Correction of CFTR function in intestinal organoids to guide treatment of cystic fibrosis

Cited by (120)

Items 101–120 of 120

1. In silico and functional characterisation of an ultra-rare CFTR mutation identifies novel lasso motif interactions regulating channel gating
   Sharon L. Wong, Nikhil T Awatade, Miro A. Astore, Katelin M. Allan, Michael J. Carnell, Iveta Šlapetová, Po‐Chia Chen, Alexander Capraro, Laura Katherine Fawcett, Renee Megan Whan et al. · 2021 · bioRxiv (Cold Spring Harbor Laboratory)
2. Lung organoid models
   Martha Rea-Moreno, T. John, YW Chen, Amy L. Ryan · 2022 · Elsevier eBooks
3. Phoenix from the Ashes: Celebrating the 2023 North American Cystic Fibrosis Conference
   Andrew Bush, Bonnie W. Ramsey, Michal Shteinberg, Fernando J. Martínez · 2023 · American Journal of Respiratory and Critical Care Medicine
4. Cystic Fibrosis: a real-world challenge to predict individual outcomes
   Danya Muilwijk · 2023
5. Targeted Therapy for Cystic Fibrosis in Children
   Alla V. Burlutskaya, V. Brisin, Anastasia V. Statova, O. Yu. Zenkina, Yu. V. Pisotskaya · 2023 · Innovative medicine of Kuban
6. The Risk of Developing of Malnutrition and the Principles of Correction of Nutritional Status Disorders in Children with Cystic Fibrosis
   Е. И. Клещенко, Шимченко Елена Васильевна, Aleksander F. Komarov, Valeria E. Kharchenko · 2023 · Педиатрическая фармакология
7. Organoides intestinais como ferramenta para rastreio de moduladores da CFTR na população miscigenada com fibrose cística do Brasil
   Gabriela da Silva Leite · 2021
8. Cystic fibrosis
   Andrew Bush, Caroline M. Elston · 2020
9. CFTR rescue in W1282X cystic fibrosis patient-derived intestinal organoids (PDIOs) mediated by translational readthrough-inducing drugs (TRIDs)
   Riccardo Perriera, Anabela S. Ramalho, François L. Vermeulen, Emanuele Vitale, Ivana Pibiri, Andrea Pace, Laura Lentini · 2025 · Genetics in Medicine Open
10. Author’s Reply to Yang and Wang: “Personalized Medicine in Cystic Fibrosis: Characterization of Eight Rare CFTR Variants in Intestinal Organoids and Cellular Models”
    Margarida Duarte Amaral, Ines Pankonien · 2026 · Molecular Diagnosis & Therapy
11. The organoid revolution to assess mycobacterial pulmonary infections
    Stephen Adonai Leon‐Icaza · 2022
12. Patient‐Derived Intestinal Organoids in the Global Cystic Fibrosis Landscape
    Suzanne Kroes, Jennifer L. Taylor‐Cousar, Marco Zampoli, Bulent Taner Karadag, Cornelis Korstiaan van der Ent, Karin M. de Winter‐de Groot, Jeffrey Matthijn Beekman, Sacha Spelier · 2026 · Pediatric Pulmonology
13. Gene Therapy Against Hereditary Diseases
    Sachin Kumar · 2026 · Springer eBooks
14. Transcriptomic and functional profiling of human intestinal organoids identifies enhanced calcium signalling and thrombospondin-2 activity in cystic fibrosis
    Ellie Slater, Woo Jin Yang, Nefeli Skoufou-Papoutsaki, Stephen A. Renshaw, Róisı́n M. Owens, Matthias Zilbauer · 2026 · Journal of Cystic Fibrosis
15. The role of sweat chloride in determining CFTR protein restoration in people with cystic fibrosis
    Edith T. Zemanick, Simon Y. Graeber, Carlo Castellani, Garry R. Cutting, Isabelle Fajac, Michael W. Konstan, Rachel W. Linnemann, Edward F. McKone, Adam Metcalf, George Marty Solomon et al. · 2026 · The Lancet Respiratory Medicine
16. Combining Gene Therapy with Current Modulator Treatments for Cystic Fibrosis: A Promising Area of Research
    Xavier Buin, Rosy Ghanem, Ines Pankonien, Frédéric Becq, Margarida Duarte Amaral, Tristan Montier · 2026 · Pharmaceutics
17. Modeling inflammation and inflammatory diseases in organoids
    Amber De Moor, Hugo E J Vankelecom, Kaline Arnauts · 2026 · British Medical Bulletin
18. CFTR Functional Rescue and Heterogeneous Clinical Outcomes Following Elexacaftor/Tezacaftor/Ivacaftor Therapy in People with Cystic Fibrosis Carrying the W1282R Variant
    E. Kondratyeva, Anna Sergeevna Efremova, Yuliya L. Melyanovskaya, Elena Zhekaite, Maria Sapelnikova, Michael Milovanov, Olga Shchagina, Anna Voronkova, Victoria Sherman, Stanislav Krasovsky et al. · 2026 · International Journal of Molecular Sciences
19. Challenges in targeted therapy for cystic fibrosis in a patient with the complex allele [L467F; F508del]: from failure of first-line modulator therapy to successful use of vanzacaftor+tezacaftor+deutivacaftor combination
    Anastasia V. Prokopenko, Svetlana I. Petrova, Yu.V. Peshekhonova, Alla A. Kuznetsova · 2026 · PULMONOLOGIYA
20. Theratyping for personalized medicine across cystic fibrosis disease models
    Valentino Bezzerri, Tarini Nawamalie Abeysinghe Gunawardena, Tanja Y. Gonska, Alvin P. Chan, Rasha Salih, Francesca Lucca, Theo J. Moraes, Steven D. Freedman, Marco Cipolli · 2026 · Communications Medicine