Hartman, Heather A.

In utero CRISPR-mediated therapeutic editing of metabolic genes

Rossidis, A. C., Stratigis, J. D., Chadwick, A. C., Hartman, H. A., Ahn, N. J., Li, H., Singh, K., Coons, B. E., Li, L., Lv, W., et al. (2018) · Nature Medicine

CRISPR and Genetic EngineeringVirus-based gene therapy research

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In utero gene editing for monogenic lung disease

Alapati, D., Zacharias, W. J., Hartman, H. A., Rossidis, A. C., Stratigis, J. D., Ahn, N. J., Coons, B., Zhou, S., Li, H., Singh, K., et al. (2019) · Science Translational Medicine

CRISPR and Genetic EngineeringVirus-based gene therapy research

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In utero adenine base editing corrects multi-organ pathology in a lethal lysosomal storage disease

Bose, S. K., White, B. M., Kashyap, M. V., Dave, A., De Bie, F. R., Li, H., Singh, K., Menon, P., Wang, T., Teerdhala, S., et al. (2021) · Nature Communications

Lysosomal Storage Disorders ResearchVirus-based gene therapy research

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