Miller, Timothy M.

Amyotrophic lateral sclerosis care and research in the United States during the COVID ‐19 pandemic: Challenges and opportunities

Andrews, J. A., Berry, J. D., Baloh, R. H., Carberry, N., Cudkowicz, M. E., Dedi, B., Glass, J., Maragakis, N. J., Miller, T. M., Paganoni, S., et al. (2020) · Muscle & Nerve

Amyotrophic Lateral Sclerosis ResearchTelemedicine and Telehealth Implementation

Cited by 57

TSC1 loss increases risk for tauopathy by inducing tau acetylation and preventing tau clearance via chaperone-mediated autophagy

Alquezar, C., Schoch, K. M., Geier, E. G., Ramos, E. M., Scrivo, A., Li, K. H., Argouarch, A. R., Mlynarski, E. E., Dombroski, B., DeTure, M., et al. (2021) · Science Advances

Alzheimer's disease research and treatmentsAutophagy in Disease and Therapy

Cited by 56

CNS microRNA profiles: a database for cell type enriched microRNA expression across the mouse central nervous system

Pomper, N., Liu, Y., Hoye, M. L., Dougherty, J. D., & Miller, T. M. (2020) · Scientific Reports

MicroRNA in disease regulationNeuroinflammation and Neurodegeneration Mechanisms

Cited by 39

Design of the First-in-Human study of IONIS-MAPTRx, a Tau-lowering antisense oligonucleotide, in patients with alzheimer disease (S2.006)

Mignon, L., Kordasiewicz, H., Lane, R., Smith, A., Miller, T., Narayanan, P., Swayze, E., Norris, D., Fitzsimmons, B., & Bennett, F. (2018) · Neurology

Alzheimer's disease research and treatmentsDementia and Cognitive Impairment Research

Cited by 29

Elucidating brain transport pathways and cell type-dependent gene silencing of a durable lipid–siRNA conjugate administered into cerebrospinal fluid

Sorets, A. G., Schwensen, K. R., Francini, N., Kjar, A., Abdulrahman, A. M., Shostak, A., Katdare, K. A., Schoch, K. M., Cowell, R. P., Park, J. C., et al. (2025) · Nucleic Acids Research

RNA Interference and Gene DeliveryBarrier Structure and Function Studies

Cited by 6

Lipid-siRNA conjugate accesses a perivascular transport mechanism and achieves widespread and durable knockdown in the central nervous system

Sorets, A., Schwensen, K., Francini, N., Kjar, A., Abdulrahman, A., Shostak, A., Katdare, K., Schoch, K., Cowell, R., Park, J., et al. (2024) · bioRxiv (Cold Spring Harbor Laboratory)

RNA Interference and Gene DeliveryBarrier Structure and Function Studies

Cited by 4