Recombinant Adeno-Associated Viral Vectors Mediate Long-Term Transgene Expression in Muscle

Clark, K. Reed, Sferra, Thomas J., Johnson, Philip R.·1997·Human Gene Therapy

Cited by (153)

Items 101–153 of 153

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  2. Gene Transfer into the CNS Using Recombinant Adeno-associated Virus: Analysis of Vector DNA Forms Resulting in Sustained Expression
    Kelly Reed Clark, Thomas J. Sferra, Warren David Lo, Guang Qu, Ruju Chen, Philip R. Johnson · 1999 · Journal of drug targeting
  3. Adeno-Associated Virus Vectors Show Variable Dependence on Divalent Cations for Thermostability: Implications for Purification and Handling
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  4. Double strand interaction is the predominant pathway for intermolecular recombination of adeno-associated viral genomes.
    Y. Yue, D. Duan · 2003 · Virology
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  7. Microsphere-adenoviral complexes target and transduce the glomerulus in vivo
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  8. Adeno-Associated Virus-Mediated Vascular Endothelial Growth Factor Gene Therapy in Skeletal Muscle before Transplantation Promotes Revascularization of Regenerating Muscle
    Gayle M. Smythe, May C. Lai, Miranda D. Grounds, Piroska Elizabeth Rakoczy · 2002 · Tissue Engineering
  9. Adenovirus-mediated human pancreatic lipase gene transfer to rat bile: gene therapy of fat malabsorption
    David G. Kuhel, Shuqin Zheng, Patrick Tso, David Y. Hui · 2000 · American Journal of Physiology-Gastrointestinal and Liver Physiology
  10. Recombinant adeno-associated virus type 2 mediates highly efficient gene transfer in regenerating rat skeletal muscle
    Jérôme Abadie, Véronique Blouin, Lydie Guigand, Monique Wyers, Y. Chérel · 2002 · Gene Therapy
  11. Gene Transfer And Models Of Gene Therapy For The Myocardium
    M. Yvonne Alexander, Keith A. Webster, Patricia H. McDonald, Howard M. Prentice · 1999 · Clinical and Experimental Pharmacology and Physiology
  12. Gene Transfer to the Gastrointestinal Tract After Peroral Administration of Recombinant Adeno‐associated Virus Type 2 Vectors
    Guohong Shao, Kristin C. Greathouse, Qin Miao Huang, Chiou-Miin Wang, Thomas J. Sferra · 2006 · Journal of Pediatric Gastroenterology and Nutrition
  13. Regulated hAAT Expression from a Novel rAAV Vector and Its Application in the Prevention of Type 1 Diabetes
    Hongxia Ma, Yuanqing Lu, Keith Lowe, Lonneke M. van der Meijden-Erkelens, Clive Henry Wasserfall, Mark A. Atkinson, Sihong Song · 2019 · Journal of Clinical Medicine
  14. Gene-Based Vaccine Approaches for Respiratory Syncytial Virus
    Rebecca J. Loomis, Philip R. Johnson · 2013 · Current topics in microbiology and immunology
  15. Optimization of transfection mediated by calcium phosphate for plasmid rAAV‐LacZ (recombinant adeno‐associated virus–β‐galactosidase reporter gene) production in suspension‐cultured HEK‐293 (human embryonic kidney 293) cells
    Lei Feng, Meijin Guo, Shuxiang Zhang, Ju Chu, Yingping Zhuang, Siliang Zhang · 2007 · Biotechnology and Applied Biochemistry
  16. Delivery of Recombinant Adeno-Associated Virus Vectors to Rat Diaphragm Muscle via Direct Intramuscular Injection
    Ashley J. Smuder, Darin J. Falk, Kurt J. Sollanek, W. Bradley Nelson, Scott K. Powers · 2013 · Human Gene Therapy Methods
  17. Biological Intervention Based on Cell and Gene Therapy to Improve Muscle Healing after Laceration
    C Lee · 2000 · Journal of Musculoskeletal Research
  18. Understanding the Cross-Talk between Ovarian Tumors and Immune Cells: Mechanisms for Effective Immunotherapies
    Maurizio Chiriva‐Internati, Leonardo Mirandola, W. Martin Kast, Marjorie Jenkins, Everardo Cobos, Martin J. Cannon · 2011 · International Reviews of Immunology
  19. Adeno-associated virus vector-mediated gene transfer to somatic cells in the central nervous system
    Ronald L. Klein, Ronald J. Mandel, Nicholas Muzyczka · 2000 · Advances in virus research
  20. Long‐Term Expression of a Transferred Gene in Epstein–Barr Virus Transformed Human B Cells
    Guixiu Shi, Yingyi Wang, Y. Liu, Wei Cui, Fangtao Zhao, Ling Zhu · 2001 · Scandinavian Journal of Immunology
  21. Efficient infection of mature skeletal muscle with herpes simplex virus vectors by using dextran sulfate as a co-receptor
    Sonia N. Yeung, K Bockhold, Frank Tufaro · 1999 · Gene Therapy
  22. Challenges for gene therapy for muscular dystrophy
    Jerry R. Mendell, K. Reed Clark · 2006 · Current Neurology and Neuroscience Reports
  23. BIOLOGICAL INTERVENTION BASED ON CELL AND GENE THERAPY TO IMPROVE MUSCLE HEALING AFTER LACERATION
    Chang Woo Lee, Kazumasa Fukushima, Arvydas Ūsas, Lin Xin, Dalip Pelinkovic, Vladimir Martinek, George T. Somogyi, Paul D. Robbins, Freddie H. Fu, Johnny Huard · 2000 · Journal of Musculoskeletal Research
  24. IGF1 gene transfer into skeletal muscle using recombinant adeno-associated virus in a rat model of liver cirrhosis
    Mikel Zaratiegui, Inma Castilla‐Cortázar, Maria Inmaculada Garcia‐Fernandez, Jorge Augusto Quiroga, Jesús Prìeto, Francisco Javier Novo · 2002 · Journal of Physiology and Biochemistry
  25. Towards metabolic sink therapy for mut methylmalonic acidaemia: Correction of methylmalonyl‐CoA mutase deficiency in T lymphocytes from a mut methylmalonic acidaemia child by retroviral‐mediated gene transfer
    Chun‐che Chang, K J Hsiao, Y.‐M. Lee, C.‐M. Lin · 1999 · Journal of Inherited Metabolic Disease
  26. Concepts in Genetic Medicine
    2007 · Wiley eBooks
  27. Adeno-Associated Viral Vector Mediated Expression of Broadly- Neutralizing Antibodies Against HIV-Hitting a Fast-Moving Target
    Chringma Sherpa, Stuart F.J. Le Grice · 2020 · Current HIV Research
  28. Adeno‐associated viral vectors for gene therapy
    Terence R. Flotte, Kenneth I. Berns · 2005 · Laboratory techniques in biochemistry and molecular biology
  29. Recombinant Adeno-Associated Virus-Mediated Expression of O6-Alkylguanine-DNA-alkyltransferase Protects Human Epithelial and Hematopoietic Cells against Chloroethylating Agent Toxicity
    S.J. Longhurst, Joseph A. Rafferty, John R. Arrand, N. Cortez, Catherine Giraud, Kenneth I. Berns, LJ Fairbairn · 1999 · Human Gene Therapy
  30. Adeno-Associated Virus Based Gene Therapy in Skeletal Muscle
    Richard J. Bartlett, Jesica M. McCue · 2003 · Humana Press eBooks
  31. A gene therapy approach to treatment of autoimmune disease
    Christine M. Seroogy, C. Garrison Fathman · 1998 · Immunologic Research
  32. Expression of HIV-1 broadly neutralizing antibodies mediated by recombinant adeno-associated virus 8 in vitro and in vivo
    Yongjiao Yu, Lu Fu, Xiaoyu Jiang, Shanshan Guan, Ziyu Kuai, Wei Kong, Yuhua Shi, Yaming Shan · 2016 · Molecular Immunology
  33. The persistence of alien genomes
    Peter J. Tattersall · 2000 · Proceedings of the National Academy of Sciences
  34. Ectopic Expression of Active Processed Form of Atrial Natriuretic Peptide in Skeletal Myoblasts
    Jonghoe Byun, Suhn Hee Kim, Sung Zoo Kim, Jean‐Michel Heard, Jeoung-Eun Huh, Yoon-Hyuk Choe, Sun-Jin Park, Eun-A Jung, Duk‐Kyung Kim · 2000 · Biochemical and Biophysical Research Communications
  35. Molecular Therapies for the Nervous System and Muscle
    George Karpati · 2003 · Springer eBooks
  36. Genetic Vaccines and Therapy
    Lourdes M. Andino, Thomas J. Conlon, Stacy Porvasnik, Sanford L. Boye, William W. Hauswirth, Alfred S. Lewin · 2015
  37. Adeno-associated Virus and AAV Vectors for Gene Delivery
    Barrie Carter, Haim Burstein, RICHARD W. PELUSO · 2003 · CRC Press eBooks
  38. Gene and cell therapy approaches for the prevention and treatment of ventricular arrhythmias
    Shankar Prasad Parajuli, J. Kevin Donahue · 2020 · Elsevier eBooks
  39. Adeno-Associated Viral Vectors for Clinical Gene Therapy in the Brain
    R. Samulski, J. Giles · 2005 · KARGER eBooks
  40. AAV-MEDIATED GENE TRANSFER TO MODELS OF MUSCULAR DYSTROPHY: INSIGHTS INTO ASSEMBLY OF MULTI-SUBUNIT MEMBRANE PROTEINS.
    Devin C. Dressman · 2002 · D-Scholarship@Pitt (University of Pittsburgh)
  41. Viral-vectored ribozymes as therapy for autosomal dominant retinal disease
    William W. Hauswirth, Matthew M. LaVail, John G. Flannery, Alfred S. Lewin · 2001 · Clinical Neuroscience Research
  42. Thérapie génique des dystrophies musculaires
    Nathalie Vincent · 1999 · Annales de l Institut Pasteur / Actualités
  43. The Development of Approaches Based on Gene Therapy to Improve Muscle Healing Following Injury
    Jacques Ménétrey, Channarong Kasemkijwattana, Charles S. Day, Patrick P. Bosch, Morey S. Moreland, Freddie H. Fu, Johnny Huard · 2000 · Birkhäuser Boston eBooks
  44. Clinical Protocol Phase I Trial of Intramuscular Injection of a Recombinant Adeno-Associated Virus Alpha 1-Antitrypsin (rAAV2-CB-hAAT) Gene Vector to AAT-Deficient Adults
    Terence R. Flotte, Mark Brantly, L. Terry Spencer, Barry J. Byrne, Carolyn T. Spencer, Dawn J. Baker · 2004
  45. Adeno-Associated Virus-Based Vectors
    Nathalie Dutheil, Erwan Bézard · 2013 · Neuromethods
  46. Ylkmsduction of hepatocellular carcinoma @ICC) using recombinant adeno-associated virus (rAA..: in vitro and in viva effwts of genotoxic agents
    Dacheng Peng, Cheng Qian, Yonglian Sun, Miguel Barajas, Jesús Prìeto · 2000
  47. Based on Gene Therapy to Improve Muscle Healing Following Injury
    Jacques Ménétrey, Charles S. Day, Patrick P. Bosch, Morey S. Moreland, Freddie H. Fu, Johnny Huard · 2000
  48. Targeting Gene Therapy to the Tumor Vasculature
    Kelvin K. W. Lau, Roy Bicknell · 2002 · Humana Press eBooks
  49. Faculty Opinions recommendation of Gene therapy restores auditory and vestibular function in a mouse model of Usher syndrome type 1c.
    Levon Michael Khachigian · 2019 · Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
  50. The Use of Different Vectors and Strategies for Gene Transfer to the Musculoskeletal System
    Johnny Huard · 2000 · Birkhäuser Boston eBooks
  51. Adeno—Associated Virus (AAV) Vectors for Musculoskeletal Gene Transfer
    Xiao Xiao, Ryan Pruchnic, Juan Li, Johnny Huard · 2000 · Birkhäuser Boston eBooks
  52. Site-specific integration in mammalian cells mediated by a new hybrid baculovirus-adeno-associated virus vector
    Alessandra Recchia · 1998 · IRIS UNIMORE (University of Modena and Reggio Emilia)
  53. Long-read target enrichment sequencing for rAAV integration site analysis in engineered clones with targeted viral insertion
    Erica Coratella, Myriam Lemmens, Mevion Oertli, Yoann Gilbart, Kristian Davidsen, Lara Bontadelli, Rebecca Bohnert, Joyce Rigal, Jennifer Bian, Tara Alpert et al. · 2026 · Molecular Therapy — Nucleic Acids