A genome-editing strategy to treat β-hemoglobinopathies that recapitulates a mutation associated with a benign genetic condition

Traxler, Elizabeth A, Yao, Yu, Wang, Yong-Dong, Woodard, Kaitly J, Kurita, Ryo, Nakamura, Yukio, Hughes, Jim R, Hardison, Ross C +3 more·2016·Nature Medicine
DOI 10.1038/nm.4170

Cited by (367)

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  26. Additional file 23 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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  29. Additional file 2 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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  30. Additional file 12 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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  31. Additional file 15 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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  32. Additional file 5 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
    Nicholas Brookhouser, Toan Nguyen, Stefan J. Tekel, Kylie Standage-Beier, Xiao Wang, Brafman, David A. · 2020 · Figshare
  33. Additional file 8 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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  34. Additional file 7 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
    Nicholas Brookhouser, Toan Nguyen, Stefan J. Tekel, Kylie Standage-Beier, Xiao Wang, Brafman, David A. · 2020 · Figshare
  35. Additional file 22 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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  36. Additional file 3 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
    Nicholas Brookhouser, Toan Nguyen, Stefan J. Tekel, Kylie Standage-Beier, Xiao Wang, Brafman, David A. · 2020 · Figshare
  37. Additional file 17 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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  38. Additional file 19 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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  39. Additional file 20 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
    Nicholas Brookhouser, Toan Nguyen, Stefan J. Tekel, Kylie Standage-Beier, Xiao Wang, Brafman, David A. · 2020 · Figshare
  40. Additional file 11 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
    Nicholas Brookhouser, Toan Nguyen, Stefan J. Tekel, Kylie Standage-Beier, Xiao Wang, Brafman, David A. · 2020 · Figshare
  41. Additional file 13 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
    Nicholas Brookhouser, Toan Nguyen, Stefan J. Tekel, Kylie Standage-Beier, Xiao Wang, Brafman, David A. · 2020 · Figshare
  42. Additional file 6 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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  43. Additional file 10 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
    Nicholas Brookhouser, Toan Nguyen, Stefan J. Tekel, Kylie Standage-Beier, Xiao Wang, Brafman, David A. · 2020 · Figshare
  44. Additional file 1 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
    Nicholas Brookhouser, Toan Nguyen, Stefan J. Tekel, Kylie Standage-Beier, Xiao Wang, Brafman, David A. · 2020 · Figshare
  45. Additional file 9 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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  46. Additional file 16 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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  47. Additional file 4 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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  48. Additional file 14 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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  49. Additional file 21 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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  50. Additional file 18 of A Cas9-mediated adenosine transient reporter enables enrichment of ABE-targeted cells
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