Gene therapy clinical trials worldwide to 2017: An update

Cited by (903)

Items 801–900 of 903

1. Genetics, genetic profiles, and Jewish law
   Yehoshua Weissinger, Yechiel Michael Barilan · 2022 · Oxford University Press eBooks
2. Precision and persons in medicine
   Yechiel Michael Barilan, Margherita Brusa · 2022 · Oxford University Press eBooks
3. Therapeutic peptides in anticancer therapy
   Sabya Sachi Das, Amit Kumar Dubey, Ishan Moitra, P. R. P. Verma, Sandeep Kumar Singh, Shubhankar Kumar Singh · 2022 · Elsevier eBooks
4. Nanotechnology Application in tissue regeneration and gene therapy
   Ayano Shanko, Devinder Kumar, Dr Deepak Prashar, Nikita rawat, Pooja Negi, Susheel Kumar Sharma · 2022 · YMER Digital
5. Introduction
   John H. Evans · 2020
6. Gene Therapy
   Olga Maslova, Alexander K. Koliada, Alexander M. Vaiserman · 2019 · Elsevier eBooks
7. Conclusion
   John H. Evans · 2020
8. Unlocking effective transgene expression potential in gene therapy with viral vectors
   Nur Shuhaidatul Sarmiza Abdul Halim, Noor Hanis Abu Halim, Lelamekala Vengidasan, Norashikin Zakaria, Ida Shazrina Ismail, Badrul Hisham Yahaya · 2021 · Biomedical Research and Therapy
9. Bioinspired Nanodesigns for Molecular Encapsulation
   2021 · Royal Society of Chemistry eBooks
10. Polymeric Nanomaterials for Cancer Theranostics
    Rajarshi Roychoudhury · 2022 · BENTHAM SCIENCE PUBLISHERS eBooks
11. Cell-Based Therapy and Genome Editing in Parkinson’s Disease: Quo Vadis?
    Yanni Schneider, Jeanette Wihan, Soeren Turan, Jürgen Winkler · 2022 · Advances in neuroethics
12. Schwerpunkte der Forschungspipelines
    Georg Watzek · 2022 · Springer eBooks
13. Hybrid Genomics
    Tariq K. Al-Shimmari · 2022 · Health informatics
14. Vector Shedding and Immunogenicity Sampling in AAV-Based Gene Therapy for Retinitis Pigmentosa Patients
    Ahra Cho · 2022 · Methods in molecular biology
15. Looking for Tumor Specific Promoters In Silico
    К. Н. Кашкин · 2022 · Russian Journal of Bioorganic Chemistry
16. Applications of Nanoporous and Metamaterials: An Unornamented Review
    2022 · Nanosistemi Nanomateriali Nanotehnologii
17. National Survey on Clinical Practice of Gene Therapy using Adeno-associated Virus Vector ―The Actual Status and Hurdle on Clinical Practice in Gene Therapy for Spinal Muscular Atrophy―
    Masayoshi Nakakuni, Masafumi Onodera · 2022 · Rinsho yakuri/Japanese Journal of Clinical Pharmacology and Therapeutics
18. A Validatable Droplet Digital Polymerase Chain Reaction Assay for the Detection of Adeno-Associated Viral Vectors in Bioshedding Studies of Tears
    Bryanna Longacre, Amanda Souaysene, Carrie A. Vyhlidal, Matthew R. Pennington · 2023 · Journal of Visualized Experiments
19. JoVE Video Dataset
    Bryanna Longacre, Amanda Souaysene, Carrie A. Vyhlidal, Matthew R. Pennington · 2023
20. Hydrogel‐Based Gene Therapy
    Shweta Kumari, Dipti Jena, Vedant Kumar Prajapati, Shashi Ranjan Singh, Garima Tripathi · 2023 · Wiley eBooks
21. The Junction of Biomaterials and Gene Therapy – Current Strategies and Future Directions
    Ranjan Kumar Singh, Sunita Panchawat, Chennu M.M. Prasada Rao, Joohee Pradhan, Tanniru Rajeswari, Deepika Bairagee, Ajay Kumar Garg · 2023
22. A REVIEW ON OVERVIEW OF GENE AND RNA BASED THERAPIES
    Tandel Muskan Vijaykumar, Prajapati Hardikkumar Bharatbhai, Anuradha Parixit Prajapati, Sachin B. Narkhede, Shailesh Luhar · 2023 · EPRA International Journal of Research & Development (IJRD)
23. Gene Therapy for Genetic Muscle Diseases
    J. W. Lee · 2023 · Korean Journal of Neuromuscular Disorders
24. Advanced Therapy Medicinal Products: Clinical, Non-clinical, and Quality Considerations
    Enrico Mastrobattista, Erik Doevendans, Niek Peter van Til, Vera Kemp, Jeroen de Vrij, Karin H. Hoogendoorn · 2024 · Springer eBooks
25. Surfactants as a Means of Delivering a Reporter Genetic Construct Based on Binase Suicide Gene to Tumor Cells
    Дудкина Елена Владимировна, Elmira A. Vasilieva, Ульянова Вера Владимировна, Lucia Ya. Zakharova, Olga N. Ilinskaya · 2024 · Russian Journal of Bioorganic Chemistry
26. [Study on gene therapy for DPOAE and ABR threshold changes in adult Otof-/- mice].
    Zijing Wang, Qi Cao, Shaowei Hu, Xintai Fan, Jun Lv, Hui Wang, Wuqing Wang, Huawei Li, Yilai Shu · 2024 · PubMed Central
27. GFP chromophore derived amphiphiles containing [12]aneN3 and biotin moieties as bio-imaging and targeting nonviral gene vectors
    Qian Wang, Xi Zhang, De-Zhong Xu, Zi-Han Zhang, Rui Liu, Zhong‐Lin Lu, Caiyu Zhang · 2024 · Journal of Photochemistry and Photobiology A Chemistry
28. Disease Models for Rare Genetic Disorders
    Sivakumari Kanakarajan, Rajesh Selvaraj, Patheri Kunyil Kaleena · 2024 · Springer eBooks
29. Commercial trials of medicinal products; other types of interventions; health economic analysis
    Allan K. Hackshaw · 2024 · Wiley eBooks
30. Preface
    Yechiel Michael Barilan · 2022 · Oxford University Press eBooks
31. Author’s Biography
    Yechiel Michael Barilan, Margherita Brusa, Aaron J. Ciechanover · 2022 · Oxford University Press eBooks
32. Copyright Page
    Yechiel Michael Barilan, Margherita Brusa, Aaron J. Ciechanover · 2022 · Oxford University Press eBooks
33. Copyright Page
    John H. Evans · 2020
34. Notes
    John H. Evans · 2020
35. TRANSGENE MANUFACTURING: FROM TOOLS TO APPLICATIONS
    Saeeda Wasim, Sharique Ahmad · 2024 · International Journal of Research -GRANTHAALAYAH
36. Surfactants as a means of delivering a reporter genetic construct based on binase suicide gene to tumor cells
    Дудкина Елена Владимировна, Elmira A. Vasilieva, Ульянова Вера Владимировна, Lucia Ya. Zakharova, Olga N. Ilinskaya · 2024 · Биоорганическая химия
37. Evaluation of the functional activity and specificity of the hSLPI gene promoter
    Дудкина Елена Владимировна, Alexander S. Kosnyrev, Ульянова Вера Владимировна, Alsu I. Nadyrova, Polina S. Morozova, Elena A. Kupriyanova, Olga N. Ilinskaya · 2024 · Russian Journal of Oncology
38. Licensing Processes for Gene Therapy Products: Approved and Pending Clinical Trials in the World and Turkey
    Coşkun Sılan, Buket Güngör · 2024
39. Adeno-associated virus-mediated gene therapy in central nervous system genetic disorders
    Qinglan Ling, Andrea Boitnott, Irvin T. Garza, Widler Casy, Frances C. Shaffo, Sarah E. Sinnett, Steven James Gray · 2024 · Elsevier eBooks
40. Preclinical development of viral vector gene therapies
    Mary S. Newman, Eloïse Hudry, Jacqueline A. Brassard, Justine J. Cunningham · 2024 · Elsevier eBooks
41. Gene therapy for neurodegenration
    Trideva Sastri Koduru, Riyaz Ali M. Osmani, K. Madhuchandra · 2024 · Elsevier eBooks
42. Role of genetic mechanism in cancer
    Kirti Chauhan, Rashmi Rana · 2024 · Elsevier eBooks
43. Gene-Guided Drugs
    Yuda Zhang, Tian Xu · 2024 · Springer eBooks
44. Targeting Adipose Tissue: Therapeutic Strategies and Future Directions
    Bingyang Dai, Lizhen Zheng, Ling Qin · 2024 · Contemporary Endocrinology
45. Artificial Intelligence and Gene Therapy in Ophthalmic Diseases: Current Landscape and Future Directions
    Wenjia Lu, Shanshan Li, Xin Kinson Jin · 2024 · International Conference on Smart Healthcare and Wearable Intelligent Devices (SHWID)
46. Systemic Senolysis in Naturally Aged Mice Using a FAST-PLV Gene Therapy Approach
    John D. Lewis, Henry Garcia, Douglas Brown, Arun Raturi, Jamil Nehme, Prakash Bhandari, Ping Wee, Marco Malavolta, Liliya Grin, Héctor Vega et al. · 2024 · Research Square
47. Identification of the SUMOylation Gene Signature in Colon Cancer by Transcriptome and Mendelian Randomization Integration
    Xiaobin Zhang, Qingshui Yang, Zongyu Liang, Li Zhu, Chunlei Lu · 2025 · European Journal of Cancer Care
48. Genome editing in neurodegenerative diseases: risk analysis, technological challenges, and prospects for clinical application
    Lidia Semyonovna Evert, Tatyana Vitalyevna Potupchik, Olga Fedorovna Veselova, I. Svetlakova, B. Panchenko, R. Kudasheva, A. Melnikova · 2025 · Molekulyarnaya Meditsina (Molecular medicine)
49. Advanced gene therapy in Parkinson’s disease through innovations in drug delivery systems
    Phuong-Anh Tran Nguyen, Thuy-vi Nguyen, Soyeun Park · 2025 · Journal of Pharmaceutical Investigation
50. Gene Therapy of Cancer
    Fatemeh Davodabadi, Javad Arabpour, Manisha Nigam · 2025 · Interdisciplinary biotechnological advances
51. Viral Vector Construction
    Suneetha Vuppu, Toshika Mishra, Shatakshi Mishra, Bala Kumar Stany, Anushka Das · 2025
52. S100A4-shRNA mitigates autophagy, reduces inflammation, and improves cardiac functionality in MIRI
    Guangwei Huang, Qing Huang, Chenrui Mou, Anna Duan, Fujiao He, Hai‐Long Dai · 2025 · International Journal of Cardiology Cardiovascular Risk and Prevention
53. Nucleic Acid-Based Systems for Regenerative Medicine
    Leonardo Martín, Dawid P. Grzela · 2025 · Springer eBooks
54. CRISPR Therapies for Alzheimer’s Disease
    Jichao Sun, Subhojit Roy · 2025 · Springer eBooks
55. Probing the metabolic regulator and candidate tumor suppressor ALDH1L1 as a target for non-small cell lung cancer gene therapy
    Amira A. Abdellatef, Blake R. Rushing, Susan Sumner, Natalia I. Krupenko, Sergey A. Krupenko · 2025 · Molecular Therapy Oncology
56. Marine-based biopolymers for gene delivery & DNA repair
    Farhatun Najat Maluin, Haliza Katas, Khairul Anwar Ishak · 2025 · Elsevier eBooks
57. Adenovirus-based vaccines transduce and activate human Langerhans cells
    Elina Gerber-Tichet, Thi Hong Giang Ngo, Fabien P. Blanchet, Eric J. Kremer · 2025 · bioRxiv (Cold Spring Harbor Laboratory)
58. Predicting Airborne Volatile Organic Compound Transport in Highly Sensitive In Vitro Processes and Biopharmaceutical Manufacturing Facilities with Kinetic Models
    Jason S. Russack, John T. Fox, Huey T. Huynh, Kathryn Colonna Worrilow, Derick G. Brown · 2025 · Applied In Vitro Toxicology
59. Gene Therapy: Revolutionizing the Beauty Industry with Cosmetics
    Ganesh Sonawane, Arshi Khanam, Shweta Sharma, Kajal Vijay Pansare, Ritu Mehra Gilhotra, Prashant Kumar Dhakad · 2025 · BENTHAM SCIENCE PUBLISHERS eBooks
60. Biotechnological potentials of marine bacteria in the production of enzymes
    Olugbenga Solomon Bello, Kayode Adesina Adegoke, Mayowa Emmanuel Oyedokun, Victoria Abosede Ogungbire, Oluwakemi Christiana Alao, Olatunde Sunday Oladeji, Oyeronke Olubunmi Bello, Esther Olajumoke Olagunju · 2025 · Elsevier eBooks
61. Development of recombinant anti-TLR2 antibodies and PLGA nanoparticle-based gene therapy for the treatment of neuropathic pain
    Subeen Lee, Jaekyung Jeon, Hyunji Lee, Ellane Eda Barcelon, Jinpyo Hong, Sung Joong Lee · 2026 · Molecular Therapy
62. GEN TERAPIYASI VA KELAJAKDA IRSIY KASALLIKLARNI DAVOLASH IMKONIYATLARI
    Yakubova Farida Temurovna, Toshpo`latova Muslima Azamat qizi · 2025 · Journal of new century innovations
63. GEN TERAPIYASI VA KELAJAKDA IRSIY KASALLIKLARNI DAVOLASH IMKONIYATLARI
    Yakubova Farida Temurovna, Qurbonova Joziba Faxriddin qizi · 2025 · Journal of new century innovations
64. Colorectal Cancer Pathogenesis and Treatment Strategies: Insights into the Role of p53
    Mohammad Kordkatouli, Mahmoud Heidari, Nasrinsadat Azami, Javad Poursamimi · 2025 · Multidisciplinary Cancer Investigation
65. From Microbes to Medicine: Bacteriotherapy's Emerging Role in Cancer Treatment Strategies
    Anjana Goel, Istuti Saraswat, Ayushi Sharma, Jaikishan Chaudhary · 2025 · Current Cancer Therapy Reviews
66. Progress in Multifunctional and Multimodal Biomaterials for Therapeutic Applications
    Sérgio R. S. Veloso, Valéria Gomes, Raquel G. D. Andrade, Beatriz D. Cardoso, Ana Rita O. Rodrigues, Elisabete M. S. Castanheira · 2025 · Advances in material research and technology
67. Nanomaterials for Gene Therapy in Animal Health
    Shveta Bathla · 2026 · Smart nanomaterials technology
68. Modulation of Contactless High Intensity Pulsed Electromagnetic Field Induced Electroporation and Gene Delivery Efficacy Using Various Nanoparticles
    Tamara Polajžer, Matej Kranjc, Slavko Kralj, Maja Caf, Rok Romih, Samo Hudoklin, Vitalij Novickij, Damijan Miklavčič A · 2026 · Bioelectricity
69. Elucidating the Relationship Between Physicochemical Properties and Gene Delivery of Covalently Tethered Cationic Surfactants
    Hadi Muhammad, Chandrani Samadder, Venkatesh Ravula, Praveen Kumar Vemula · 2026 · ChemNanoMat
70. Genomic Context and Insert Orientation in the Regulation of Transgene Expression in Adenoviral Vectors
    Anna Muravyeva, Svetlana Smirnikhina · 2026 · International Journal of Molecular Sciences
71. Thérapie génique pour l’amyotrophie spinale à l’aide de vecteur AAV
    Aurore Besse · 2019
72. Application of lentiviral vector in vaccinology
    Min‐Wen Ku · 2020 · theses.fr (ABES)
73. Prodrogues d’alkylphospholipides (pro-APLs) pour une nouvelle approche thérapeutique du cancer par les lipides antitumoraux
    Boris Gaillard · 2019
74. Rôle de la rupture membranaire dans l'activation de la réponse antivirale lors d'infection par l’Adénovirus
    Noémie Pied · 2018 · theses.fr (ABES)
75. Conception de matériaux π-conjugués pour la reconnaissance et la délivrance d’ADN
    Clément Kotras · 2019
76. Transfert de gènes non-viral à destination des muscles squelettiques par injection hydrodynamique via la veine saphène : pistes d'optimisations et mise en application chez la souris
    Yann Thierry Le Guen · 2019
77. Modification chimique d’AAV pour la thérapie génique
    Aurélien Leray · 2021 · theses.fr (ABES)
78. L'acceptabilité des biotechnologies médicales : les cas spécifiques de la thérapie génique et de la xénotransplantation
    Cécile Fraux · 2021
79. Auto-assemblage de polymères dynamiques et reconnaissance d'acides nucléiques
    Maëva Coste · 2021
80. Role des cellules lymphoides innees humaines (ILC) dans la reponse immunitaire contre les adenovirus chez un hote avec une immunite preexistante
    Océane Paris · 2021
81. Séroprévalence des anticorps neutralisants dirigés contre les adénovirus de types C5, D26 et B35 au Burkina Faso et au Tchad : impacts sur l’utilisation de vecteurs dérivés des Adénovirus dans un contexte de vaccination
    Tigandiba Ouoba · 2021
82. Immunogenicity of recombinant Associated Virus-derived Vectors (rAAV) : how rAAV interact with the innate immune system ?
    Samer Masri · 2022 · theses.fr (ABES)
83. Place de la préférence du patient et de la société dans l’évaluation des technologies de santé en France
    Lylia Chachoua · 2023
84. CRISPR-Cas9-based strategies for enhanced targeted integration
    Laurie Lacombe · 2024
85. Étude du canal sodique cardiaque dans un modèle murin de troubles du rythme pour une nouvelle approche thérapeutique
    Marine Ferrand · 2025 · theses.fr (ABES)
86. Engineering mRNA therapeutics for protein supplementation: Challenges and future horizons
    Yiyang Tao, Yue Zhao, Qia Su, Jianxin Pan, Jianguo Yin, Congcong Xu · 2024 · BME Horizon
87. Introduction to Gene Therapy
    Sachin Kumar · 2026 · Springer eBooks
88. Challenges and opportunities in continuous bioprocessing of lentiviral vectors and adeno-associated viral vectors
    Alexandra Solis Olivares, Agnes Julia L. Aparte, Dale J. Stibbs, Pedro Silva Couto, Qasim A. Rafiq · 2026 · Biotechnology Advances
89. Gene therapy development for retinal diseases
    Felix F. Reichel, Julia-Sophia Bellingrath, Petèr Király, M. DOMINIK FISCHER · 2026 · Handbook of clinical neurology
90. Unveiling the Silent Regulators: Noncoding RNAs in Parasitic Disease Diagnosis and Therapy
    Neyon Loku Gamage, Koshila Ranasinghe · 2026 · Journal of Parasitology Research
91. Inborn Errors of Metabolism: Pathophysiological Insights, Diagnostic Advances, and Evolving Treatment Paradigms
    Roshni G. Sadaria · 2026 · Annals of African Medicine
92. Viral vectors in drug delivery: Design and applications
    Neeraj Kumar Chouhan, Mani Sharma, Mohini Rawat, Mamta N. Talati, Harpreet Kaur, Abhishek Sharma, Kuldeep Vinchurkar · 2026 · Elsevier eBooks
93. An Intermediate‐Centric View of Cascade Cancer Nanotherapeutics
    Miaomiao Sun, Xu Liu, Xiaohuan Sun, Jie Han · 2026 · Chemistry - A European Journal
94. Genome-Wide Integration Site Profiling of Multi-Component CAR T-Cell Engineering Systems with ADA1/CD26 Co-Transduction
    Kevin Song, Yue Hu, Xiao‐Tong Song · 2026 · Biomedicines
95. Unlocking the potential of bacteriophage-based therapeutic gene delivery in hepatocellular carcinoma
    Sreemoyee Mitra, Damini, Mahima Devi, Sreyosi Guha Niyogi, Utkarsh Pratap Singh, Debanjan Lo, Hitesh Chandra Bishtania, Shubham Thakur · 2026 · Journal of the Egyptian National Cancer Institute
96. Preparation of Polymeric Nanoparticles for Gene Delivery
    Emre Şefik Çağlar, Emine Saldamlı · 2026 · Methods in molecular biology
97. CRISPR-Based Genome Editing and Delivery Systems: Advances, Challenges and Future Directions
    Anroop Kaur, Ritika Chanan, Mehga Sharma, Shailja Sharma, Devender Sharma · 2026 · IntechOpen eBooks
98. Gene Editing/CRISPR
    Thales A. C. de Guimarães, Stephen H. Tsang, Thiago Cabral · 2026 · Springer eBooks
99. Metabolic boosting via mitochondrial transfer for enhanced cell-based wound healing therapy
    Seung Hyun Lee, Hyun Su Park, Ga Ryang Ko, Yoonji Song, Jiyu Hyun, Suk Ho Bhang, Jung Seung Lee · 2026 · Journal of Tissue Engineering
100. Gene Therapy for Corneal Diseases
     Basanta Bhujel, Kyu Sang Eah, Soon Suk Kang, Ho Seok Chung, Jae Yong Kim · 2026 · BioTech