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Preclinical Demonstration of Lentiviral Vector-mediated Correction of Immunological and Metabolic Abnormalities in Models of Adenosine Deaminase Deficiency

Carbonaro, Denise A, Zhang, Lin, Jin, Xiangyang, Montiel-Equihua, Claudia, Geiger, Sabine, Carmo, Marlene, Cooper, Aaron, Fairbanks, Lynette, Kaufman, Michael L, Sebire, Neil J, Hollis, Roger P, Blundell, Michael P, Senadheera, Shantha, Fu, Pei-Yu, Sahaghian, Arineh, Chan, Rebecca Y, Wang, Xiaoyan, Cornetta, Kenneth, Thrasher, Adrian J, Kohn, Donald B, Gaspar, H Bobby·2014·Molecular Therapy
DOI 10.1038/mt.2013.265
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Research works printed but not linked: 46

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Metadata

Authors
Carbonaro, D. A., Zhang, L., Jin, X., Montiel-Equihua, C., Geiger, S., Carmo, M., Cooper, A., Fairbanks, L., Kaufman, M. L., Sebire, N. J., Hollis, R. P., Blundell, M. P., Senadheera, S., Fu, P.-Y., Sahaghian, A., Chan, R. Y., Wang, X., Cornetta, K., Thrasher, A. J., Kohn, D. B., & Gaspar, H. B.
Venue
Molecular Therapy
Publisher
Elsevier BV
Published
2014-03
Volume
22
Issue
3
Pages
607-622
ISSN
1525-0016
DOI
10.1038/mt.2013.265
Cited by
78
References
6
Language
en
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CoChat. (2026). Citation check: Preclinical Demonstration of Lentiviral Vector-mediated Correction of Immunological and Metabolic Abnormalities in Models of Adenosine Deaminase Deficiency. https://app.cochat.ai/papers/10.1038/mt.2013.265
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Carbonaro, D. A., Zhang, L., Jin, X., Montiel-Equihua, C., Geiger, S., Carmo, M., Cooper, A., Fairbanks, L., Kaufman, M. L., Sebire, N. J., Hollis, R. P., Blundell, M. P., Senadheera, S., Fu, P.-Y., Sahaghian, A., Chan, R. Y., Wang, X., Cornetta, K., Thrasher, A. J., . . . Gaspar, H. B. (2014). Preclinical Demonstration of Lentiviral Vector-mediated Correction of Immunological and Metabolic Abnormalities in Models of Adenosine Deaminase Deficiency. Molecular Therapy. https://doi.org/10.1038/mt.2013.265