Gene targeting with viral vectors

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GENETIC EXCHANGE IN SALMONELLA

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High frequency targeting of genes to specific sites in the mammalian genome

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Circular Intermediates of Recombinant Adeno-Associated Virus Have Defined Structural Characteristics Responsible for Long-Term Episomal Persistence in Muscle Tissue

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Patterns of Integration of DNA Microinjected into Cultured Mammalian Cells: Evidence for Homologous Recombination Between Injected Plasmid DNA Molecules

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Disruption of HAUSP gene stabilizes p53.

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Reexamination of Gene Targeting Frequency as a Function of the Extent of Homology between the Targeting Vector and the Target Locus

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Human gene targeting by viral vectors

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Gene Targeting in Stem Cells from Individuals with Osteogenesis Imperfecta

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Adeno-associated virus vectors preferentially transduce cells in S phase.

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Endocytosis and Nuclear Trafficking of Adeno-Associated Virus Type 2 Are Controlled by Rac1 and Phosphatidylinositol-3 Kinase Activation

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Cre-stimulated recombination atloxP-containing DNA sequences placed into the mammalian genome

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Reexamination of gene targeting frequency as a function of the extent of homology between the targeting vector and the target locus.

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Adeno-associated virus 2 co-receptors?-first reply

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Homologous recombination between plasmids in mammalian cells can be enhanced by treatment of input DNA.

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DNA-damaging agents greatly increase the transduction of nondividing cells by adeno-associated virus vectors

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Frequency and Stability of Chromosomal Integration of Adenovirus Vectors

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DNA synthesis and topoisomerase inhibitors increase transduction by adeno-associated virus vectors.

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X-Linked Inhibitor of Apoptosis Protein (XIAP) Is a Nonredundant Modulator of Tumor Necrosis Factor-Related Apoptosis-Inducing Ligand (TRAIL)- Mediated Apoptosis in Human Cancer Cells

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Analysis of Gene Targeting and Intrachromosomal Homologous Recombination Stimulated by Genomic Double-Strand Breaks in Mouse Embryonic Stem Cells

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Targeted transgene insertion into human chromosomes by adeno-associated virus vectors

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Facile methods for generating human somatic cell gene knockouts using recombinant adeno-associated viruses

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Efficient Gene Targeting Mediated by Adeno-Associated Virus and DNA Double-Strand Breaks

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Recombination During Gene Transfer into Mouse Cells Can Restore the Function of Deleted Genes

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High-Efficiency Ligation and Recombination of DNA Fragments by Vertebrate Cells

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Design and Packaging of Adeno-Associated Virus Gene Targeting Vectors

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Human Gene Targeting by Adeno-Associated Virus Vectors Is Enhanced by DNA Double-Strand Breaks

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Homologous recombination in mammalian cells mediates formation of a functional gene from two overlapping gene fragments.

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Intracellular Viral Processing, Not Single-Stranded DNA Accumulation, Is Crucial for Recombinant Adeno-Associated Virus Transduction

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Rate Limiting Steps of AAV Transduction and Implications for Human Gene Therapy

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Novel use of synthetic oligonucleotide insertion mutants for the study of homologous recombination in mammalian cells.

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Adenovirus As An Integrating Vector

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Gene Targeting with Retroviral Vectors: Recombination by Gene Conversion into Regions of Nonhomology

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High‐fidelity correction of mutations at multiple chromosomal positions by adeno‐associated virus vectors

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Introduction of single base substitutions at homologous chromosomal sequences by adeno‐associated virus vectors

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Targeted Correction of Single-Base-Pair Mutations with Adeno-Associated Virus Vectors under Nonselective Conditions

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Correction of a Deletion Mutant by Gene Targeting with an Adenovirus Vector

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Gene targeting in mouse embryonic stem cells with an adenoviral vector

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Chromosomal Integration Pattern of a Helper-Dependent Minimal Adenovirus Vector with a Selectable Marker Inserted into a 27.4-Kilobase Genomic Stuffer

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Gene targeting in human somatic cells

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Chromosomal Integration and Homologous Gene Targetingby Replication-Incompetent Vectors Based on the Autonomous ParvovirusMinute Virus ofMice

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Gene targeting with a replication-defective adenovirus vector

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Gene Targeting by Adeno-Associated Virus Vectors Is Cell-Cycle Dependent

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Correction of a deletion mutant by gene targeting with an adenovirus vector.

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Effect of cell cycle position on transformation by microinjection

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Nuclear localization signal and cell synchrony enhance gene targeting efficiency in primary fetal fibroblasts

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Efficient PRNP Gene Targeting in Bovine Fibroblasts by Adeno-Associated Virus Vectors

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Long targeting arms do not increase the efficiency of homologous recombination in the β-globin locus of murine embryonic stem cells

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Targeted insertions of two exogenous collagen genes into both alleles of their endogenous loci in cultured human cells: the insertions are directed by relatively short fragments containing the promoters and the 5' ends of the genes.

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Gene Targeting and Embryonic Stem Cells

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Adeno‐associated virus gene repair corrects a mouse model of hereditary tyrosinemia in vivo†‡

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Gene targeting in vivo by adeno‐associated virus vectors

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Targeted Genome Modifications Using Integrase-deficient Lentiviral Vectors

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Developments in Non-Viral Vector Researches in Gene Therapy

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Recombinant Adeno-Associated Viral Vectors for CNS Gene Therapy

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Cationic lipids used in non-viral gene delivery systems

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Tailoring the AAV vector capsid for gene therapy

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Adeno-Associated Virus (AAV) as a Vector for Gene Therapy

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