Azzouz, Mimoun

Systemic Delivery of scAAV9 Expressing SMN Prolongs Survival in a Model of Spinal Muscular Atrophy

Valori, C. F., Ning, K., Wyles, M., Mead, R. J., Grierson, A. J., Shaw, P. J., & Azzouz, M. (2010) · Science Translational Medicine

Neurogenetic and Muscular Disorders ResearchVirus-based gene therapy research

Cited by 285

Dopamine Gene Therapy for Parkinson’s Disease in a Nonhuman Primate Without Associated Dyskinesia

Jarraya, B., Boulet, S., Scott Ralph, G., Jan, C., Bonvento, G., Azzouz, M., Miskin, J. E., Shin, M., Delzescaux, T., Drouot, X., et al. (2009) · Science Translational Medicine

Parkinson's Disease Mechanisms and TreatmentsVirus-based gene therapy research

Cited by 186

Directly converted astrocytes retain the ageing features of the donor fibroblasts and elucidate the astrocytic contribution to human CNS health and disease.

Gatto, N., Dos Santos Souza, C., Shaw, A. C., Bell, S. M., Myszczynska, M. A., Powers, S., Meyer, K., Castelli, L. M., Karyka, E., Mortiboys, H., et al. (2021) · Aging Cell

Pluripotent Stem Cells ResearchNeuroinflammation and Neurodegeneration Mechanisms

Cited by 58

Circumventing the packaging limit of AAV-mediated gene replacement therapy for neurological disorders

Marrone, L., Marchi, P. M., & Azzouz, M. (2022) · Expert Opinion on Biological Therapy

Virus-based gene therapy researchRNA Interference and Gene Delivery

Cited by 56

Delivery of therapeutic AAV9 vectors via cisterna magna to treat neurological disorders

Marchi, P. M., Marrone, L., & Azzouz, M. (2022) · Trends in Molecular Medicine

Virus-based gene therapy researchRNA Interference and Gene Delivery

Cited by 21