Tolar, Jakub

Bone Marrow Transplantation for Recessive Dystrophic Epidermolysis Bullosa

Wagner, J. E., Ishida-Yamamoto, A., McGrath, J. A., Hordinsky, M., Keene, D. R., Woodley, D. T., Chen, M., Riddle, M. J., Osborn, M. J., Lund, T., et al. (2010) · New England Journal of Medicine

Skin and Cellular Biology ResearchHematopoietic Stem Cell Transplantation

Cited by 374

Outcomes after allogeneic hematopoietic cell transplantation for childhood cerebral adrenoleukodystrophy: the largest single-institution cohort report

Miller, W. P., Rothman, S. M., Nascene, D., Kivisto, T., DeFor, T. E., Ziegler, R. S., Eisengart, J., Leiser, K., Raymond, G., Lund, T. C., et al. (2011) · Blood

Lysosomal Storage Disorders ResearchMetabolism and Genetic Disorders

Cited by 290

TALEN-based Gene Correction for Epidermolysis Bullosa

Osborn, M. J., Starker, C. G., McElroy, A. N., Webber, B. R., Riddle, M. J., Xia, L., DeFeo, A. P., Gabriel, R., Schmidt, M., Von Kalle, C., et al. (2013) · Molecular Therapy

CRISPR and Genetic EngineeringVirus-based gene therapy research

Cited by 258

Evaluation of TCR Gene Editing Achieved by TALENs, CRISPR/Cas9, and megaTAL Nucleases

Osborn, M. J., Webber, B. R., Knipping, F., Lonetree, C.-L., Tennis, N., DeFeo, A. P., McElroy, A. N., Starker, C. G., Lee, C., Merkel, S., et al. (2016) · Molecular Therapy

CRISPR and Genetic EngineeringCAR-T cell therapy research

Cited by 201

Induced Pluripotent Stem Cells from Individuals with Recessive Dystrophic Epidermolysis Bullosa

Tolar, J., Xia, L., Riddle, M. J., Lees, C. J., Eide, C. R., McElmurry, R. T., Titeux, M., Osborn, M. J., Lund, T. C., Hovnanian, A., et al. (2011) · Journal of Investigative Dermatology

Pluripotent Stem Cells ResearchSkin and Cellular Biology Research

Cited by 155

Rapid Induction of Cerebral Organoids From Human Induced Pluripotent Stem Cells Using a Chemically Defined Hydrogel and Defined Cell Culture Medium

Lindborg, B. A., Brekke, J. H., Vegoe, A. L., Ulrich, C. B., Haider, K. T., Subramaniam, S., Venhuizen, S. L., Eide, C. R., Orchard, P. J., Chen, W., et al. (2016) · Stem Cells Translational Medicine

Pluripotent Stem Cells ResearchNeurogenesis and neuroplasticity mechanisms

Cited by 141

Leukotriene-receptor inhibition for the treatment of systemic mastocytosis

Tolar, J., Tope, W. D., & Neglia, J. P. (2004) · New England Journal of Medicine

Mast cells and histamineHistiocytic Disorders and Treatments

Cited by 70

Modeling and rescue of defective blood–brain barrier function of induced brain microvascular endothelial cells from childhood cerebral adrenoleukodystrophy patients

Lee, C. A. A., Seo, H. S., Armien, A. G., Bates, F. S., Tolar, J., & Azarin, S. M. (2018) · Fluids and Barriers of the CNS

Barrier Structure and Function StudiesDrug Transport and Resistance Mechanisms

Cited by 52

Early diagnosis of cerebral X-linked adrenoleukodystrophy in boys with Addison’s disease improves survival and neurological outcomes

Polgreen, L. E., Chahla, S., Miller, W., Rothman, S., Tolar, J., Kivisto, T., Nascene, D., Orchard, P. J., & Petryk, A. (2011) · European Journal of Pediatrics

Lysosomal Storage Disorders ResearchMetabolism and Genetic Disorders

Cited by 49