Adeno-Associated Virus Gene Therapy for Liver Disease
Kattenhorn, Lisa M., Tipper, Christopher H., Stoica, Lorelei, Geraghty, Deborah S., Wright, Teresa L., Clark, K. Reed, Wadsworth, Samuel C.·2016·Human Gene Therapy
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- Liver Lymphatic Dysfunction as a Driver of Fibrosis and Cirrhosis ProgressionJain Jeong, Shao‐Jung Hsu, Daiki Horikami, Teruo Utsumi, Yilin Yang, Nikolai Arefyev, Xuchen Zhang, Shi‐Ying Cai, James L. Boyer, Rolando Garcia-Milan et al. · 2025 · bioRxiv (Cold Spring Harbor Laboratory)
- Adeno-Associated virus 8 delivers an immunomodulatory peptide to mouse liver more efficiently than to rat liverYuqing Wang, Ayrea E. Hurley, Marco De Giorgi, Mark R. Tanner, Rong-Chi Hu, Michael W. Pennington, William R. Lagor, Christine Beeton · 2023 · PLoS ONE
- Gene editing: a near future for the treatment of genetic kidney diseasesFernando Gómez-García, Miguel Ángel García-González · 2024 · Kidney International
- Liver Transplantation for Monogenic Metabolic Diseases Involving the KidneyMaurizio Salvadori, Aris Tsalouchos · 2017 · Journal of Renal and Hepatic Disorders
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- APPLICATION OF RADIOISOTOPES AND IONIZING RADIATION FOR INSECT CONTROL.W. Kloft, A. Suess, A. Haisch · 1971 · OSTI OAI (U.S. Department of Energy Office of Scientific and Technical Information)
- Gene TherapyOlga Maslova, Alexander K. Koliada, Alexander M. Vaiserman · 2019 · Elsevier eBooks
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- Faculty Opinions recommendation of Adeno-associated virus vector as a platform for gene therapy delivery.Michael George Fehlings · 2020 · Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
- The Alphaherpesvirus Latency Associated Promoter 2 (LAP2) Drives Strong Transgene Expression in Peripheral Tissue Depending on Administration Route and AAV SerotypeCarola J. Maturana, Angela Chan, Jessica L. Verpeut, Esteban A. Engel · 2022 · bioRxiv (Cold Spring Harbor Laboratory)
- Human Hepatocyte Transduction with Adeno-Associated Virus VectorZhenwei Song, Wenwei Shao, Liujiang Song, Xieolei Pei, Chengwen Li · 2022 · Methods in molecular biology
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- Lipid nanoparticle-mediated delivery of mRNA for IL-21 achieves clearance of hepatitis B virus in mouse modelsZhongliang Shen, Shenyan Zhang, Nannan Liu, Qirong Jiang, Zixiang Gao, Weiju Hao, Qiang Deng, Jing Liu, Jiming Zhang, Youhua Xie · 2023
- Optimizing gene therapy for infant mice with citrullinemia type 1Andrea Bazo · 2023
- Strategies to target and genetically modify the liver sinusoidLara J. Westwood, David George Le Couteur, Nicholas J. Hunt, Victoria Carroll Cogger · 2024 · Elsevier eBooks
- Novel AAV843 Vector-Mediated Gene Replacement Therapy Rescues Primary Hyperoxaluria Type I in MiceJingjia Zhang, Ye Yin, Baowei Ji, Manqing Sun, Yuanyan Jiang, Xiaohui Wu, Xiao Xiao, Qian Shen, Xia Wu, Hong Xu · 2026 · Cells
- Adeno-associated virus in the liver : natural history of the infection and consequences in tumor developmentTiziana La Bella · 2018 · theses.fr (ABES)
- Caractérisation de l’environnement thymique et de la thymopoïèse en conditions physiologiques et dans le contexte de stratégies thérapeutiques par ciblage direct du thymusAlice Machado · 2021
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