Gene therapy clinical trials worldwide to 2017: An update

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Items 701–800 of 903

1. Smart Nanocarrier Systems for Diabetic Wound Healing: Preclinical Innovations and Clinical Progress in Drug and Gene Delivery
   Praveen Bhat, Abinash Satapathy, Neha Yadav, Abhisek Satapathy, Kunal Chandrakar, Ansuman Satapathy, Shiv Kumar Bhardwaj, Nikita Patel · 2026 · Journal of Drug Delivery and Therapeutics
2. Enhancer-based gene therapy: a new path for precision medicine
   Hany E. S. Marei · 2026 · Hereditas
3. Targeted Gene and Genome-Editing Strategies for Epilepsy: Experimental Advances and Translational Challenges
   Mohd Yaqub Mir, Bilal Ahmad Seh, Kashf Rafiq, Ádám Légrádi · 2026 · International Journal of Molecular Sciences
4. Successful In Vitro Modification of the Dmd Gene Using Prime Editing
   Ayesha Siddika, Fatima El Husseiny, Joël Rousseau, Jacques P. Tremblay · 2026 · Cells
5. Targeting Adenoviral Entry to Enhance Oncolytic Antitumor Response
   Hidde J. Haisma · 2013 · The Open Gene Therapy Journal
6. Targeted Therapeutic Genome Engineering: Opportunities and Bottlenecks in Medical Translation
   Jessica A. Kretzmann, David C. Luther, Marck Nörret, Vincent M. Rotello, K. Swaminathan Iyer · 2019 · ACS symposium series
7. Gene editing in translational research.
   Marc Güell · 2019 · Revista de Bioética y Derecho
8. Ultrasound and Microbubble Gene Delivery for Targeting Altered Placental MicroRNAs in Preeclampsia
   Sonya Frazier, Hannah L. Morgan, Martin McBride, Angela C. Bradshaw, Helen Mulvana, Delyth Graham · 2019 · IEEE International Ultrasonics Symposium
9. A TECNOLOGIA DE CRISPR-CAS9 NA TERAPIA GÊNICA DO CÂNCER DE PULMÃO
   Raphael Ladislau de Alcantara, Hellen Patricia Santos Lima, Gabriel de Oliveira Barbosa, Lucas Cândido Gonçalves, Adriana Priscila Lázaro da Silva, Xisto Sena Passos, Antônio Márcio Teodoro Cordeiro Silva · 2019 · Revista Brasileira Militar de Ciências
10. Enhanced Biosynthesis of Plasmid DNA from Escherichia coli Applying Experimental Design
    Luís A. Passarinha · 2020 · Methods in molecular biology
11. Biomaterials in Tissue Engineering and Regenerative Medicine: In Vitro Disease Models and Advances in Gene-Based Therapies
    Swathi Dahariya, Vasagiri Nagarjuna · 2021 · Springer eBooks
12. Vírus de laboratório
    Sara Calafate, DN/ VIB/ KU Leuven · 2021 · Revista de Ciência Elementar
13. NOSE TO BRAIN DELIVERY: ROLE OF VIRAL AND NON-VIRAL VECTORS FOR NEUROLOGICAL DISORDER
    Shubham Musale, Prabhanjan Shridhar Giram · 2021 · INDIAN DRUGS
14. Gene therapy
    Deepti Saini · 2020 · Elsevier eBooks
15. Genomics and precision medicine
    Farhat Moazam · 2022 · Oxford University Press eBooks
16. Advanced drug delivery systems for targeting obesity
    Nisha Gulati, Kamal Dua, Harish Dureja · 2022 · Elsevier eBooks
17. CRISPR/Cas-9 and its therapeutic applications in Onco-viral diseases
    Bibi Salma Tassaduq Naqvi, Mehboob Alam, Arzoo Nazir, Shah Zeb, Alam Khan, Shanza Rafique Malik, Naveed Shah, Muhammad Naveed, Muhammad Fawad Khan · 2023 · International Journal of Health Sciences
18. Harnessing xylitol utilization in Escherichia coli for antibiotic-free plasmid and recombinant protein production
    Vincent Fung Kin Yuen, Dongxu Yuan, Ying Zhou, Handing Wang, Daniel Zhi Jun Tan, Kang Zhou · 2023 · Biochemical Engineering Journal
19. Impact of using the principle of spectral-dynamic analysis of the intensity of the electret field of the "Vim Vitae" electronic complex on a living organism
    Oleksandr HLOBA, Юлія Валеріївна Антонова-Рафі, Walery Żukow, Tatyana HARNYK, Viktor Sinyov · 2023 · Physical rehabilitation and recreational health technologies
20. AVANÇOS NA TERAPIA GENÉTICA PARA DOENÇAS GENÉTICAS RARAS
    Vitória Vilas Boas da Silva Bomfim, Guilherme Oliveira Pinheiro, Marina Brandão Ramalho de Brito, Gustavo Henrique de Moura Vardasca, Maria Luisa Xavier Cadête, Lais Nadille Lins Coelho · 2023 · Revista Ibero-Americana de Humanidades, Ciências e Educação
21. Application of Cyclodextrin based Polymers for the Gene Delivery
    Yousef Khazaei Monfared, Claudio Cecone, Adrián Matencio, Gjylije Hoti, Ilona Kabrikova, Ibrahim Hussein, Mohammed Desoky, Francesco Trotta · 2023 · IEEE Nanotechnology Materials and Devices Conference (NMDC)
22. CRISPR/Cas systems and techniques
    Anuj Kumar Poonia, Bhavika Batra, Milan Kumar Lal, Vijay Gahlaut · 2024 · Elsevier eBooks
23. Viral vectors for gene therapy
    Ang‐Chen Tsai, Silveli Suzuki‐Hatano, Christina A. Pacak · 2024 · Elsevier eBooks
24. [Advances in gene therapy for inborn errors of immunity].
    Ting Li, Hongmei Song · 2024 · PubMed Central
25. GTO: a comprehensive gene therapy omnibus
    Xuehang Meng, Yujia Du, Chang Xin Liu, Zhaoyu Zhai, Jianbo Pan · 2024 · Nucleic Acids Research
26. Current Updates, Recent Trends and Future Directions of Gene Therapy on Various Eye Disorders
    Saeed Ur Rehman, Umar Javed, Ammara Saleem, Muhammad Hamzah Saleem, Usman Hameed, Khadija Muzaffar, Tajammal Raza, Rabia Ijaz, Fiza Ali · 2025 · Indus journal of bioscience research.
27. Unlocking the Puzzle of Mammalian Transfection: The Role of the RNA-sensing-Mediated Interferon Response in the Cellular Defense Against Foreign DNA Intrusion
    Xiaoyu Li, Yicen Zhou, Jie Wei, Wei Sun, Ligang Fan, Jian Yan · 2025 · International Journal of Biological Sciences
28. Towards gene therapy of endometriosis
    Anastasia Shubina, Anton Kiselev, Anna Egorova, Баранов Владислав Сергеевич · 2012 · Journal of obstetrics and women s diseases
29. Minimal conditioning in Fanconi anemia promotes multi‐lineage marrow engraftment at 10‐fold lower cell doses
    Kevin G. Haworth, Christina M. Ironside, Megan A. Ramirez, Sarah Weitz, Brian C. Beard, Jonathan D. Schwartz, Jennifer E. Adair, Hans‐Peter Kiem · 2018 · The Journal of Gene Medicine
30. Biothérapies
    Serge Braun · 2019 · médecine/sciences
31. Porous Silicon Nanoparticles for Applications in Nano-medicine
    Morteza Hasanzadeh Kafshgari, Nicolas Hans Voelcker, Frances J. Harding · 2018 · Elsevier eBooks
32. Gene Therapy for Treatment of Melanoma Cancer
    Oisorjo Chakraborty, Aishwarya Mukherjee, Pranab Roy · 2017 · Annals of Applied Microbiology & Biotechnology Journal
33. DNA complexes as an efficient gene anticancer drug delivery therapy
    Loutfy H. Madkour · 2019 · Nucleic Acids as Gene Anticancer Drug Delivery Therapy
34. Liver gene transfection by retrograde intrabiliary infusion facilitated by temporary biliary obstruction
    Chenguang Dai, Min Wang, Lili Zhao, Chunfang Xu, Jin Huang, Zhining Fan · 2019 · The Journal of Gene Medicine
35. Potential Applications of Cationic Lipids in Nucleic Acid-Based Therapeutic Delivery System
    Sunil Kardani, Devendra J. Vaishnav · 2021 · Springer eBooks
36. microRNA Modulation
    Irene Mencía Castaño, Rosanne M. Raftery, Caroline M. Curtin, Johannes Grillari, Heinz R. Redl, Fergal J. O’Brien · 2020 · Springer eBooks
37. Targeted Therapeutics for Rare Disorders
    Kim M. Keeling, André Leier, David M. Bedwell, Ann T. Chen, Robert A. Kesterson, Tatiana T. Marquez‐Lago, Ulrich F. Müller, Jiangbing Zhou, Linda J. Popplewell, DEEANN E. WALLIS · 2022 · Elsevier eBooks
38. Synthesis of Double Hydrophilic Block Copolymers Poly(2‐isopropyl‐2‐oxazoline‐b‐ethylenimine) and their DNA Transfection Efficiency
    Gwendoline Delecourt, Laetitia Plet, Yann Thierry Le Guen, Özgül Tezgel, Guillaume Tresset, Patrick Midoux, Tristan Montier, Véronique Bennevault, Philippe Guégan · 2022 · Macromolecular Bioscience
39. Estabelecimento de linhagens celulares de melanoma canino e transdução com vetores adenovirais aprimorados
    Gissele Rolemberg Oliveira Silva · 2019
40. Long term AAV2/9-mediated silencing of PMP22 prevents CMT1A disease in rats and validates skin biomarkers as treatment outcome measure
    Benoît Gautier, Hélène Hajjar, Sylvia Soares, Jade Berthelot, Marie Deck, Scarlette Abbou, Graham R. Campbell, Claire-Maëlle Fovet, Vlad Schütza, Antoine Jouvenel et al. · 2020 · bioRxiv (Cold Spring Harbor Laboratory)
41. High-content image-based drug screen identifies a clinical compound against cell transmission of adenovirus
    Fanny Georgi, Fabien Kuttler, Luca Murer, Vardan Andriasyan, Robert Witte, Artur Yakimovich, Gerardo Turcatti, Urs F. Greber · 2020 · bioRxiv (Cold Spring Harbor Laboratory)
42. Defining public attitudes and understanding of human gene therapy in Australia
    Michel Watson · 2021 · ANU Open Research (Australian National University)
43. The Importance of Family and Caregiver Perspectives of Emerging Gene Therapies
    Jill L. Maron · 2022 · Clinical Therapeutics
44. Inhibition of sensory neuron driven acute, inflammatory, and neuropathic pain using a humanised chemogenetic system
    Jimena Pérez-Sánchez, Steven J. Middleton, Luke A. Pattison, Helen Hilton, Mosab Ali Awadelkareem, Sana R. Zuberi, Maria B. Renke, Huimin Hu, Xun Yang, Alex J. Clark et al. · 2023 · bioRxiv (Cold Spring Harbor Laboratory)
45. The Influence of Multivalent Charge and PEGylation on Shape Transitions in Fluid Lipid Assemblies: From Vesicles to Discs, Rods, and Spheres
    Victoria M. Steffes, Zhening Zhang, Kai K. Ewert, Cyrus R. Safinya · 2023 · bioRxiv (Cold Spring Harbor Laboratory)
46. Utilization of Chitosan for Gene Delivery
    Johnson Olaleye Oladele · 2023
47. Desenvolvimento e caracterização de vetores não virais para entrega gênica baseados em proteínas e lipossomas.
    Rafael Ferraz Alves · 2013
48. Caracterização de nanopartículas pDNA-protamina e pDNA-protamina-lipossoma e avaliação da eficiência de entrega gênica a células de mamífero.
    Daniel Campos Silva · 2016
49. Gene Transfer Therapy: A Survey of Clinical Trials for Treatment of Various Cancers
    Shruthi Selvaraj · 2016 · Proceedings of the World Congress on New Technologies
50. Bioreducible polycationic gene vectors
    G. Si · 2015
51. Perspectives in Gene Therapy
    Marek Jakóbisiak · 2009 · Advances in respiratory medicine
52. Utilização de shRNA anti-hexon, anti-IVa2 e anti-pol durante a produção de vírus adeno-associado como estratégia de eliminar Adenovírus helper: prova de princípio
    Marlous Vinícius Gomes Lana · 2017
53. Brush polymers for nucleic acid delivery and self assembly
    Xueguang Lu · 2017
54. Otimização de parâmetros de transferência in vivo do gene do hormônio de crescimento visando a correção fenotípica de camundongos anões
    Eliana Rosa Lima Filha · 2016
55. Desenvolvimento de nanopartículas metal-proteína para a entrega de DNA em estudos de terapia e vacinação gênicas.
    Matheus Mlot Palma · 2017
56. A novel reflection on sleep disorders approach
    Faustin Armel Etindele Sosso · 2017 · Sleep Medicine and Disorders International Journal
57. SYNTHESIS OF CONJUGATES OF OLIGONUCLEOTIDES AND 11,11-D2-LINOLEIC ACID DERIVATIVES VIA AZIDE-ALKYNE CYCLOADDITION
    Maksim A. Fomich, Andrei V. Bekish, Olga L. Sharko, Konstantin N. Prokhorevich, Vadim V. Shmanai · 2018 · Proceedings of the National Academy of Sciences of Belarus Chemical Series
58. Genetic medicines and genome editing - possible cure for monogenic and polygenic hereditary disorders
    Rabia Bibi · 2018 · Pure and Applied Biology
59. Susd2/SUSD2, a putative tumor suppressor gene, inhibits growth of colorectal cancer cells
    Toshiwo Andoh, Kensuke Kumamoto, Shinichi Suzuki, Yoshiko Matsumoto, Chiyo Oukouchi, Manabu Iwadate, Satoshi Suzuki, Hiroshi Mizunuma, Seiichi Takenoshita · 2018 · Annals of Cancer Research and Therapy
60. Artificial viral capsid proteins : mimicking nature to deliver medicines
    Lione Willems · 2019
61. Gene Therapy: An Outstanding Technique For Diseases
    Nayade Sarmiento, Selena Tinoco · 2019 · Bionatura
62. DETERMINANTS OF AAV TRANSPORT ACROSS THE BLOOD-BRAIN BARRIER
    Blake H. Albright · 2019 · Carolina Digital Repository (University of North Carolina at Chapel Hill)
63. Innovation in biosafety oversight: The Harvard Catalyst Common Reciprocal IBC Reliance Authorization Agreement
    Rebecca R. Caruso, Theodore A. Myatt, Barbara E. Bierer · 2019 · Journal of Clinical and Translational Science
64. Future Preventive Gene Therapy of Polygenic Diseases from a Population Genetics Perspective
    Roman Teo Oliynyk · 2019 · bioRxiv (Cold Spring Harbor Laboratory)
65. Can Hsp Targeted Gene Therapy Be a New Hope for Gliomas?
    Evren Önay Uçar, Aslıhan Şengelen, Elçin Güngör, Elif Mertoğlu, Murat Pekmez, Nazlı Arda · 2019 · Heat shock proteins
66. Creating Catholic Regenerative Medicine Organizations in a Secular Biotechnology Field: A Physician-Scientist Experience
    Alan B. Moy · 2019 · The Linacre Quarterly
67. Characteristics of ribonucleic acid
    Loutfy H. Madkour · 2019 · Elsevier eBooks
68. THE DEVELOPMENT of a SAFE and OPTIMIZED GENE THERAPY for HUMAN DISEASES
    Alva Sahiri Alexander Supit, Linda Maya Tompodung · 2019 · JURNAL BIOSAINS
69. Gene Therapy: A Strategy for the Treatment of Alzheimer’s Disease
    Danielle Weber‐Adrian · 2019 · Health Science Inquiry
70. Gene editing in PRKDC severe combined immunodeficiency and ataxia telangiectasia
    V. Prakash · 2017
71. Suppression of cancer stem cells
    Carla García-Mazás, Sheila Barrios-Esteban, Nœmi Csaba, Marcos García-Fuentes · 2020 · Elsevier eBooks
72. Biomaterials for gene editing therapeutics
    Gayong Shim, Dongyoon Kim, Quoc‐Viet Le, Junho Byun, Jin-Won Park, Yu‐Kyoung Oh · 2020 · Elsevier eBooks
73. Cationic Polymers and Polymeric Micelles as Plasmid DNA and CRISPR-Cas9 Ribonucleoprotein Delivery Vehicles
    Zhe Tan · 2019 · University of Minnesota Digital Conservancy (University of Minnesota)
74. Optimization transgene expression of short fully synthesized lipopeptide-based transfection agent for non-viral gene delivery vehicle
    null Tarwadi, Dewi Esti Restiani, Sabar Pambudi, Jalal J. Jazayeri, Colin William Pouton, Heni Rachmawati, Rahmana Emran Kartasasmita, Sukmadjaja Asyarie · 2018
75. Transferrin receptor-mediated gene delivery using functionalised gold nanoparticles.
    Jananee Padayachee · 2018 · ResearchSpace (University of KwaZulu-Natal)
76. A módosított messenger RNS-terápia lehetőségei a kardiális regenerációban
    Gábor Tamás Szabó · 2020 · Cardiologia Hungarica
77. Adeno-associated virus-mediated gene therapy in central nervous system genetic disorders
    Widler Casy, Qinglan Ling, Frances C. Shaffo, Sarah E. Sinnett, Steven James Gray · 2020 · Elsevier eBooks
78. Molecular therapies for bradyarrhythmias
    Anna M. D. Végh, Harsha D. Devalla, Dirk Geerts, Hanno L. Tan, Vincent M. Christoffels, Marie‐José Goumans, Gerard J.J. Boink · 2020 · Elsevier eBooks
79. Schwerpunkte der Forschungspipelines
    Georg Watzek · 2020 · Springer eBooks
80. Spor Hekimliğinde Etik Yaklaşımlar ve Malpraktis
    Sabriye Ercan, Hüseyin Tolga Acar, Berke Aksöz · 2020 · Selçuk Tıp Dergisi
81. The First Barriers in the Human Genetic Engineering Debate
    John H. Evans · 2020
82. The CRISPR Era, the National Academies Report, and the Median Trait Barrier
    John H. Evans · 2020
83. Possible Barriers Further Down the Slope
    John H. Evans · 2020
84. Differential gene expression analysis and weighted gene co-expression network analysis reveal mechanism behind the development of duodenal carcinoma in familial adenomatous polyposis
    Weiqing Liu, Xuan-Yu Meng, Xiaoting Liu, Lei Liang, Zhi-Yong Kou, Wenliang Li, Jun Hyeok Yang · 2021 · Research Square
85. Non-viral Vectors and Drug Delivery: In Vitro Assessment
    Dragos Peptanariu, Marc J.M. Abadie, Mariana Pinteală · 2021 · Springer eBooks
86. Polymeric Carriers for Transporting Nucleic Acids—Contributions to the Field
    Lilia Clima, Andrei Ioan Dascalu, Bogdan Florin Craciun, Mariana Pinteala · 2021 · Springer eBooks
87. Eletrotransferência do gene do hormônio de crescimento de camundongo associada à administração de células-tronco mesenquimais em modelo murino de osteogênese imperfeita
    Alissandra de M. Gomes · 2021
88. Looking for Tumor Specific Transcription Factors. Study of Promoters in Silico
    К. Н. Кашкин · 2021 · bioRxiv (Cold Spring Harbor Laboratory)
89. Gene therapy of neuropathic pain after spinal cord injury
    Irina V. Kalashnikova, Matthew A. Farmer, Lonnie D. Shea, Jonghyuck Park · 2021 · Elsevier eBooks
90. Study of the availability of gene therapeutic drugs in the Russian Federation
    Konstantin Koshechkin, P. A. Romanov, A. Mokhov, A. Khokhlov · 2021 · Remedium
91. Engineering of AAV-Mediated in Vivo Targeted DNA Methylation Editing System via Staphylococcus Aureus Derived Cas9-SunTag
    Naoki Yamamoto, Sumiyo Morita, Izuho Hatada, Maky Ideta-Otsuka, Hideki Tamura, Minoru Narita, Katsuhide Igarashi · 2021 · Research Square
92. microRNA Modulation
    Irene Mencía Castaño, Rosanne M. Raftery, Caroline M. Curtin, Johannes Grillari, Heinz R. Redl, Fergal J. O’Brien · 2019 · Springer eBooks
93. Pharmacologically controlled neurotrophic factor gene therapy for Parkinson's disease
    Shi Cheng · 2019
94. Novel Polymer Systems for Gene Therapy
    Diana Diaz‐Dussan, Yi‐Yang Peng, Ravin Narain · 2022
95. Optimized Pretreatment Method for Long-Term Transduction Efficiency of AAV Into Rat Bladder
    Yanyuan Wu, Jiatong Zhou, Haojie Chen, Bowen Shi, Jie Ding, Jun Qi · 2022 · Research Square
96. Islamic Sunni perspectives on the ethics of precision medicine
    Mehrunisha Suleman · 2022 · Oxford University Press eBooks
97. Personalized medicine and disorders of consciousness
    Joseph Jack Fins · 2022 · Oxford University Press eBooks
98. The revolution of personalized medicine is already upon us in rare diseases
    Christopher P. Austin · 2022 · Oxford University Press eBooks
99. Gender and personalized medicine
    Marianne J. Legato · 2022 · Oxford University Press eBooks
100. Personalized medicine and genetic newborn screening
     Margherita Brusa, Donna L. Dickenson · 2022 · Oxford University Press eBooks