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Efficacy of adeno-associated virus gene therapy in a MNGIE murine model enhanced by chronic exposure to nucleosides

Vila-Julià, Ferran, Cabrera-Pérez, Raquel, Cámara, Yolanda, Molina-Berenguer, Miguel, Lope-Piedrafita, Silvia, Hirano, Michio, Mingozzi, Federico, Torres-Torronteras, Javier, Martí, Ramon·2020·eBioMedicine
DOI 10.1016/j.ebiom.2020.103133PMC PMC7689515
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Metadata

Authors
Vila-Julià, F., Cabrera-Pérez, R., Cámara, Y., Molina-Berenguer, M., Lope-Piedrafita, S., Hirano, M., Mingozzi, F., Torres-Torronteras, J., & Martí, R.
Venue
eBioMedicine
Publisher
Elsevier BV
Published
2020-12
Volume
62
Pages
103133
ISSN
2352-3964
DOI
10.1016/j.ebiom.2020.103133
PMC
PMC7689515
Cited by
22
References
5
Language
en
Licence
Funders
  • Generalitat de Catalunya (2018FI_B_01115, SLT002/16/00370)
  • Instituto de Salud Carlos III (PI15/00465, PI18/01574, PMP15/00025)

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