Pekrun, Katja

Bioengineered AAV Capsids with Combined High Human Liver Transduction In Vivo and Unique Humoral Seroreactivity

Paulk, N. K., Pekrun, K., Zhu, E., Nygaard, S., Li, B., Xu, J., Chu, K., Leborgne, C., Dane, A. P., Haft, A., et al. (2018) · Molecular Therapy

Virus-based gene therapy researchRNA Interference and Gene Delivery

Cited by 161

Selection of rAAV vectors that cross the human blood-brain barrier and target the central nervous system using a transwell model

Song, R., Pekrun, K., Khan, T. A., Zhang, F., Paşca, S. P., & Kay, M. A. (2022) · Molecular Therapy - Methods & Clinical Development

Virus-based gene therapy researchBarrier Structure and Function Studies

Cited by 36

AAV-mediated genome editing is influenced by the formation of R-loops

Puzzo, F., Crossley, M. P., Goswami, A., Zhang, F., Pekrun, K., Garzon, J. L., Cimprich, K. A., & Kay, M. A. (2024) · Molecular Therapy

Virus-based gene therapy researchCRISPR and Genetic Engineering

Cited by 4

AAV-mediated genome editing is influenced by the formation of R-loops

Puzzo, F., Crossley, M. P., Goswami, A., Zhang, F., Pekrun, K., Garzon, J. L., Cimprich, K. A., & Kay, M. A. (2024) · Molecular Therapy

Virus-based gene therapy researchCRISPR and Genetic Engineering

Cited by 4