CRISPR/Cas9 genome editing in human hematopoietic stem cells.
Cited by (317)
Items 301–317 of 317
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- Site-specific Integration of Therapeutic-length Genes using TIVID SystemXiao‐Bing Zhang, Zhu-Ying Gao, Tian-Lai Shen, Chong-Ya Cheng, Yu-Meng Zhang, Li-Ming Zhang, Xi-Die Zhao, Jianping Zhang · 2025 · Research Square
- Additional file 1 of Efficient delivery of a large-size Cas9-EGFP vector in porcine fetal fibroblasts using a Lonza 4D-Nucleofector systemLiu, Weiwei, Wang, Xiaoguo, Liu, Ruirong, Liao, Yaya, Peng, Zhiwei, Jiang, Haoyun, Jing, Qiqi, 幸宇云 · 2023 · Figshare
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- A Dual-Viral Delivery Platform Enables Efficient Site-Specific Integration of Therapeutic-Length Genes in Human Primary Stem CellsZhu-Ying Gao, Tian-Lai Shen, Chong-Yan Cheng, Yuanhao Sun, Liming Zhang, Jian-Ping Zhang, Xiao-Bing Zhang · 2026 · Human Gene Therapy
- CRISPR/Cas9 gene editing in hematopoietic stem and progenitor cells to accelerate the translation of cellular therapies and immunotherapiesLaura Falceto Font, Dan Jin, John Figg, Connor P. Francis, Kaytora Long-James, Jeffrey Drake, Alexandra Reid, Caitland Love, Brianna McDonald, David Hilferty et al. · 2026 · Journal of Translational Research
- Editing around the target: epitope engineering to protect stem cell graftsJoanne Seoyoung Baek, Gabriele Casirati, Pietro Genovese, Saar I. Gill · 2026 · Blood Advances
- CRISPR integration of an FLT3 CAR into the TRAC locus generates CAR T cells for AMLMaya Graham Noer, Kimmie B. Christensen, Nanna S. Mikkelsen, Sigrid Fu Skjelbostad, Frederik Holm Rothemejer, Thomas Rea Wittenborn, Simon Fammé, Kasper Mikkelsen, Torben Barington, Martin Kristian Thomsen et al. · 2026 · Genome Medicine
- Glycosylation orchestrates megakaryocytic fate of hematopoietic stem cells via Wnt-MUC13 signalingAlejandro Roisman, Leonardo Rivadeneyra, Lindsey R. Conroy, Natalia Weich, Agata Steenackers, Melissa M. Lee‐Sundlov, Simon H. Glabere, Shikan Zheng, Katelyn E. Rosenbalm, Mark Zogg et al. · 2026 · Nature Communications
- Therapeutic CRISPR/Cas9 delivery approaches: strengths, limitations, and a roadmap for clinical translationMaryam Rezaee, Farideh Izadi, Saeed Nobaharian, Leila Hassani, Esmaeil Rezaei, Sara Sadeghi Amini, Ali Akbar Pourfathollah, Ali Kowsari, Sirous Naeimi, Khalil Khashei Varnamkhasti et al. · 2026 · Beni-Suef University Journal of Basic and Applied Sciences
- SLC25A38 gene modification mediated by CRISPR/Cas9 in HEK293T cell lineShokoufeh Yazdanparast, Hamid Galehdari, S.R. Khatami, Elham Hoveizi · 2026 · Journal of Applied Genetics
- Cell and Gene Therapies Manufacturing Challenges and Integrated Good Manufacturing Practices Solutions: A Lifecycle PerspectiveRajath Samaga, Udisha Singh, Sachin Dattram Pawar · 2026 · Biotechnology and Bioengineering
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- CRISPR‐Cas9 and precision editing technologies linking functional genomics to clinical translation in genetic diseasesZijing Wen, Jianming Su · 2026 · Clinical and Translational Medicine
- Prime editing of human hematopoietic stem cells for correction of GATA2 deficiencyJonas Holst Wolff, Thomas Wisbech Skov, Sofie Rahbek Dorset, Janni Sjelborg, Sujan Ravendran, Anne Louise Revenfeld, Didde Haslund, Anaïs Marie Julie Møller, Mette Holm, Martin Kristian Thomsen et al. · 2026 · Science Translational Medicine