Lukason, Michael

CRISPR/Cas9-Mediated Genome Editing as a Therapeutic Approach for Leber Congenital Amaurosis 10

Ruan, G.-X., Barry, E., Yu, D., Lukason, M., Cheng, S. H., & Scaria, A. (2017) · Molecular Therapy

CRISPR and Genetic EngineeringRetinal Development and Disorders

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Preclinical safety evaluation of AAV2-sFLT01— a gene therapy for age-related macular degeneration

MacLachlan, T. K., Lukason, M., Collins, M., Munger, R., Isenberger, E., Rogers, C., Malatos, S., DuFresne, E., Morris, J., Calcedo, R., et al. (2011) · Molecular Therapy

Virus-based gene therapy researchRetinal Development and Disorders

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Novel anti-VEGF chimeric molecules delivered by AAV vectors for inhibition of retinal neovascularization

Pechan, P., Rubin, H., Lukason, M., Ardinger, J., DuFresne, E., Hauswirth, W. W., Wadsworth, S. C., & Scaria, A. (2009) · Gene Therapy

Angiogenesis and VEGF in CancerRetinal Development and Disorders

Cited by 104

Rationally designed AAV2 and AAVrh8R capsids provide improved transduction in the retina and brain

Sullivan, J. A., Stanek, L. M., Lukason, M. J., Bu, J., Osmond, S. R., Barry, E. A., O’Riordan, C. R., Shihabuddin, L. S., Cheng, S. H., & Scaria, A. (2018) · Gene Therapy

Virus-based gene therapy researchRNA Interference and Gene Delivery

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Engineered Capsids for Efficient Gene Delivery to the Retina and Cornea

Frederick, A., Sullivan, J., Liu, L., Adamowicz, M., Lukason, M., Raymer, J., Luo, Z., Jin, X., Rao, K. N., & O'Riordan, C. (2020) · Human Gene Therapy

Virus-based gene therapy researchRetinal Development and Disorders

Cited by 35