Correction of a Genetic Disease in Mouse via Use of CRISPR-Cas9

Cited by (619)

Items 601–619 of 619

1. CRISPR/Cas9: the future of human gene editing
   Nur Diyana Zulkifli, Sa’udah Badriah Mohd Sani, Cheng Heng Wong, Munirah Mahadzan, Muhammad Hazeeq Asyraf Suhimi, Nurulisa Zulkifli, Kumitaa Theva Das · 2025 · Elsevier eBooks
2. Additional file 2 of ssDNA is not superior to dsDNA as long HDR donors for CRISPR-mediated endogenous gene tagging in human diploid RPE1 and HCT116 cells
   Akira Mabuchi, Shoji Hata, Mariya Genova, Chiharu Tei, Kei Ito, Masayasu Hirota, Takuma Komori, Masamitsu Fukuyama, Takumi Chinen, Toyoda, Atsushi et al. · 2023 · Figshare
3. Additional file 1 of Prime editing in mice reveals the essentiality of a single base in driving tissue-specific gene expression
   Pan Gao, Lyu, Qing, Ghanam, Amr R., Cícera Regina Lazzarotto, Gregory A. Newby, Zhang, Wei, Mihyun Choi, Orazio J. Slivano, Holden, Kevin, Walker, John A. et al. · 2021 · Figshare
4. Additional file 9 of Prime editing in mice reveals the essentiality of a single base in driving tissue-specific gene expression
   Pan Gao, Lyu, Qing, Ghanam, Amr R., Cícera Regina Lazzarotto, Gregory A. Newby, Zhang, Wei, Mihyun Choi, Orazio J. Slivano, Holden, Kevin, Walker, John A. et al. · 2021 · Figshare
5. Additional file 1 of In vivo genome editing in mouse restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers
   Chen, Menglong, Shi, Hui, Shixue Gou, Wang, Xiaomin, Li, Lei, Jin, Qin, Wu, Han, Zhang, Huili, Li, Yaqin, Wang, Liang et al. · 2021 · Figshare
6. Additional file 1 of CRISPR/Cas9-mediated gene knockout and interallelic gene conversion in human induced pluripotent stem cells using non-integrative bacteriophage-chimeric retrovirus-like particles
   Joffrey Mianné, Amel Nasri, Van, Chloé Nguyen, Chloé Bourguignon, Mathieu Fieldès, Engi Ahmed, Christine T Duthoit, Martin, Nicolas, Hugues Parrinello, Anaïs Louis et al. · 2022 · Figshare
7. Additional file 1 of ssDNA is not superior to dsDNA as long HDR donors for CRISPR-mediated endogenous gene tagging in human diploid RPE1 and HCT116 cells
   Akira Mabuchi, Shoji Hata, Mariya Genova, Chiharu Tei, Kei Ito, Masayasu Hirota, Takuma Komori, Masamitsu Fukuyama, Takumi Chinen, Toyoda, Atsushi et al. · 2023 · Figshare
8. Etude de la correction de mutations non sens par de nouvelles molécules pouvant servir d'approches thérapeutiques ciblées
   Hana Benhabiles · 2017 · theses.fr (ABES)
9. Création de résistance à large spectre contre la bactériose foliaire du riz au Mali
   Hinda Doucouré · 2017
10. In vivo exploration of the impact of ribosome biogenesis alterations on intestinal homeostasis and tumorigenesis in the adult mouse
    Aurélien Raveux · 2018 · theses.fr (ABES)
11. Protéinuries génétiques causées par déficit de réabsorption tubulaire proximale
    Mathilde Bedin · 2019 · theses.fr (ABES)
12. Émergence virale et mécanismes associés : exemples de la recombinaison non-réplicative chez les entérovirus et de la restriction du SARS-CoV-2 par DAXX
    Alice Mac Kain · 2021 · theses.fr (ABES)
13. Thérapie génique par CRISPR/Cas9 pour corriger des épithéliums bronchiques dérivés de cellules souches pluripotentes induites (iPSCs) de patients atteints de dyskinésie ciliaire primitive (DCP) : une preuve de concept
    Joffrey Mianné · 2020 · theses.fr (ABES)
14. The role of meiotic genes in primary ovarian insufficiency and non-obstructive azoospermia: a genetic perspective
    Kimiya Padidar, Maryam Varkiani, Mehdi Totonchi · 2026 · Middle East Fertility Society Journal
15. Molecular Engineering of CRISPR Nanomaterials toward Cancer Theranostics
    Guimei Li, Siyuan Wang, Jingjing Zhang · 2026 · ACS Nano Medicine
16. Contemporary Research Methodologies in Ayurveda: From Molecule to Man
    Reshma Shettigar · 2026
17. hnRNPK condensates facilitate enhancer–promoter looping and RNA polymerase II recruitment
    Rong Ye, Hailian Zhao, Juan Chen, Qigui Wu, Di Wang, Zhaokui Cai, Ruoyan Wang, Jingxin Li, Tiantian Cheng, Ming Zhang et al. · 2026 · Nature Genetics
18. CRISPR–Cas9 genome editing: technological advances, delivery strategies and precision engineering of primary cells for therapeutic application in genetic disorders and diabetes mellitus
    M N Islam, Md Mahmudul Islam, Han Feng, Sm Faysal Bellah, M Morsed Zaman Miah, M. Hossain · 2026 · Molecular Biology Reports
19. Disrupted valine metabolism and SCPC-mediated neurological toxicity in ECHS1 deficiency
    Meghan M. Eller, Madison A. Bunce, Mamta Verma, Raegan M. Adams, Xiaorong Fu, Alina P. Montalbano, Felix Nitschke, Shawn C. Burgess, Rachel M. Bailey · 2026 · Frontiers in Molecular Biosciences