Functionally defined therapeutic targets in diffuse intrinsic pontine glioma

Grasso, Catherine S, Tang, Yujie, Truffaux, Nathalene, Berlow, Noah E, Liu, Lining, Debily, Marie-Anne, Quist, Michael J, Davis, Lara E +32 more·2015·Nature Medicine

Cited by (686)

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  1. Additional file 5 of Reversal of cancer gene expression identifies repurposed drugs for diffuse intrinsic pontine glioma
    Guisheng Zhao, Patrick A. Newbury, Yukitomo Ishi, Eugene Chekalin, Billy Zeng, Benjamin Scott Glicksberg, Anita Wen, Shreya Paithankar, Takahiro Sasaki, Amreena Suri et al. · 2022 · Figshare
  2. Dual Targeting of Histone Deacetylases and MYC as Potential Treatment Strategy for H3-K27M Pediatric Gliomas
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  3. Reviewer #2 (Public Review): Dual Targeting of Histone Deacetylases and MYC as Potential Treatment Strategy for H3-K27M Pediatric Gliomas
    Danielle Algranati, Roni Oren, Bareket Dassa et al. · 2024 · eLife
  4. Author response: Dual Targeting of Histone Deacetylases and MYC as Potential Treatment Strategy for H3-K27M Pediatric Gliomas
    Danielle Algranati, Roni Oren, Bareket Dassa, Liat Fellus-Alyagor, Alexander N. Plotnikov, Haim Michael Barr, Alon Harmelin, Nir London, Guy Ron, Noa Furth et al. · 2024 · eLife
  5. eLife Assessment: Dual Targeting of Histone Deacetylases and MYC as Potential Treatment Strategy for H3-K27M Pediatric Gliomas
    Yamini Dalal · 2024 · eLife
  6. Dual Targeting of Histone Deacetylases and MYC as Potential Treatment Strategy for H3-K27M Pediatric Gliomas
    Danielle Algranati, Roni Oren, Bareket Dassa, Liat Fellus-Alyagor, Alexander N. Plotnikov, Haim Michael Barr, Alon Harmelin, Nir London, Guy Ron, Noa Furth et al. · 2024 · eLife
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  14. Advances in preclinical models for pediatric diffuse intrinsic pontine glioma
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  15. Additional file 1 of Histone deacetylase inhibitor panobinostat induces antitumor activity in epithelioid sarcoma and rhabdoid tumor by growth factor receptor modulation
    Anne C. Harttrampf, Maria Eugénia Marques Da Costa, Aline Renoult, Estelle Daudigeos‐Dubus, Birgit Geoerger · 2021 · Figshare
  16. Additional file 4 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  17. Additional file 5 of LncRNA NUTM2A-AS1 silencing inhibits glioma via miR-376a-3p/YAP1 axis
    Yuecheng Zeng, Zhenyu Yang, Yang, Yang, Wang, Peng · 2024 · Figshare
  18. Additional file 6 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  19. Additional file 2 of Histone deacetylase inhibitor panobinostat induces antitumor activity in epithelioid sarcoma and rhabdoid tumor by growth factor receptor modulation
    Anne C. Harttrampf, Maria Eugénia Marques Da Costa, Aline Renoult, Estelle Daudigeos‐Dubus, Birgit Geoerger · 2021 · Figshare
  20. Additional file 8 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  21. Additional file 5 of TP53 wild-type/PPM1D mutant diffuse intrinsic pontine gliomas are sensitive to a MDM2 antagonist
    Xu, Cheng, Liu, Heng, Christopher J. Pirozzi, Chen, Lee H., Paula K. Greer, Bill H. Diplas, Zhang, Liwei, Matthew S. Waitkus, Yiping He, Hai Yan · 2021 · Figshare
  22. Additional file 3 of TP53 wild-type/PPM1D mutant diffuse intrinsic pontine gliomas are sensitive to a MDM2 antagonist
    Xu, Cheng, Liu, Heng, Christopher J. Pirozzi, Chen, Lee H., Paula K. Greer, Bill H. Diplas, Zhang, Liwei, Matthew S. Waitkus, Yiping He, Hai Yan · 2021 · Figshare
  23. Additional file 1 of Targeting GBM with an Oncolytic Picornavirus SVV-001 alone and in combination with fractionated Radiation in a Novel Panel of Orthotopic PDX models
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  24. Additional file 2 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  25. Additional file 6 of Histone deacetylase inhibitor panobinostat induces antitumor activity in epithelioid sarcoma and rhabdoid tumor by growth factor receptor modulation
    Anne C. Harttrampf, Maria Eugénia Marques Da Costa, Aline Renoult, Estelle Daudigeos‐Dubus, Birgit Geoerger · 2021 · Figshare
  26. Additional file 16 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  27. Additional file 10 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  28. Additional file 1 of TP53 wild-type/PPM1D mutant diffuse intrinsic pontine gliomas are sensitive to a MDM2 antagonist
    Xu, Cheng, Liu, Heng, Christopher J. Pirozzi, Chen, Lee H., Paula K. Greer, Bill H. Diplas, Zhang, Liwei, Matthew S. Waitkus, Yiping He, Hai Yan · 2021 · Figshare
  29. Additional file 1 of Common molecular features of H3K27M DMGs and PFA ependymomas map to hindbrain developmental pathways
    Pun, Matthew, Pratt, Drew, Patricia R. Nano, Joshi, Piyush K., Li Jiang, Bernhard Englinger, Rao, Arvind, Cieslik, Marcin, Arul M. Chinnaiyan, Aldape, Kenneth et al. · 2024 · Figshare
  30. Additional file 9 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  31. Additional file 12 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  32. Additional file 4 of Histone deacetylase inhibitor panobinostat induces antitumor activity in epithelioid sarcoma and rhabdoid tumor by growth factor receptor modulation
    Anne C. Harttrampf, Maria Eugénia Marques Da Costa, Aline Renoult, Estelle Daudigeos‐Dubus, Birgit Geoerger · 2021 · Figshare
  33. Additional file 4 of TP53 wild-type/PPM1D mutant diffuse intrinsic pontine gliomas are sensitive to a MDM2 antagonist
    Xu, Cheng, Liu, Heng, Christopher J. Pirozzi, Chen, Lee H., Paula K. Greer, Bill H. Diplas, Zhang, Liwei, Matthew S. Waitkus, Yiping He, Hai Yan · 2021 · Figshare
  34. Additional file 2 of LncRNA NUTM2A-AS1 silencing inhibits glioma via miR-376a-3p/YAP1 axis
    Yuecheng Zeng, Zhenyu Yang, Yang, Yang, Wang, Peng · 2024 · Figshare
  35. Additional file 1 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  36. Additional file 5 of Histone deacetylase inhibitor panobinostat induces antitumor activity in epithelioid sarcoma and rhabdoid tumor by growth factor receptor modulation
    Anne C. Harttrampf, Maria Eugénia Marques Da Costa, Aline Renoult, Estelle Daudigeos‐Dubus, Birgit Geoerger · 2021 · Figshare
  37. Additional file 1 of Laminin-associated integrins mediate Diffuse Intrinsic Pontine Glioma infiltration and therapy response within a neural assembloid model
    Sauradeep Sinha, Michelle S. Huang, Georgios Mikos, Yudhishtar S. Bedi, Luis Soto, Sarah Lensch, Manish Ayushman, Lacramioara Bintu, Nidhi Bhutani, Sarah C. Heilshorn et al. · 2024 · Figshare
  38. Additional file 6 of TP53 wild-type/PPM1D mutant diffuse intrinsic pontine gliomas are sensitive to a MDM2 antagonist
    Xu, Cheng, Liu, Heng, Christopher J. Pirozzi, Chen, Lee H., Paula K. Greer, Bill H. Diplas, Zhang, Liwei, Matthew S. Waitkus, Yiping He, Hai Yan · 2021 · Figshare
  39. Additional file 2 of TP53 wild-type/PPM1D mutant diffuse intrinsic pontine gliomas are sensitive to a MDM2 antagonist
    Xu, Cheng, Liu, Heng, Christopher J. Pirozzi, Chen, Lee H., Paula K. Greer, Bill H. Diplas, Zhang, Liwei, Matthew S. Waitkus, Yiping He, Hai Yan · 2021 · Figshare
  40. Additional file 4 of Reversal of cancer gene expression identifies repurposed drugs for diffuse intrinsic pontine glioma
    Guisheng Zhao, Patrick A. Newbury, Ishi, Yukitomo, Eugene Chekalin, Zeng, Billy, Glicksberg, Benjamin S., Anita Wen, Shreya Paithankar, Takahiro Sasaki, Amreena Suri et al. · 2022 · Figshare
  41. Additional file 1 of LncRNA NUTM2A-AS1 silencing inhibits glioma via miR-376a-3p/YAP1 axis
    Yuecheng Zeng, Zhenyu Yang, Yang, Yang, Wang, Peng · 2024 · Figshare
  42. Additional file 3 of LncRNA NUTM2A-AS1 silencing inhibits glioma via miR-376a-3p/YAP1 axis
    Yuecheng Zeng, Zhenyu Yang, Yang, Yang, Wang, Peng · 2024 · Figshare
  43. Additional file 3 of Histone deacetylase inhibitor panobinostat induces antitumor activity in epithelioid sarcoma and rhabdoid tumor by growth factor receptor modulation
    Anne C. Harttrampf, Maria Eugénia Marques Da Costa, Aline Renoult, Estelle Daudigeos‐Dubus, Birgit Geoerger · 2021 · Figshare
  44. Additional file 7 of TP53 wild-type/PPM1D mutant diffuse intrinsic pontine gliomas are sensitive to a MDM2 antagonist
    Xu, Cheng, Liu, Heng, Christopher J. Pirozzi, Chen, Lee H., Paula K. Greer, Bill H. Diplas, Zhang, Liwei, Matthew S. Waitkus, Yiping He, Hai Yan · 2021 · Figshare
  45. Additional file 2 of Laminin-associated integrins mediate Diffuse Intrinsic Pontine Glioma infiltration and therapy response within a neural assembloid model
    Sauradeep Sinha, Michelle S. Huang, Georgios Mikos, Yudhishtar S. Bedi, Luis Soto, Sarah Lensch, Manish Ayushman, Lacramioara Bintu, Nidhi Bhutani, Sarah C. Heilshorn et al. · 2024 · Figshare
  46. Additional file 3 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  47. Additional file 4 of LncRNA NUTM2A-AS1 silencing inhibits glioma via miR-376a-3p/YAP1 axis
    Yuecheng Zeng, Zhenyu Yang, Yang, Yang, Wang, Peng · 2024 · Figshare
  48. Additional file 13 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  49. Additional file 7 of Histone deacetylase inhibitor panobinostat induces antitumor activity in epithelioid sarcoma and rhabdoid tumor by growth factor receptor modulation
    Anne C. Harttrampf, Maria Eugénia Marques Da Costa, Aline Renoult, Estelle Daudigeos‐Dubus, Birgit Geoerger · 2021 · Figshare
  50. Additional file 14 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  51. Additional file 15 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  52. Additional file 11 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  53. Additional file 5 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  54. Additional file 7 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  55. Additional file 17 of Purine salvage promotes treatment resistance in H3K27M-mutant diffuse midline glioma
    Erik R. Peterson, Sajjakulnukit, Peter, Andrew J. Scott, Caleb Heaslip, Andren, Anthony, Kari Wilder-Romans, Zhou, Weihua, Sravya Palavalasa, Navyateja Korimerla, Angelica Lin et al. · 2024 · Figshare
  56. Additional file 1 of Histone H3.3 K27M chromatin functions implicate a network of neurodevelopmental factors including ASCL1 and NEUROD1 in DIPG
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  58. A new hope: Clinical advances in targeted therapies for pediatric diffuse midline glioma
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  60. Molecular Characterization of Pediatric Brainstem Gliomas (DIPG) and Identification of New Therapeutic Targets
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