Highly Efficient Genome Editing of Murine and Human Hematopoietic Progenitor Cells by CRISPR/Cas9
Gundry, Michael C., Brunetti, Lorenzo, Lin, Angelique, Mayle, Allison E., Kitano, Ayumi, Wagner, Dimitrios, Hsu, Joanne I., Hoegenauer, Kevin A. +3 more·2016·Cell Reports
Cited by (264)
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- Stress hematopoiesis induces a proliferative advantage in TET2 deficiencyVinothkumar Rajan, Keon Collett, Rachel Woodside, Sergey V. Prykhozhij, Michelle Moksa, Annaïck Carles, Marcus Wong, Mira F. Liebman, Martin Hirst, Jason N. Berman · 2021 · Leukemia
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- Noncoding RNA and Epigenetic Change in Hematopoietic Stem Cell AgingDavid Garrick, Antoine David, Christelle Freitas, Dounia Djeghloul, Michèle Goodhardt · 2019 · Springer eBooks
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- Hacking hematopoiesis – emerging tools for examining variant effectsMichael C. Gundry, Vijay G. Sankaran · 2023 · Disease Models & Mechanisms
- Gene Editing in Hematopoietic Stem CellsJiaoyang Liao, Yuxuan Wu · 2023 · Advances in experimental medicine and biology
- Gentherapie von Hämoglobinkrankheiten – aktuelle Konzepte und HerausforderungenAndreas E. Kulozik, Joachim B. Kunz · 2019 · Transfusionsmedizin
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- Correction of Griscelli Syndrome Type 2 causing mutations in the RAB27A gene with CRISPR/Cas9Özgür Doğuş Erol, Şimal Şenocak, Burcu Özçimen, Gülen Güney-Esken, Hasan Basri Kılıç, Çetin Kocaefe, Niek Peter van Til, Fatima Aerts‐Kaya · 2024 · TURKISH JOURNAL OF BIOLOGY
- Noncoding RNA and Epigenetic Change in Hematopoietic Stem Cell AgingDavid Garrick, Antoine David, Christelle Freitas, Dounia Djeghloul, Michèle Goodhardt · 2017 · Springer eBooks
- Therapeutic gene editing in hematopoietic progenitor cells from a mouse model of Fanconi anemiaMaría José Pino-Barrio, Yari A. Gimenez, M Villanueva, Marcus Hildenbeutel, Rebeca Sánchez‐Domínguez, Sandra Rodríguez, Roser M. Pujol, Jordi Surrallés, Paula Rı́o, Toni Cathomen et al. · 2018 · bioRxiv (Cold Spring Harbor Laboratory)
- Enhancing the Efficiency of CRISPR/Cas9 Precise Gene Editing for Cystic Fibrosis Gene TherapyKyle E. Seigel · 2018 · TSpace (University of Toronto)
- Measure Twice, Cut Once: Therapeutic Editing of HSPCs Requires Precise PlanningRachel E. Rau, Margaret A. Goodell · 2019 · Cell stem cell
- Optimized guide RNA selection recommendations for using sp Cas9 gene editing in human hematopoietic stem and progenitor cellsHan J. M. P. Verhagen, Carlijn Kuijk, Anne M. Kokke, Laurens Rutgers, Santhe A. van der Meulen, Gerard J. van Mierlo, Carlijn Voermans, Emile van den Akker · 2020 · bioRxiv (Cold Spring Harbor Laboratory)
- Engineered stem cells combine stem cell and gene therapy approaches to move intestine therapy from bench to bedMahmoud Shaaban Mohamed, Mahmoud I. Elbadry, Chao‐Ling Yao · 2021 · Elsevier eBooks
- Investigation of the Transcriptional Role of a RUNX1 Intronic Silencer by CRISPR/Cas9 Ribonucleoprotein in Acute Myeloid Leukemia CellsChi‐Keung Cheng, Terry H. Y. Wong, Yuk‐Lin Yung, Nelson C. N. Chan, Margaret H.L. Ng · 2019 · Journal of Visualized Experiments
- Efficient repair of human homozygous genetic mutation by CRISPR/Cas9 mediated interlocus gene conversionFei Yang, Jingtao Pang, Guolong Liu, Yang Yang, Shenguang Qin, Ying Zhang, Yongrong Lai, Dan Liang, Yuxuan Wu · 2022 · bioRxiv (Cold Spring Harbor Laboratory)
- Genome Editing to Abrogate Muscle AtrophyTingting Yang, Priyanka Gokulnath, Xinxiu Meng, Guoping Li, Junjie Xiao · 2022 · Advances in experimental medicine and biology
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- Reactivate expression of fetal hemoglobin In CD34+ primary adult erythroid cells by gene therapyNetchanok Leela-adisorn · 2016
- CRISPR/Cas9 gene editing for treating gene and protein disordersChukwuebuka Emmanuel Umeyor, Preeya Negi, Riya Agarwal, Sonali Nitin Hanjankar, Vandana Bharat Patravale · 2025 · Elsevier eBooks
- Establishment of a Reverse Genetics System for the Study of Human Immune Functions in MicePriya Pal, Shuai Gao, Hongbo Gao, Marina Cella, Qiankun Wang, Liang Shan · 2025 · bioRxiv (Cold Spring Harbor Laboratory)
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- Additional file 4 of The histone methyltransferase Setd8 alters the chromatin landscape and regulates the expression of key transcription factors during erythroid differentiationMyers, Jacquelyn A., Couch, Tyler, Zachary C. Murphy, Jeffrey T. Malik, Michael R. Getman, Laurie A. Steiner · 2020 · Figshare
- Additional file 3 of The histone methyltransferase Setd8 alters the chromatin landscape and regulates the expression of key transcription factors during erythroid differentiationMyers, Jacquelyn A., Couch, Tyler, Zachary C. Murphy, Jeffrey T. Malik, Michael R. Getman, Laurie A. Steiner · 2020 · Figshare
- Additional file 1 of The histone methyltransferase Setd8 alters the chromatin landscape and regulates the expression of key transcription factors during erythroid differentiationMyers, Jacquelyn A., Couch, Tyler, Zachary C. Murphy, Jeffrey T. Malik, Michael R. Getman, Laurie A. Steiner · 2020 · Figshare
- Additional file 2 of The histone methyltransferase Setd8 alters the chromatin landscape and regulates the expression of key transcription factors during erythroid differentiationMyers, Jacquelyn A., Couch, Tyler, Zachary C. Murphy, Jeffrey T. Malik, Michael R. Getman, Laurie A. Steiner · 2020 · Figshare
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