Makkia, Rasha

DNA nanoparticle-mediated ABCA4 delivery rescues Stargardt dystrophy in mice

Han, Z., Conley, S. M., Makkia, R. S., Cooper, M. J., & Naash, M. I. (2012) · Journal of Clinical Investigation

Retinal Development and DisordersRNA Interference and Gene Delivery

Cited by 150

S/MAR-containing DNA nanoparticles promote persistent RPE gene expression and improvement in RPE65-associated LCA

Koirala, A., Makkia, R. S., Conley, S. M., Cooper, M. J., & Naash, M. I. (2013) · Human Molecular Genetics

RNA Interference and Gene DeliveryRetinal Development and Disorders

Cited by 75

Genomic DNA nanoparticles rescue rhodopsin-associated retinitis pigmentosa phenotype

Han, Z., Banworth, M. J., Makkia, R., Conley, S. M., Al‐Ubaidi, M. R., Cooper, M. J., & Naash, M. I. (2015) · The FASEB Journal

Retinal Development and DisordersRNA Interference and Gene Delivery

Cited by 54

Increased cone sensitivity to ABCA4 deficiency provides insight into macular vision loss in Stargardt's dystrophy

Conley, S. M., Cai, X., Makkia, R., Wu, Y., Sparrow, J. R., & Naash, M. I. (2012) · Biochimica et Biophysica Acta (BBA) - Molecular Basis of Disease

Retinal Development and DisordersRetinal Diseases and Treatments

Cited by 54

Persistence of non-viral vector mediated RPE65 expression: Case for viability as a gene transfer therapy for RPE-based diseases

Koirala, A., Conley, S. M., Makkia, R., Liu, Z., Cooper, M. J., Sparrow, J. R., & Naash, M. I. (2013) · Journal of Controlled Release

Retinal Development and DisordersRNA Interference and Gene Delivery

Cited by 47