Robust systemic transduction with AAV9 vectors in mice: efficient global cardiac gene transfer superior to that of AAV8

Cited by (612)

Items 601–612 of 612

  1. Capsid Engineering of Adeno-Associated Viruses for Targeted Gene Therapy in Kidney Diseases
    Mohammadreza Ghaffarzadeh-Esfahani, Yousof Gheisari · 2026 · Human Gene Therapy
  2. CD8+ T cell activation occurs 24 hours after AAV administration and is driven by muscle promoter specificity
    Lindsay Jeanpierre, Coralie Pecquet, Hanadi Saliba, Pauline Finard, Stéphane Terry, Gianni Tavella, Inès Guesmia, Sylvie Boutin, Bérangère Bertin, Sofia Benkhelifa‐Ziyyat et al. · 2026 · JCI Insight
  3. Comparative Transduction Profiling of Four Intravenously Delivered AAV Capsids in the Neonatal Murine Nervous System
    H X Gao, Tonghui Xu · 2026 · Biomedicines
  4. Highly potent MyoAAV4A vector reverses GSD III pathology in aged mice and enables long-term muscle disease correction in young adult mice
    Kuo-An Liao, Haiqing Yi, Haoyue Zhang, William Eisner, Sarah P. Young, Baodong Sun · 2026 · Molecular Therapy Advances
  5. A receptor-Fc based SFV replicon Trim-Away platform for targeted viral protein degradation
    Yiming Han, Qisheng Dong, Zhen Tian, X G Wang, Pengbo Wang, Quanyong Liu, Yangxue Liu, Qi Guo, Shoutao Zhang · 2026 · Virology Journal
  6. Tripartite motif 16 mitigates endotoxemia-induced cardiac dysfunction via the Cav-1/Src/YAP signaling axis in mice
    Bing Han, Kaina Zhang, Yating Li, Yeqing Zheng, Mengqing Liu, Mengyao You, Yang Guo, Gaowa Bao, Lei Zhang, Zhenghang Zhao et al. · 2026 · International Immunopharmacology
  7. Cellular crosstalk between endothelial and vascular smooth muscle cells via the BACH1/COL3A1 axis promotes vascular calcification in chronic kidney disease
    Jing Ning, Sitian Fang, Minzi Qiu, Honghong Zou, Yanxia Chen · 2026 · Inflammation Research
  8. GAS6 mediates Benzo[a]pyrene-induced pathological cardiac hypertrophy via the mTOR/HIF-1α glycolytic remodeling axis
    Guangming Li, Feihu Long, Zhiyue Liu, Jiarui Nicole Fu, Yuanyin Teng, Shanshan Cai, Xiaoling Zhang, Yingji Wang · 2026 · Chemico-Biological Interactions
  9. Variable expressivity in long QT syndrome type 2 rabbits defines a low threshold for therapeutic I Kr restoration
    Nilufer Nermin Turan, Allison Navarrete-Welton, Yichun Lu, Tae Yun Kim, Karim Roder, Elif Sengun, Anatoli Y. Kabakov, Peter Bronk, Rebecca Martínez-Moreno, Brett Baggett et al. · 2026 · American Journal of Physiology-Heart and Circulatory Physiology
  10. A genome-scale ORF screen for resilience factors that protect the RPE and restore vision in aged mice
    Yuancheng Ryan Lu, Han Shen, Kathrin M Kajderowicz, 艾家和, Yi Hua Chen-Neumann, Yan Hu, Alexander Tyshkovskiy, Qiannuo Lou, Tianwei Dong, Louisa Grauvogel et al. · 2026 · bioRxiv (Cold Spring Harbor Laboratory)
  11. Estrategias de transferencia génica en cerebro mediadas por vectores virales adenoasociados
    José Miguel Brito Armas, Ibrahim González Marrero, Agustín Lorenzo Castañeyra Perdomo, Emilia María Carmona Calero, Antonio Alayón Fumero, Javier R. Castro Hernández, Rafael Fuentes · 2009 · Majorensis: Revista Electrónica de Ciencia y Tecnología
  12. RNA Interference and MicroRNA Modulation for the Treatment of Cardiac Disorders
    Wolfgang C. Poller, Lennart Suckau, Sandra Pinkert, Henry Fechner · 2008 · Springer eBooks