In vivo genome editing using nuclease-encoding mRNA corrects SP-B deficiency

Mahiny, Azita J, Dewerth, Alexander, Mays, Lauren E, Alkhaled, Mohammed, Mothes, Benedikt, Malaeksefat, Emad, Loretz, Brigitta, Rottenberger, Jennifer +15 more·2015·Nature Biotechnology
DOI 10.1038/nbt.3241

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