Functional Repair of CFTR by CRISPR/Cas9 in Intestinal Stem Cell Organoids of Cystic Fibrosis Patients

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12. On the Corner of Models and Cure: Gene Editing in Cystic Fibrosis
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18. Theratyping in cystic fibrosis
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19. An organoid model to assay the role of CFTR in the human epididymis epithelium
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33. Organoids as Model Systems for Gastrointestinal Diseases: Tissue Engineering Meets Genetic Engineering
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35. Cystic Fibrosis: The Dawn of a New Therapeutic Era
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