous System
Zhang, Hongwei, Yang, Bin, Mu, Xin, Ahmed, Seemin Seher, Su, Qin, He, Ran, Wang, Hongyan, Mueller, Christian +4 more·2011·Molecular Therapy
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- Optimized AAV capsids for diseases of the basal ganglia show robust potency and distribution in adult nonhuman primatesDavid E. Leib, YH Chen, Luis Tecedor, Paul T. Ranum, Megan S. Keiser, BC Lewandowski, Ellie M. Carrell, S Arora, Icnelia Huerta-Ocampo, Xing Liu et al. · 2024 · bioRxiv (Cold Spring Harbor Laboratory)
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- Gene therapy for Krabbe disease: evidence from mouse and canine modelsYang Li, Xiang Dong, Jian Cheng Guo, Yafeng Lv · 2025 · Gene
- ADAR-mediated RNA editing in CNS disorders: from pathogenic mechanisms to therapeutic opportunitiesFushuang Zheng, Rongli Guan, Xiaojin Yu, Jiaxin Yang, Hai Zhao, Fan Yang · 2026 · Cellular & Molecular Biology Letters
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