Gregori, Ninel Z.

Human embryonic stem cell-derived retinal pigment epithelium in patients with age-related macular degeneration and Stargardt's macular dystrophy: follow-up of two open-label phase 1/2 studies

Schwartz, S. D., Regillo, C. D., Lam, B. L., Eliott, D., Rosenfeld, P. J., Gregori, N. Z., Hubschman, J.-P., Davis, J. L., Heilwell, G., Spirn, M., et al. (2015) · The Lancet

Retinal Development and DisordersRetinal Diseases and Treatments

Cited by 1,327

Initial results from a first-in-human gene therapy trial on X-linked retinitis pigmentosa caused by mutations in RPGR

Cehajic-Kapetanovic, J., Xue, K., Martinez-Fernandez de la Camara, C., Nanda, A., Davies, A., Wood, L. J., Salvetti, A. P., Fischer, M. D., Aylward, J. W., Barnard, A. R., et al. (2020) · Nature Medicine

Retinal Development and DisordersVirus-based gene therapy research

Cited by 368

Choroideremia gene therapy phase 2 clinical trial: 24-month results

Lam, B. L., Davis, J. L., Gregori, N. Z., MacLaren, R. E., Girach, A., Verriotto, J. D., Rodriguez, B., Rosa, P. R., Zhang, X., & Feuer, W. J. (2019) · American Journal of Ophthalmology

Retinal Development and DisordersRetinal Diseases and Treatments

Cited by 161

Surgical technique for subretinal gene therapy in humans with inherited retinal degeneration

Davis, J. L., Gregori, N. Z., MacLaren, R. E., & Lam, B. L. (2019) · Retina

Retinal Development and DisordersRetinal Diseases and Treatments

Cited by 72

Stargardt macular dystrophy and evolving therapies

Hussain, R. M., Ciulla, T. A., Berrocal, A. M., Gregori, N. Z., Flynn, H. W., & Lam, B. L. (2018) · Expert Opinion on Biological Therapy

Retinal Development and DisordersRetinal Diseases and Treatments

Cited by 56

Intraoperative use of microscope-integrated optical coherence tomography for subretinal gene therapy delivery

Gregori, N. Z., Lam, B. L., & Davis, J. L. (2019) · Retina

Retinal Development and DisordersRetinal Diseases and Treatments

Cited by 54

Assessment of visual function with cotoretigene toliparvovec in X-linked retinitis pigmentosa in the randomized XIRIUS phase 2/3 study

Lam, B. L., Pennesi, M. E., Kay, C. N., Panda, S., Gow, J. A., Zhao, G., MacLaren, R. E., MacLaren, R., Aleman, T., Birch, D., et al. (2024) · Ophthalmology

Retinal Development and DisordersVirus-based gene therapy research

Cited by 51