Recombinant Adeno-Associated Viral Vectors Mediate Long-Term Transgene Expression in Muscle
Clark, K. Reed, Sferra, Thomas J., Johnson, Philip R.·1997·Human Gene Therapy
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- IGF1 gene transfer into skeletal muscle using recombinant adeno-associated virus in a rat model of liver cirrhosisMikel Zaratiegui, Inma Castilla‐Cortázar, Maria Inmaculada Garcia‐Fernandez, Jorge Augusto Quiroga, Jesús Prìeto, Francisco Javier Novo · 2002 · Journal of Physiology and Biochemistry
- Towards metabolic sink therapy for mut methylmalonic acidaemia: Correction of methylmalonyl‐CoA mutase deficiency in T lymphocytes from a mut methylmalonic acidaemia child by retroviral‐mediated gene transferChun‐che Chang, K J Hsiao, Y.‐M. Lee, C.‐M. Lin · 1999 · Journal of Inherited Metabolic Disease
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- The persistence of alien genomesPeter J. Tattersall · 2000 · Proceedings of the National Academy of Sciences
- Ectopic Expression of Active Processed Form of Atrial Natriuretic Peptide in Skeletal MyoblastsJonghoe Byun, Suhn Hee Kim, Sung Zoo Kim, Jean‐Michel Heard, Jeoung-Eun Huh, Yoon-Hyuk Choe, Sun-Jin Park, Eun-A Jung, Duk‐Kyung Kim · 2000 · Biochemical and Biophysical Research Communications
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- Genetic Vaccines and TherapyLourdes M. Andino, Thomas J. Conlon, Stacy Porvasnik, Sanford L. Boye, William W. Hauswirth, Alfred S. Lewin · 2015
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- Adeno-Associated Viral Vectors for Clinical Gene Therapy in the BrainR. Samulski, J. Giles · 2005 · KARGER eBooks
- AAV-MEDIATED GENE TRANSFER TO MODELS OF MUSCULAR DYSTROPHY: INSIGHTS INTO ASSEMBLY OF MULTI-SUBUNIT MEMBRANE PROTEINS.Devin C. Dressman · 2002 · D-Scholarship@Pitt (University of Pittsburgh)
- Viral-vectored ribozymes as therapy for autosomal dominant retinal diseaseWilliam W. Hauswirth, Matthew M. LaVail, John G. Flannery, Alfred S. Lewin · 2001 · Clinical Neuroscience Research
- Thérapie génique des dystrophies musculairesNathalie Vincent · 1999 · Annales de l Institut Pasteur / Actualités
- The Development of Approaches Based on Gene Therapy to Improve Muscle Healing Following InjuryJacques Ménétrey, Channarong Kasemkijwattana, Charles S. Day, Patrick P. Bosch, Morey S. Moreland, Freddie H. Fu, Johnny Huard · 2000 · Birkhäuser Boston eBooks
- Clinical Protocol Phase I Trial of Intramuscular Injection of a Recombinant Adeno-Associated Virus Alpha 1-Antitrypsin (rAAV2-CB-hAAT) Gene Vector to AAT-Deficient AdultsTerence R. Flotte, Mark Brantly, L. Terry Spencer, Barry J. Byrne, Carolyn T. Spencer, Dawn J. Baker · 2004
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- Site-specific integration in mammalian cells mediated by a new hybrid baculovirus-adeno-associated virus vectorAlessandra Recchia · 1998 · IRIS UNIMORE (University of Modena and Reggio Emilia)
- Long-read target enrichment sequencing for rAAV integration site analysis in engineered clones with targeted viral insertionErica Coratella, Myriam Lemmens, Mevion Oertli, Yoann Gilbart, Kristian Davidsen, Lara Bontadelli, Rebecca Bohnert, Joyce Rigal, Jennifer Bian, Tara Alpert et al. · 2026 · Molecular Therapy — Nucleic Acids