A Compact, High-Accuracy Cas9 with a Dinucleotide PAM for In Vivo Genome Editing

Cited by (265)

Items 201–265 of 265

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  16. Spatially concentrated adenine base editors efficiently correct PLP1 mutations in oligodendrocytes
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  18. Advancements in genome editing tools and technologies for improvement of horticultural crops
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  19. The CRISPR/Cas-associated scaRNA modulates efeUOB expression and stress responses in Neisseria meningitidis
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  21. Translating base editors: a decade of progress from the bench to the clinic
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  26. DeepEmbCas9: Cas9 coevolution and sgRNA structural information for CRISPR-Cas9 cleavage activity prediction
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  27. CRISPR-Cas Systems Reduced to a Minimum
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  28. Development of therapeutic genome engineering in laminin-α2-deficient congenital muscular dystrophy
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  29. Modulating the activity of CRISPR/Cas9 genome editing by small molecules
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  30. 神先先生の古稀及び定年を迎えられるにあたって (神先秀雄・薄田桂・友松芳郎三教授古稀記念特輯)
    宏 井上 · 1981 · 関西大学社会学部紀要
  31. Faculty Opinions recommendation of Inhibition of histone deacetylase 1 (HDAC1) and HDAC2 enhances CRISPR/Cas9 genome editing.
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  32. CRISPR Cas
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  35. Quantitative assaying of SpCas9-NG with fluorescent reporters
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  36. Molecular Mechanisms of Type II CRISPR ‐ Cas Systems
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  38. EDSpliCE, a CRISPR-Cas9 gene editing platform to rescue splicing, effectively corrects inherited retinal dystrophy-associated splicing defects
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  39. Gene Expression and Editing in Mammalian Retinal Ganglion Cells
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  40. Characterization of the genome editing with miniature nucleases TnpB, IscB and enIscB in Escherichia coli strains
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  41. CRISPR/Cas9-based genetic engineering for translational research in neurological disorders
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  42. Rational Design of Enhanced Nme2Cas9 and Nme2 Smu Cas9 Nucleases and Base Editors
    Nathan Bamidele, Aditya Valji Ansodaria, Zexiang Chen, Haoyang Cheng, Rebecca Panwala, Eva Jazbec, Erik J. Sontheimer · 2024 · bioRxiv (Cold Spring Harbor Laboratory)
  43. Nano-Polymers as Cas9 Inhibitors
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  44. Machine learning-driven optimization of specific, compact, and efficient base editors via single-round diversification
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  46. Double-stranded DNA deaminase DddAE1347A can increase the efficiency and targeting range of cytidine base editors
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  47. Additional file 2 of Engineered domain-inlaid Nme2Cas9 adenine base editors with increased on-target DNA editing and targeting scope
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  48. Additional file 3 of Engineered domain-inlaid Nme2Cas9 adenine base editors with increased on-target DNA editing and targeting scope
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  49. Additional file 1 of Short cell-penetration peptide conjugated bioreducible polymer enhances gene editing of CRISPR system
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    Ding Zhao, Gao, Xun, Zhou, Jiale, Li, Jinze, Yuqiang Qian, Wang, Di, Niu, Wenchao, Tao Zhang, Hu, Mingyang, Haoyang Xiong et al. · 2023 · Figshare
  51. In vivo genome editing with a novel Cj4Cas9
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  52. Iterative engineering of a compact Cas9 ortholog for in vivo gene editing via single AAV delivery
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  59. Adenine base editing correction of LMNA c.745C>T (p.R249W) in congenital muscular dystrophy myoblasts improves cellular phenotype while revealing deleterious p.L248P bystander effects
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