Functional correction in mouse models of muscular dystrophy using exon-skipping tricyclo-DNA oligomers

Goyenvalle, Aurélie, Griffith, Graziella, Babbs, Arran, Andaloussi, Samir El, Ezzat, Kariem, Avril, Aurélie, Dugovic, Branislav, Chaussenot, Rémi, Ferry, Arnaud, Voit, Thomas, Amthor, Helge, Bühr, Claudia, Schürch, Stefan, Wood, Matthew J A, Davies, Kay E, Vaillend, Cyrille, Leumann, Christian, Garcia, Luis·2015·Nature Medicine

DOI 10.1038/nm.3765

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Authors: Goyenvalle, A., Griffith, G., Babbs, A., Andaloussi, S. E., Ezzat, K., Avril, A., Dugovic, B., Chaussenot, R., Ferry, A., Voit, T., Amthor, H., Bühr, C., Schürch, S., Wood, M. J. A., Davies, K. E., Vaillend, C., Leumann, C., & Garcia, L.
Venue: Nature Medicine
Publisher: Springer Science and Business Media LLC
Published: 2015-02-02
Volume: 21
Issue: 3
Pages: 270-275
ISSN: 1078-8956 (ISSN-L)
1546-170X
DOI: 10.1038/nm.3765
OpenAlex: W2062078686
Cited by: 327
References: 0
FWCI: 19.81
Type: journal article
Language: en
Open access: closed

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