Highly Efficient Genome Editing of Murine and Human Hematopoietic Progenitor Cells by CRISPR/Cas9

Gundry, Michael C., Brunetti, Lorenzo, Lin, Angelique, Mayle, Allison E., Kitano, Ayumi, Wagner, Dimitrios, Hsu, Joanne I., Hoegenauer, Kevin A. +3 more·2016·Cell Reports

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  38. Therapeutic gene editing in hematopoietic progenitor cells from a mouse model of Fanconi anemia
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  39. Enhancing the Efficiency of CRISPR/Cas9 Precise Gene Editing for Cystic Fibrosis Gene Therapy
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  40. Measure Twice, Cut Once: Therapeutic Editing of HSPCs Requires Precise Planning
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  44. Efficient repair of human homozygous genetic mutation by CRISPR/Cas9 mediated interlocus gene conversion
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  56. Additional file 2 of The histone methyltransferase Setd8 alters the chromatin landscape and regulates the expression of key transcription factors during erythroid differentiation
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