Wong, Brenda

Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne’s Muscular Dystrophy

Lek, A., Wong, B., Keeler, A., Blackwood, M., Ma, K., Huang, S., Sylvia, K., Batista, A. R., Artinian, R., Kokoski, D., et al. (2023) · New England Journal of Medicine

Virus-based gene therapy researchNeurogenetic and Muscular Disorders Research

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Randomized phase 2 trial and open-label extension of domagrozumab in Duchenne muscular dystrophy

Wagner, K. R., Abdel-Hamid, H. Z., Mah, J. K., Campbell, C., Guglieri, M., Muntoni, F., Takeshima, Y., McDonald, C. M., Kostera-Pruszczyk, A., Karachunski, P., et al. (2020) · Neuromuscular Disorders

Muscle Physiology and DisordersNeurogenetic and Muscular Disorders Research

Cited by 67