Human ES- and iPS-Derived Myogenic Progenitors Restore DYSTROPHIN and Improve Contractility upon Transplantation in Dystrophic Mice

Darabi, Radbod, Arpke, Robert W., Irion, Stefan, Dimos, John T., Grskovic, Marica, Kyba, Michael, Perlingeiro, Rita C.R.·2012·Cell Stem Cell

DOI 10.1016/j.stem.2012.02.015

Cited by (481)

Items 101–200 of 481

Advanced models of human skeletal muscle differentiation, development and disease: Three-dimensional cultures, organoids and beyond
Salma Jalal, Sumitava Dastidar, Francesco Saverio Tedesco · 2021 · Current Opinion in Cell Biology
Directed Differentiation of Pluripotent Stem Cells by Transcription Factors.
Yujeong Oh, Jiwon Jang · 2019 · Europe PMC (PubMed Central)
3D human induced pluripotent stem cell–derived bioengineered skeletal muscles for tissue, disease and therapy modeling
Luca Pinton, Moustafa Khedr, Valentina Maria Lionello, Shilpita Sarcar, Sara Martina Maffioletti, Sumitava Dastidar, Elisa Négroni, SungWoo Choi, Noreen Khokhar, Anne Bigot et al. · 2023 · Nature Protocols
Hedgehog Signaling Regulates MyoD Expression and Activity
Anastassia Voronova, Erin M. Coyne, Ashraf Said Al Madhoun, Joel Fair, Neven Bosiljcic, Catherine St‐Louis, Grace Li, Sherry Thurig, Valerie A. Wallace, Nadine Wiper‐Bergeron et al. · 2012 · Journal of Biological Chemistry
Physiology and Metabolism of Tissue Engineered Skeletal Muscle
Cindy S. Cheng, B. Davis, Lauran R. Madden, N. Bursac, G. Truskey · 2014 · Experimental biology and medicine
Repair or replace? Exploiting novel gene and cell therapy strategies for muscular dystrophies
Sara Benedetti, Hidetoshi Hoshiya, Francesco Saverio Tedesco · 2013 · FEBS Journal
Gene Correction of LGMD2A Patient-Specific iPSCs for the Development of Targeted Autologous Cell Therapy
Sridhar Selvaraj, Neha R. Dhoke, James Kiley, Alba Judith Mateos-Aierdi, Sudheer K. Tungtur, Ricardo Mondragón-González, Grace Killeen, Vanessa K.P. Oliveira, Adolfo López de Munaín, Rita C. R. Perlingeiro · 2019 · Molecular Therapy
Transient ectopic expression of the histone demethylase JMJD3 accelerates the differentiation of human pluripotent stem cells
Tomohiko Akiyama, Shunichi Wakabayashi, Atsumi Soma, Saeko Sato, Yuhki Nakatake, Mayumi Oda, Miyako Murakami, Miki Sakota, Nana Chikazawa-Nohtomi, Shigeru B. H. Ko et al. · 2016 · Development
The Importance of Biophysical and Biochemical Stimuli in Dynamic Skeletal Muscle Models
Babette Maleiner, Janine Tomasch, Philipp Heher, Oliver Spadiut A, Dominik Rünzler, Christiane Fuchs · 2018 · Frontiers in Physiology
Organotypic and Microphysiological Human Tissue Models for Drug Discovery and Development—Current State-of-the-Art and Future Perspectives
Sonia C. Youhanna, Aurino M. Kemas, Lena C. Preiss, Yitian Zhou, Joanne X. Shen, Selgin D. Cakal, Francesco S. Paqualini, Sravan Kumar Goparaju, Reza Zandi Shafagh, Johan Ulrik Lind et al. · 2022 · Pharmacological Reviews
Pax7 remodels the chromatin landscape in skeletal muscle stem cells
Karin C. Lilja, Nan Zhang, Alessandro Magli, Volkan Gündüz, Christopher J. Bowman, Robert W. Arpke, Radbod Darabi, Michael Kyba, Rita C. R. Perlingeiro, Brian David Dynlacht · 2017 · PLoS ONE
Direct reprogramming of fibroblasts into skeletal muscle progenitor cells by transcription factors enriched in undifferentiated subpopulation of satellite cells
Naoki Ito, Isao Kii, Noriaki Shimizu, Hirotoshi Tanaka, Shin’ichi Takeda · 2017 · Scientific Reports
iPSCs as a Platform for Disease Modeling, Drug Screening, and Personalized Therapy in Muscular Dystrophies
Jose L Ortiz-Vitali, Radbod Darabi · 2019 · Cells
Synergizing Engineering and Biology to Treat and Model Skeletal Muscle Injury and Disease
Nenad Bursac, Mark E. Juhas, Thomas A. Rando · 2015 · Annual Review of Biomedical Engineering
Premyogenic progenitors derived from human pluripotent stem cells expand in floating culture and differentiate into transplantable myogenic progenitors
Fusako Sakai‐Takemura, Asako Narita, Satoru Masuda, Toshifumi Wakamatsu, Nobuharu Watanabe, Takashi Nishiyama, Kenichiro Nogami, Matthias Blanc, Shin’ichi Takeda, Yuko Miyagoe‐Suzuki · 2018 · Scientific Reports
Human skeletal muscle organoids model fetal myogenesis and sustain uncommitted PAX7 myogenic progenitors
Lampros Mavrommatis, Hyun‐Woo Jeong, Urs Kindler, Gemma Gomez‐Giro, Marie‐Cécile Kienitz, Martin Stehling, Olympia Ekaterini Psathaki, Dagmar Zeuschner, Maria Gabriele Bixel, Dong Han et al. · 2023 · eLife
Induced Fetal Human Muscle Stem Cells with High Therapeutic Potential in a Mouse Muscular Dystrophy Model
Mingming Zhao, Atsutoshi Tazumi, Satoru Takayama, Nana Takenaka-Ninagawa, Minas Nalbandian, Miki Nagai, Yumi Nakamura, Masanori Nakasa, Akira Watanabe, Makoto Ikeya et al. · 2020 · Stem Cell Reports
Cell therapy in muscular dystrophies: many promises in mice and dogs, few facts in patients
Daniel Skuk, Jacques P. Tremblay · 2015 · Expert Opinion on Biological Therapy
Invited review: Stem cells and muscle diseases: advances in cell therapy strategies
Elisa Négroni, Teresa Gidaro, Anne Bigot, Gillian Sandra Butler-Browne, Vincent Mouly, Capucine Trollet · 2014 · Neuropathology and Applied Neurobiology
Pluripotent stem cell derived cardiovascular progenitors – A developmental perspective
Matthew J. Birket, Christine L. Mummery · 2015 · Developmental Biology
Coaxing stem cells for skeletal muscle repair
Karl J. A. McCullagh, Rita C. R. Perlingeiro · 2014 · Advanced Drug Delivery Reviews
Differentiation and sarcomere formation in skeletal myocytes directly prepared from human induced pluripotent stem cells using a sphere-based culture
Nunnapas Jiwlawat, Eileen M. Lynch, Jennifer Glaser, Ivy M. Smit-Oistad, Jeremy I. Jeffrey, Jonathan M. Van Dyke, Masatoshi Suzuki · 2017 · Differentiation
A Novel Protocol for Directed Differentiation of C9orf72-Associated Human Induced Pluripotent Stem Cells Into Contractile Skeletal Myotubes
Elliot W. Swartz, Jaeyun Baek, Mochtar Pribadi, Kevin J. Wojta, Sandra Almeida, Anna Karydas, Fen‐Biao Gao, Bruce L. Miller, Giovanni Coppola · 2016 · Stem Cells Translational Medicine
Directed Myogenic Differentiation of Human Induced Pluripotent Stem Cells
Emi Shoji, Knut Woltjen, Hidetoshi Sakurai · 2015 · Methods in molecular biology
Pluripotent stem cell-derived myogenic progenitors remodel their molecular signature upon in vivo engraftment
Tania Incitti, Alessandro Magli, Radbod Darabi, Ce Yuan, Karena Lin, Robert W. Arpke, Karim Azzag, Ami Yamamoto, Ron M. Stewart, James Alexander Thomson et al. · 2019 · Proceedings of the National Academy of Sciences
Mechanisms of Skeletal Muscle Atrophy and Molecular Circuitry of Stem Cell Fate in Skeletal Muscle Regeneration and Aging
Sue C. Bodine, Indranil Sinha, Hugh Lee Sweeney · 2023 · The Journals of Gerontology Series A
Isolation, characterization, and molecular regulation of muscle stem cells
So‐ichiro Fukada, Yuran Ma, Takuji Ohtani, Yoko Watanabe, Satoshi Murakami, Masahiko Yamaguchi · 2013 · Frontiers in Physiology
Adult Stem Cells and Skeletal Muscle Regeneration
Domiziana Costamagna, Emanuele Berardi, Gabriele Ceccarelli, Maurilio Sampaolesi · 2015 · Current Gene Therapy
Highly contractile 3D tissue engineered skeletal muscles from human iPSCs reveal similarities with primary myoblast-derived tissues
Erik van der Wal, Alessandro Iuliano, Stijn L.M. in ‘t Groen, Anjali P. Bholasing, Dominik Priesmann, Preeti Sharma, Bianca den Hamer, Vittorio Saggiomo, Marcus Krüger, W.W.M. Pim Pijnappel et al. · 2023 · Stem Cell Reports
Stem Cell Differentiation Toward the Myogenic Lineage for Muscle Tissue Regeneration: A Focus on Muscular Dystrophy
S. Ostrovidov, X. Shi, R. B. Sadeghian, S. Salehi, T. Fujie, Hojae Bae, M. Ramalingam, A. Khademhosseini · 2015 · Stem Cell Reviews and Reports
Improvement of ventilator-induced lung injury by IPS cell-derived conditioned medium via inhibition of PI3K/Akt pathway and IP-10-dependent paracrine regulation
Li‐Fu Li, Yung-Yang Liu, Cheng‐Ta Yang, Yueh Chien, Nae-Fang Twu, Mong‐Lien Wang, Chien‐Ying Wang, Chung-Chi Huang, Kuo‐Chin Kao, Han‐Shui Hsu et al. · 2012 · Biomaterials
Engineered matrices for skeletal muscle satellite cell engraftment and function
Woojin M. Han, Young Charles Jang, Andrés J. Garcı́a · 2016 · Matrix Biology
Long-term engraftment of myogenic progenitors from adipose-derived stem cells and muscle regeneration in dystrophic mice
Yu Zhang, Yuling Zhu, Yaqin Li, Jiqing Cao, Huili Zhang, Menglong Chen, Liang Wang, Cheng Zhang · 2015 · Human Molecular Genetics
Physiological and ultrastructural features of human induced pluripotent and embryonic stem cell-derived skeletal myocytes in vitro
G. Skoglund, J. Lainé, Radbod Darabi, E. Fournier, R. Perlingeiro, N. Tabti · 2014 · Proceedings of the National Academy of Sciences of the United States of America
Nanotopography-responsive myotube alignment and orientation as a sensitive phenotypic biomarker for Duchenne Muscular Dystrophy
Bin Xu, Alessandro Magli, Yoska Anugrah, Steven J. Koester, Rita C. R. Perlingeiro, Wei Shen · 2018 · Biomaterials
Transcriptional landscape of myogenesis from human pluripotent stem cells reveals a key role of TWIST1 in maintenance of skeletal muscle progenitors
In Young Choi, Hotae Lim, Hyeon Jin Cho, Yohan Oh, Bin-Kuan Chou, Hao Bai, Linzhao Cheng, Yong Jun Kim, Sang‐Hwan Hyun, Hyesoo Kim et al. · 2020 · eLife
Acute conversion of patient-derived Duchenne muscular dystrophy iPSC into myotubes reveals constitutive and inducible over-activation of TGFβ-dependent pro-fibrotic signaling
Luca Caputo, Alice Granados, Jessica Lenzi, Alessandro Rosa, Slimane Ait‐Si‐Ali, Prem Puri, Sonia Albini · 2020 · Skeletal Muscle
Generation of a Functioning and Self-Renewing Diaphragmatic Muscle Construct
Caterina Trevisan, Mario Enrique Alvarèz Fallas, Edoardo Maghin, Chiara Franzin, Piero G. Pavan, Paola Caccin, Angela Chiavegato, Eugenia Carraro, Daniele Boso, Francesco Boldrin et al. · 2019 · Stem Cells Translational Medicine
Directed In Vitro Myogenesis of Human Embryonic Stem Cells and Their In Vivo Engraftment
Yongsung Hwang, S. Suk, Susan Lin, Matthew T. Tierney, Bin Du, T. Seo, Aaron Mitchell, A. Sacco, S. Varghese · 2013 · PLoS ONE
Human induced pluripotent stem cell models for the study and treatment of Duchenne and Becker muscular dystrophies
Daniela Piga, Sabrina Salani, Francesca Magri, Roberta Brusa, Eleonora Mauri, Giacomo P. Comi, Nereo Bresolin, Stefania Paola Corti · 2019 · Therapeutic Advances in Neurological Disorders
Micropatterned substrates with physiological stiffness promote cell maturation and Pompe disease phenotype in human induced pluripotent stem cell‐derived skeletal myocytes
Nunnapas Jiwlawat, Eileen M. Lynch, Brett N. Napiwocki, Alana Stempien, Randolph Scott Ashton, Timothy J. Kamp, Wendy C. Crone, Masatoshi Suzuki · 2019 · Biotechnology and Bioengineering
Sources for skeletal muscle repair: from satellite cells to reprogramming
Dario Sirabella, Luciana De Angelis, Libera Berghella · 2013 · Journal of Cachexia Sarcopenia and Muscle
WNT3A promotes myogenesis of human embryonic stem cells and enhances in vivo engraftment
Yongsung Hwang, Samuel Suk, Yu-Ru Vernon Shih, Timothy Seo, Bin Du, Yun Xie, Ziyang Li, Shyni Varghese · 2014 · Scientific Reports
Highly Efficient Derivation of Skeletal Myotubes from Human Embryonic Stem Cells
Lingjun Rao, Wenjie Tang, Youzhen Wei, Lei Bao, Ji‐Jun Chen, Haide Chen, Lixiazi He, Pengfei Lu, Jiangtao Ren, Lu Han Wu et al. · 2012 · Stem Cell Reviews and Reports
Physical regulation of stem cells differentiation into teno-lineage: current strategies and future direction
Jialin Chen, Wei Zhang, Ze Yu Liu, Boon Chin Heng, Hong Wei Ouyang, Xue Song Dai · 2014 · Cell and Tissue Research
Skeletal Muscle Regenerative Engineering
Xiaoyan Tang, Leila Daneshmandi, Guleid M. Awale, Lakshmi S. Nair, Cato T. Laurencin · 2019 · Regenerative Engineering and Translational Medicine
Neuromuscular Development and Disease: Learning From in vitro and in vivo Models
Zachary Fralish, Ethan M. Lotz, Taylor Chavez, Alastair Khodabukus, Nenad Bursac · 2021 · Frontiers in Cell and Developmental Biology
Concise Review: Stem Cell Therapy for Muscular Dystrophies
Karlijn J. Wilschut, Vivian B. Ling, Harold S. Bernstein · 2012 · Stem Cells Translational Medicine
Characterization of hiPSC-Derived Muscle Progenitors Reveals Distinctive Markers for Myogenic Cell Purification Toward Cell Therapy
Minas Nalbandian, Mingming Zhao, Mitsuru Sasaki‐Honda, Tatsuya Jonouchi, Antonio Lucena-Cacace, Takuma Mizusawa, Masahiko Yasuda, Yoshinori Yoshida, Akitsu Hotta, Hidetoshi Sakurai · 2021 · Stem Cell Reports
mRNA-mediated delivery of gene editing tools to human primary muscle stem cells
Christian Stadelmann, Silvia Di Francescantonio, Andreas Marg, Stefanie Müthel, Simone Spuler, Helena Escobar · 2022 · Molecular Therapy — Nucleic Acids
Skeletal myogenic differentiation of human urine-derived cells as a potential source for skeletal muscle regeneration
Wei Chen, Minkai Xie, Bin Yang, Shantaram Bharadwaj, Lujie Song, Guihua Liu, Shanhong Yi, Gang Ye, Anthony Atala, Yuanyuan Zhang · 2014 · Journal of Tissue Engineering and Regenerative Medicine
Sdf-1 (CXCL12) induces CD9 expression in stem cells engaged in muscle regeneration
Edyta Brzóska, Kamil Kowalski, Agnieszka Markowska‐Zagrajek, Magdalena Kowalewska, Rafał Archacki, Izabela Plaskota, Władysława Stremińska, Katarzyna Jańczyk‐Ilach, Maria A. Ciemerych · 2015 · Stem Cell Research & Therapy
rAAV-Mediated Tumorigenesis: Still Unresolved After an AAV Assault
Paul N. Valdmanis, Leszek Lisowski, Mark A. Kay · 2012 · Molecular Therapy
Satellite cell therapy – from mice to men
Akshay Bareja, Andrew N. Billin · 2013 · Skeletal Muscle
Nkx2-5 Mediates Differential Cardiac Differentiation Through Interaction with Hoxa10
Ann N. Behrens, Michelina Iacovino, Jamie L. Lohr, Yi Ren, Claudia Zierold, Richard Paul Harvey, Michael Kyba, Daniel J. Garry, Cindy M. Martin · 2013 · Stem Cells and Development
Time-dependent Pax3-mediated chromatin remodeling and cooperation with Six4 and Tead2 specify the skeletal myogenic lineage in developing mesoderm
Alessandro Magli, June Baik, Lauren J. Mills, Il‐Youp Kwak, Bridget S. Dillon, Ricardo Mondragón-González, David A. Stafford, Scott Allen Swanson, Ron M. Stewart, James Alexander Thomson et al. · 2019 · PLoS Biology
Genomic Safe Harbor Expression of PAX7 for the Generation of Engraftable Myogenic Progenitors
Hyunkee Kim, Sridhar Selvaraj, James Kiley, Karim Azzag, Bayardo I. Garay, Rita C. R. Perlingeiro · 2020 · Stem Cell Reports
Therapy of Genetic Disorders: Novel Therapies for Duchenne Muscular Dystrophy
Jane T. Seto, Niclas E. Bengtsson, Jeffrey S. Chamberlain · 2014 · Current Pediatrics Reports
Dystrophin Cardiomyopathies: Clinical Management, Molecular Pathogenesis and Evolution towards Precision Medicine
Domenico D’Amario, Aoife Gowran, Francesco Canonico, Elisa Castiglioni, Davide Rovina, Rosaria Santoro, Pietro Spinelli, Rachele Adorisio, Antonio Amodeo, Gianluca Lorenzo Perrucci et al. · 2018 · Journal of Clinical Medicine
Myogenic progenitor specification from pluripotent stem cells
Alessandro Magli, Rita C. R. Perlingeiro · 2017 · Seminars in Cell and Developmental Biology
Nutraceuticals and Their Potential to Treat Duchenne Muscular Dystrophy: Separating the Credible from the Conjecture
K. Woodman, C. Coles, S. Lamandé, J. White · 2016 · Nutrients
Reversible immortalisation enables genetic correction of human muscle progenitors and engineering of next‐generation human artificial chromosomes for Duchenne muscular dystrophy
Sara Benedetti, Narumi Uno, Hidetoshi Hoshiya, Martina Ragazzi, Giuliana Ferrari, Yasuhiro Kazuki, Louise Anne Moyle, Rossana Tonlorenzi, Angelo Lombardo, Soraya Chaouch et al. · 2017 · EMBO Molecular Medicine
Advancements in stem cells treatment of skeletal muscle wasting
M. Meregalli, A. Farini, C. Sitzia, Y. Torrente · 2014 · Frontiers in Physiology
Generation and Characterization of a MYF5 Reporter Human iPS Cell Line Using CRISPR/Cas9 Mediated Homologous Recombination
Jianbo Wu, Samuel D. Hunt, Haipeng Xue, Ying Liu, Radbod Darabi · 2016 · Scientific Reports
Neuromuscular disease modeling on a chip
Jeffrey W. Santoso, Megan Laura McCain · 2020 · Disease Models & Mechanisms
Genetic Rescue of Mitochondrial and Skeletal Muscle Impairment in an Induced Pluripotent Stem Cells Model of Coenzyme Q10 Deficiency
Damià Romero–Moya, Carlos Santos‐Ocaña, Julio Castaño, Glòria Garrabou, José A. Rodríguez‐Gómez, Vanesa Ruiz-Bonilla, Clara Bueno, Patricia González‐Rodríguez, Alessandra Giorgetti, Eusebio Perdiguero et al. · 2017 · Stem Cells
Recapitulating muscle disease phenotypes with myotonic dystrophy 1 induced pluripotent stem cells: a tool for disease modeling and drug discovery
Ricardo Mondragón-González, Rita C. R. Perlingeiro · 2018 · Disease Models & Mechanisms
Chemical induced conversion of mouse fibroblasts and human adipose-derived stem cells into skeletal muscle-like cells
Varun Bansal, Debojyoti De, Jieun An, Tong Mook Kang, Hyeon‐Ju Jeong, Jong‐Sun Kang, Kyeong Kyu Kim · 2018 · Biomaterials
Nano-biomaterials and advanced fabrication techniques for engineering skeletal muscle tissue constructs in regenerative medicine
Seokgyu Han, Sebastián Herrera Cruz, Sungsu Park, Su Ryon Shin · 2023 · Nano Convergence
Reliable and versatile immortal muscle cell models from healthy and myotonic dystrophy type 1 primary human myoblasts
Boris Pantic, Doriana Borgia, Silvia Giunco, Adriana Malena, Tohru Kiyono, Sergio Salvatori, Anita De Rossi, Emiliano Giardina, Federica Carla Sangiuolo, Elena Pegoraro et al. · 2016 · Experimental Cell Research
Recombinase-Mediated Reprogramming and Dystrophin Gene Addition in mdx Mouse Induced Pluripotent Stem Cells
Chunli Zhao, Alfonso P. Farruggio, Christopher R.R. Bjornson, Christopher L. Chavez, Jonathan M. Geisinger, Tawny L. Neal, Marisa Karow, Michèle P. Calos · 2014 · PLoS ONE
Core Transcription Factors Promote Induction of PAX3-Positive Skeletal Muscle Stem Cells
Takahiko Sato, Koki Higashioka, Hidetoshi Sakurai, Takuya Yamamoto, Naoki Goshima, Morio Ueno, Chie Sotozono · 2019 · Stem Cell Reports
Advance genome editing technologies in the treatment of human diseases: CRISPR therapy (Review)
Meryem Alagöz, Nasim Kherad · 2020 · International Journal of Molecular Medicine
Base editing repairs an SGCA mutation in human primary muscle stem cells
Helena Escobar, Anne Krause, Sandra Keiper, Janine Kieshauer, Stefanie Müthel, Manuel García de Paredes, Eric Metzler, Ralf Kühn, Florian Heyd, Simone Spuler · 2021 · JCI Insight
Generation of Equine-Induced Pluripotent Stem Cells and Analysis of Their Therapeutic Potential for Muscle Injuries
Eunmi Lee, Ah-Young Kim, Eunjoo Hwang Lee, Jin‐Kyu Park, Se‐Il Park, Ssang‐Goo Cho, Hong Kyun Kim, Shin‐Yoon Kim, Kyu‐Shik Jeong · 2016 · Cell Transplantation
Insulin/Glucose-Responsive Cells Derived from Induced Pluripotent Stem Cells: Disease Modeling and Treatment of Diabetes
Sevda Gheibi, T. Singh, J. P. D. da Cunha, M. Fex, H. Mulder · 2020 · Cells
Myogenic Precursors from iPS Cells for Skeletal Muscle Cell Replacement Therapy
Isart Roca, Jordi Requena Osete, Michael J. Edel, Ana Belén Alvarez Palomo · 2015 · Journal of Clinical Medicine
Generation and validation of PAX7 reporter lines from human iPS cells using CRISPR/Cas9 technology
Jianbo Wu, Samuel D. Hunt, Haipeng Xue, Ying Liu, Radbod Darabi · 2016 · Stem Cell Research
Myogenic Cell Transplantation in Genetic and Acquired Diseases of Skeletal Muscle
Olivier Boyer, Gillian Sandra Butler-Browne, Hector Chinoy, Giulio Cossu, Francesco Galli, James B Lilleker, Alessandro Magli, Vincent Mouly, Rita C. R. Perlingeiro, Stefano Carlo Previtali et al. · 2021 · Frontiers in Genetics
Bioengineering human skeletal muscle models: Recent advances, current challenges and future perspectives
Yunsong Jiang, Tugce Torun, Sara Martina Maffioletti, Andrea Serio, Francesco Saverio Tedesco · 2022 · Experimental Cell Research
Etv2 rescues Flk1 mutant embryoid bodies
Tara L. Rasmussen, Cindy M. Martin, Camille A. Walter, Xiaozhong Shi, Rita C. R. Perlingeiro, Naoko Koyano‐Nakagawa, Daniel J. Garry · 2013 · genesis
Pluripotent Stem Cells for Gene Therapy of Degenerative Muscle Diseases
Mariana Loperfido, Heather B. Steele-Stallard, Francesco Saverio Tedesco, Thierry VandenDriessche · 2015 · Current Gene Therapy
Perspectives on mitochondrial dysfunction in the regeneration of aging skeletal muscle
Kai Wang, Mailin Gan, Yuhang Lei, Tianci Liao, Jiayan Li, Lili Niu, Ye Zhao, Lei Chen, Yan Wang, Li Zhu et al. · 2025 · Cellular & Molecular Biology Letters
Myogenic Progenitor Cell Lineage Specification by CRISPR/Cas9-Based Transcriptional Activators
Jennifer B. Kwon, Ashish Vankara, Adarsh R. Ettyreddy, Joel D. Bohning, Charles A. Gersbach · 2020 · Stem Cell Reports
iMyoblasts for ex vivo and in vivo investigations of human myogenesis and disease modeling
Guo, Dongsheng, Daman, Katelyn, Chen, Jennifer JC, Shi, Meng-Jiao, Yan, Jing, Matijasevic, Zdenka, Rickard, Amanda M, Bennett, Monica H, Kiselyov, Alex, Zhou, Haowen et al. · 2022 · eLife
Inducing Stem Cell Myogenesis Using NanoScript
Sahishnu Patel, Perry To‐Tien Yin, Hiroshi Sugiyama, Ki‐Bum Lee · 2015 · ACS Nano
Directed midbrain and spinal cord neurogenesis from pluripotent stem cells to model development and disease in a dish
Ilary Allodi, Eva Hedlund · 2014 · Frontiers in Neuroscience
Derivation of Skeletal Myogenic Precursors from Human Pluripotent Stem Cells Using Conditional Expression of PAX7
Radbod Darabi, Rita C. R. Perlingeiro · 2014 · Methods in molecular biology
Cored in the act: the use of models to understand core myopathies
Aurora Fusto, Louise Anne Moyle, Penney M. Gilbert, Elena Pegoraro · 2019 · Disease Models & Mechanisms
A universal gene correction approach for FKRP-associated dystroglycanopathies to enable autologous cell therapy
Neha R. Dhoke, Hyunkee Kim, Sridhar Selvaraj, Karim Azzag, Haowen Zhou, Nélio Alessandro de Jesus Oliveira, Sudheer K. Tungtur, Carolina Ortiz‐Cordero, James Kiley, Qi Long Lu et al. · 2021 · Cell Reports
Endogenous Mesenchymal Stromal Cells in Bone Marrow Are Required to Preserve Muscle Function in mdx Mice
Ryo Fujita, Katsuto Tamai, Eriko Aikawa, Keisuke Nimura, Saki Ishino, Yasushi Kikuchi, Yasufumi Kaneda · 2014 · Stem Cells
Evaluation systems of generated forces of skeletal muscle cell-based bio-actuators
Kazunori Shimizu, Hideaki Fujita, Eiji Nagamori · 2012 · Journal of Bioscience and Bioengineering
Pluripotent Stem Cells and Other Innovative Strategies for the Treatment of Ocular Surface Diseases
Johanna M Erbani, Daniel Aberdam, Jérôme Larghero, Valérie Vanneaux · 2016 · Stem Cell Reviews and Reports
Extracellular Vesicles from Skeletal Muscle Cells Efficiently Promote Myogenesis in Induced Pluripotent Stem Cells
Denisa Baci, Maila Chirivì, Valentina Pace, Fabio Maiullari, Marika Milan, Andrea Rampin, Paolo Somma, Dario Presutti, S. Garavelli, Antonino Bruno et al. · 2020 · Cells
Emerging gene editing strategies for Duchenne muscular dystrophy targeting stem cells
Carmen Bertoni · 2014 · Frontiers in Physiology
Evaluation of the Therapeutic Potential of Human iPSCs in a Murine Model of VML
Jianbo Wu, Nadine Matthias, Shubhang Bhalla, Radbod Darabi · 2020 · Molecular Therapy
Development of the excitation-contraction coupling machinery and its relation to myofibrillogenesis in human iPSC-derived skeletal myocytes
Jeanne Lainé, Gunnar Skoglund, Emmanuel Fournier, Nacira Tabti · 2018 · Skeletal Muscle
Simple and efficient differentiation of human iPSCs into contractible skeletal muscles for muscular disease modeling
Muhammad Irfanur Rashid, Takuji Ito, Fuyuki Miya, Daisuke Shimojo, Kanae Arimoto, Kazunari Onodera, Rina Okada, Takunori Nagashima, Kazuki Z. Yamamoto, Zohora Khatun et al. · 2023 · Scientific Reports
Genome Editing Gene Therapy for Duchenne Muscular Dystrophy
A. Hotta · 2015 · Journal of Neuromuscular Diseases
Human artificial chromosomes for Duchenne muscular dystrophy and beyond: challenges and hopes
Francesco Saverio Tedesco · 2015 · Chromosome Research