In vivo gene transfer to the mouse eye using an HIV-based lentiviral vector; efficient long-term transduction of corneal endothelium and retinal pigment epithelium

Self-Inactivating Lentivirus Vector for Safe and Efficient In Vivo Gene Delivery

Zufferey, R., Dull, T., Mandel, R. J., Bukovsky, A., Quiroz, D., Naldini, L., & Trono, D. (1998) · Journal of Virology · doi:10.1128/jvi.72.12.9873-9880.1998 · Cited by 1,815

HIV-1 Genome Nuclear Import Is Mediated by a Central DNA Flap

Zennou, V., Petit, C., Guétard, D., Nerhbass, U., Montagnier, L., & Charneau, P. (2000) · Cell · doi:10.1016/s0092-8674(00)80828-4 · Cited by 864

Stable and efficient gene transfer into the retina using an HIV-based lentiviral vector

Miyoshi, H., Takahashi, M., Gage, F. H., & Verma, I. M. (1997) · Proceedings of the National Academy of Sciences · doi:10.1073/pnas.94.19.10319 · Cited by 497

Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus

Flannery, J. G., Zolotukhin, S., Vaquero, M. I., LaVail, M. M., Muzyczka, N., & Hauswirth, W. W. (1997) · Proceedings of the National Academy of Sciences · doi:10.1073/pnas.94.13.6916 · Cited by 409

Gene transfer into the mouse retina mediated by an adeno-associated viral vector

Ali, R. R. (1996) · Human Molecular Genetics · doi:10.1093/hmg/5.5.591 · Cited by 258

Cell cycle protein expression and proliferative status in human corneal cells.

Joyce, N. C., Meklir, B., Joyce, S. J., & Zieske, J. D. (1996) · PubMed · Cited by 251

Immune Responses Limit Adenovirally Mediated Gene Expression in the Adult Mouse Eye

Reichel, M., Ali, R., Thrasher, A., Hunt, D., Bhattacharya, S., & Baker, D. (1998) · Gene Therapy · doi:10.1038/sj.gt.3300691 · Cited by 106

Efficient and sustained transgene expression in human corneal cells mediated by a lentiviral vector

Wang, X.-Y., Appukuttan, B., Ott, S. H., Patel, R. J., Irvine, J. A., Song, J., Park, J.-H. C., Smith, R. R., & Stout, J. T. (2000) · Gene Therapy · doi:10.1038/sj.gt.3301075 · Cited by 94

The cellular basis of aqueous outflow regulation

Francis, B. A., & Alvarado, J. A. (1997) · Current Opinion in Ophthalmology · doi:10.1097/00055735-199704000-00005 · Cited by 25

Stable and efficient gene transfer into the mutant retinal pigment epithelial cells of the Mitfvit mouse using a lentiviral vector

Galileo, D. S., Hunter, K., & Smith, S. B. (1999) · Current Eye Research · doi:10.1076/ceyr.18.2.135.5376 · Cited by 20

Porcine endogenous retroviruses PERV A and A/C recombinant are insensitive to a range of divergent mammalian TRIM5α proteins including human TRIM5α

Wood, A., Webb, B. L. J., Bartosch, B., Schaller, T., Takeuchi, Y., & Towers, G. J. (2009) · Journal of General Virology · doi:10.1099/vir.0.007377-0 · Cited by 31

Non-Primate Lentiviral Vectors and Their Applications in Gene Therapy for Ocular Disorders

Cavalieri, V., Baiamonte, E., & Iacono, M. L. (2018) · Viruses · doi:10.3390/v10060316 · Cited by 29

Cryopreservation and Lentiviral-Mediated Genetic Modification of Human Primary Cultured Corneal Endothelial Cells

Suh, L. H., Zhang, C., Chuck, R. S. H., Stark, W. J., Naylor, S., Binley, K. M., Chakravarti, S., & Jun, A. S. (2007) · Investigative Ophthalmology & Visual Science · doi:10.1167/iovs.06-0771 · Cited by 27

VIP and VIP Gene Silencing Modulation of Differentiation Marker N-Cadherin and Cell Shape of Corneal Endothelium in Human Corneas Ex Vivo

Koh, S. M., Chandrasekara, K., Abbondandolo, C. J., Coll, T. J., & Rutzen, A. R. (2008) · Investigative Ophthalmology & Visual Science · doi:10.1167/iovs.07-1543 · Cited by 26

Hare TRIM5α Restricts Divergent Retroviruses and Exhibits Significant Sequence Variation from Closely Related Lagomorpha TRIM5 Genes

Fletcher, A. J., Hué, S., Schaller, T., Pillay, D., & Towers, G. J. (2010) · Journal of Virology · doi:10.1128/jvi.01514-10 · Cited by 26

Gene therapy approaches to prolonging corneal allograft survival

Williams, K. A., Jessup, C. F., & Coster, D. J. (2004) · Expert Opinion on Biological Therapy · doi:10.1517/14712598.4.7.1059 · Cited by 25

Leber Congenital Amaurosis Caused by Mutations in GUCY2DPreprint

Boye, S. L. (2014) · Cold Spring Harbor Perspectives in Medicine · doi:10.1101/cshperspect.a017350 · Cited by 25

Gene Delivery to the Retina Using Lentiviral Vectors

Greenberg, K. P., Lee, E. S., Schaffer, D. V., & Flannery, J. G. (2007) · Springer eBooks · doi:10.1007/0-387-32442-9_36 · Cited by 24

Suppression of Choroidal Neovascularization in Mice by Subretinal Delivery of Multigenic Lentiviral Vectors Encoding Anti-Angiogenic MicroRNAs

Askou, A. L., Benckendorff, J. N. E., Holmgaard, A., Storm, T., Aagaard, L., Bek, T., Mikkelsen, J. G., & Corydon, T. J. (2017) · Human Gene Therapy Methods · doi:10.1089/hgtb.2017.079 · Cited by 24

In vivo gene transfer to the rat retina using herpes simplex virus type 1 (HSV-1)-based amplicon vectors

Fraefel, C., Mendes-Madeira, A., Mabon, O., Lefebvre, A., Meur, G. L., Ackermann, M., Moullier, P., & Rolling, F. (2005) · Gene Therapy · doi:10.1038/sj.gt.3302553 · Cited by 22

Efficient lentiviral gene transfer into corneal stroma cells using a femtosecond laser

Bemelmans, A., Arsenijévic, Y., & Majo, F. (2009) · Gene Therapy · doi:10.1038/gt.2009.41 · Cited by 22

The DEAD box RNA helicase DDX42 is an intrinsic inhibitor of positive‐strand RNA viruses

Bonaventure, B., Rebendenne, A., Valadão, A. L. C., Arnaud‐Arnould, M., Gracias, S., García-de-Gracia, F., McKellar, J., Labaronne, E., Tauziet, M., Vivet‐Boudou, V., et al. (2022) · EMBO Reports · doi:10.15252/embr.202154061 · Cited by 20

Development of photoreceptor‐specific promoters and their utility to investigate EIAV lentiviral vector mediated gene transfer to photoreceptors

Nicoud, M., Kong, J., Iqball, S., Kan, O., Naylor, S., Gouras, P., Allikmets, R. L., & Binley, K. (2007) · The Journal of Gene Medicine · doi:10.1002/jgm.1115 · Cited by 22

Inhibition of spumavirus gene expression by PHF11

Kane, M., Mele, V., Liberatore, R. A., & Bieniasz, P. D. (2020) · PLoS Pathogens · doi:10.1371/journal.ppat.1008644 · Cited by 21

Prospects for genetic modulation of corneal graft survival

Williams, K. A., Brereton, H. M., & Coster, D. J. (2008) · Eye · doi:10.1038/eye.2008.378 · Cited by 21

Evaluation of tolerance to lentiviral LV-RPE65 gene therapy vector after subretinal delivery in non-human primates.

Matet, A., Kostic, C., Bemelmans, A.-P., Moulin, A., Rosolen, S. G., Martin, S., Mavilio, F., Amirjanians, V., Stieger, K., Lorenz, B., et al. (2017) · Translational Research · doi:10.1016/j.trsl.2017.06.012 · Cited by 20

Targeting eEF1A reprograms translation and uncovers broad-spectrum antivirals against cap or m6A protein synthesis routes

Molina, E. M., Bech‐Serra, J. J., Franco‐Trepat, E., Jarne-Sanz, I., Perez‐Zsolt, D., Badía, R., Riveira‐Muñoz, E., García-Vidal, E., Sancho, L. R., Franco, S., et al. (2025) · Nature Communications · doi:10.1038/s41467-025-56151-y · Cited by 20

Cyclophilins and nucleoporins are required for infection mediated by capsids from circulating HIV-2 primary isolates

Mamede, J. I., Damond, F., de Bernardo, A., Matheron, S., Descamps, D., Battini, J., Sitbon, M., & Courgnaud, V. (2017) · Scientific Reports · doi:10.1038/srep45214 · Cited by 22

Genetically modified lentiviruses that preserve microvascular function protect against late radiation damage in normal tissues

Khan, A., Paget, J. T.-E. H., McLaughlin, M., Kyula, J., Wilkinson, M., Pencavel, T. D., Mansfield, D., Roulstone, V., Seth, R., Halle, M., et al. (2018) · Science Translational Medicine · doi:10.1126/scitranslmed.aar2041 · Cited by 20

Gene Therapy with Endogenous Inhibitors of Angiogenesis for Neovascular Age-Related Macular Degeneration: Beyond Anti-VEGF Therapy

Prea, S. M., Chan, E. C., Dusting, G. J., Vingrys, A. J., Bui, B. V., & Liu, G. (2015) · Journal of Ophthalmology · doi:10.1155/2015/201726 · Cited by 21

Abrogation of Marek’s disease virus replication using CRISPR/Cas9

Hagag, I. T., Wight, D. J., Bartsch, D., Sid, H., Jordan, I., Bertzbach, L. D., Schusser, B., & Kaufer, B. B. (2020) · Scientific Reports · doi:10.1038/s41598-020-67951-1 · Cited by 19

Gene Therapy in Corneal Transplantation

Qazi, Y., & Hamrah, P. (2013) · Seminars in Ophthalmology · doi:10.3109/08820538.2013.825297 · Cited by 18

Positive selection in dNTPase SAMHD1 throughout mammalian evolution

Monit, C., Morris, E. R., Ruis, C., Szafran, B., Thiltgen, G., Tsai, M.-H., Mitchison, N. A., Bishop, K. N., Stoye, J. P., Taylor, I. A., et al. (2019) · Proceedings of the National Academy of Sciences · doi:10.1073/pnas.1908755116 · Cited by 16

Spatiotemporal control of actomyosin contractility by MRCKβ signaling drives phagocytosis

Zihni, C., Georgiadis, A., Ramsden, C. M., Sánchez-Heras, E., Haas, A. J., Nommiste, B., Semenyuk, O., Bainbridge, J. W., Coffey, P. J., Smith, A. J., et al. (2022) · The Journal of Cell Biology · doi:10.1083/jcb.202012042 · Cited by 17

Retinal gene therapy: current progress and future prospects

Ku, C. A., & Pennesi, M. E. (2015) · Expert Review of Ophthalmology · doi:10.1586/17469899.2015.1035711 · Cited by 16

In situ regeneration of retinal pigment epithelium by gene transfer of E2F2: a potential strategy for treatment of macular degenerations

Kampik, D., Basche, M., Luhmann, U. F. O., Nishiguchi, K. M., Williams, J. A. E., Greenwood, J., Moss, S. E., Han, H. R., Azam, S. A., Durán, Y., et al. (2017) · Gene Therapy · doi:10.1038/gt.2017.89 · Cited by 16

Knockdown of NBCe1 In Vivo Compromises the Corneal Endothelial Pump

Cai-ling, L., Cheng, Q., Nguyen, T. T., & Bonanno, J. A. (2010) · Investigative Ophthalmology & Visual Science · doi:10.1167/iovs.10-5257 · Cited by 16

Absence of Functional and Structural Abnormalities Associated with Expression of EGFP in the Retina

Nour, M., Quiambao, A. B., Al‐Ubaidi, M. R., & Naash, M. I. (2003) · Investigative Ophthalmology & Visual Science · doi:10.1167/iovs.03-0663 · Cited by 16

Transduction of functionally active TAT fusion proteins into cornea

Guo, X., Hutcheon, A. E. K., & Zieske, J. D. (2004) · Experimental Eye Research · doi:10.1016/j.exer.2003.12.010 · Cited by 16

Subtype-specific differences in the development of accessory mutations associated with high-level resistance to HIV-1 nucleoside reverse transcriptase inhibitors

Koning, F., Castro, H., Dunn, D. T., Tilston, P., Cane, P. A., Mbisa, J. L., & on behalf of the UK Collaborative Group on HIV Drug Resistance (2013) · Journal of Antimicrobial Chemotherapy · doi:10.1093/jac/dkt012 · Cited by 15

Insights gained from gene therapy in animal models of retGC1 deficiency

Boye, S. L. (2014) · Frontiers in Molecular Neuroscience · doi:10.3389/fnmol.2014.00043 · Cited by 15

Intraocular mRNA delivery with endogenous MmPEG10-based virus-like particles

Li, M., Liu, Z., Wang, D., Ye, J., Shi, Z., Pan, C., Zhang, Q., Ju, R., Zheng, Y., & Liu, Y. (2024) · Experimental Eye Research · doi:10.1016/j.exer.2024.109899 · Cited by 15

The evolution of HIV-1 reverse transcriptase in route to acquisition of Q151M multi-drug resistance is complex and involves mutations in multiple domains

Mbisa, J. L., Gupta, R. K., Kabamba, D., Mulenga, V., Kalumbi, M., Chintu, C., Parry, C. M., Gibb, D. M., Walker, A. S., Cane, P. A., et al. (2011) · Retrovirology · doi:10.1186/1742-4690-8-31 · Cited by 14

How to keep injured CNS neurons viable—strategies for neuroprotection and gene transfer to retinal ganglion cells

Isenmann, S., Schmeer, C. W., & Kretz, A. (2004) · Molecular and Cellular Neuroscience · doi:10.1016/j.mcn.2004.01.005 · Cited by 13

What Is Next for Retinal Gene Therapy?Preprint

Vandenberghe, L. H. (2015) · Cold Spring Harbor Perspectives in Medicine · doi:10.1101/cshperspect.a017442 · Cited by 12

Prospects for gene therapy of inherited retinal disease

Bainbridge, J. W. (2009) · Eye · doi:10.1038/eye.2008.412 · Cited by 12

Corneal Epithelial Cell Culture Model for Pharmaceutical Studies

Toropainen, E. (2007) · Cited by 12

Gene Therapy for Retinal Dystrophies: Twenty Years in the Making

Ali, R. R. (2012) · Human Gene Therapy · doi:10.1089/hum.2012.2506 · Cited by 12

HIV-1 Capsid Rapidly Induces Long-Lived CPSF6 Puncta in Non-Dividing Cells, but Similar Puncta Already Exist in Uninfected T-Cells

Guedán, A., Burley, M., Caroe, E. R., & Bishop, K. N. (2024) · Viruses · doi:10.3390/v16050670 · Cited by 10

Clinical applications of retinal gene therapies

Fu, X., Huu, V. A. N., Duan, Y., Kermany, D., Valentim, C. C. S., Zhang, R., Zhu, J., Zhang, C. L., Sun, X., & Zhang, K. (2018) · Precision Clinical Medicine · doi:10.1093/pcmedi/pby004 · Cited by 12

A streamlined implementation of the glutamine synthetase-based protein expression system

Knox, R. G., Nettleship, J. E., Chang, V. T.-C., Hui, Z., Santos, A. M., Rahman, N., Ho, L., Owens, R. J., & Davis, S. J. (2013) · BMC Biotechnology · doi:10.1186/1472-6750-13-74 · Cited by 11

Modulation of Contact Inhibition by ZO-1/ZONAB Gene Transfer—A New Strategy to Increase the Endothelial Cell Density of Corneal Grafts

Kampik, D., Basche, M., Georgiadis, A., Luhmann, U. F. O., Larkin, F., Smith, A. J., & Ali, R. R. (2019) · Investigative Ophthalmology & Visual Science · doi:10.1167/iovs.18-26260 · Cited by 10

Lentiviral Vectors Containing a Retinal Pigment Epithelium Specific Promoter for Leber Congenital Amaurosis Gene Therapy

Bemelmans, A., Kostic, C., Hornfeld, D., Jaquet, M., Crippa, S. V., Hauswirth, W. W., Lem, J., Wang, Z., Schorderet, D. F., Munier, F. L., et al. (2006) · Advances in experimental medicine and biology · doi:10.1007/0-387-32442-9_35 · Cited by 10

Beyond retrovirus infection: HIV meets gene therapy

da Silva, F. H., Dalberto, T. P., & Nardi, N. B. (2006) · Genetics and Molecular Biology · doi:10.1590/s1415-47572006000200027 · Cited by 9

Role of Novel Rat-specific Fc Receptor in Macrophage Activation Associated with Crescentic Glomerulonephritis

Page, T. H., D’Souza, Z., Nakanishi, S., Serikawa, T., Pusey, C. D., Aitman, T. J., Cook, H. T., & Behmoaras, J. V. (2011) · Journal of Biological Chemistry · doi:10.1074/jbc.m111.260695 · Cited by 9

Terapia gênica em distrofias hereditárias de retina

Côco, M., Han, S. W., & Sallum, J. M. F. (2009) · Arquivos Brasileiros de Oftalmologia · doi:10.1590/s0004-27492009000400026 · Cited by 9

Detection and Selection of Lentiviral Vector-Transduced Cells

Cui, Y. R., & Chang, L.-J. (2003) · Humana Press eBooks · doi:10.1385/1-59259-393-3:69 · Cited by 8

Concepts in Genetic Medicine

(2007) · Wiley eBooks · doi:10.1002/9780470184585 · Cited by 8

Mouse Models of Human Retinal Disease Caused by Expression of Mutant Rhodopsin

Nour, M., & Naash, M. I. (2003) · Advances in experimental medicine and biology · doi:10.1007/978-1-4615-0067-4_22 · Cited by 8

Lentiviral delivered aflibercept OXB-203 for treatment of neovascular AMD

Iqball, S., Beck, D. K., Devarajan, G., Khoo, C. P., O’Connor, D. M., Ellis, S., Guzman, E., Mitrophanous, K. A., & Lad, Y. (2023) · Molecular Therapy — Methods & Clinical Development · doi:10.1016/j.omtm.2023.07.001 · Cited by 6

Delocalized quinolinium-macrocyclic peptides, an atypical chemotype for CNS penetration

Pingitore, V., Pancholi, J., Hornsby, T. W., Warne, J. M., Pryce, G., McCormick, L. J., Hill, J. M., Bhosale, G., Peng, J., Newton, L. S., et al. (2024) · Science Advances · doi:10.1126/sciadv.ado3501 · Cited by 6

Advances in corneal surgery and cell therapy: challenges and perspectives for eye banks

Ferrari, S., Barbaro, V., Iorio, E. D., Fasolo, A., & Ponzin, D. (2009) · Expert Review of Ophthalmology · doi:10.1586/eop.09.19 · Cited by 6

Temporally controlled targeted somatic mutagenesis in mouse eye pigment epithelium

Mori, M., Gargowitsch, L., Bornert, J., Garnier, J., Mark, M. P., Chambon, P., & METZGER, D. (2012) · genesis · doi:10.1002/dvg.22044 · Cited by 6

Genetic Manipulation of Corneal Endothelial Cells: Transfection and Viral Transduction

Bertelmann, E. (2008) · Methods in molecular biology · doi:10.1007/978-1-59745-241-0_13 · Cited by 6

Lentiviral Vectors for Gene Delivery to the Nervous System

Eleftheriadou, I., & Mazarakis, N. D. (2015) · Neuromethods · doi:10.1007/978-1-4939-2306-9_2 · Cited by 5

The role ofcis-regulatory elements in the design of gene therapy vectors for inherited blindness

Corbo, J. C. (2008) · Expert Opinion on Biological Therapy · doi:10.1517/14712598.8.5.599 · Cited by 5

Inherited Diseases of Photoreceptors and Prospects for Gene Therapy

Montana, C. L., & Corbo, J. C. (2008) · Pharmacogenomics · doi:10.2217/14622416.9.3.335 · Cited by 5

Gene Therapy for Rhodopsin MutationsPreprint

Lewin, A. S., & Smith, W. C. (2022) · Cold Spring Harbor Perspectives in Medicine · doi:10.1101/cshperspect.a041283 · Cited by 6

CXCL12-Targeted Immunomodulatory Gene Therapy Reduces Radiation-Induced Fibrosis in Healthy Tissues

Paget, J. T.-E. H., Ward, J. A., McKean, A. R., Mansfield, D., McLaughlin, M., Kyula, J., Smith, H. G., Roulstone, V., Li, C., Zhou, Y., et al. (2024) · Molecular Cancer Therapeutics · doi:10.1158/1535-7163.mct-23-0872 · Cited by 4

Analysis of SAMHD1 Restriction by Flow Cytometry in Human Myeloid U937 Cells

Ordonez, P., Bishop, K. N., Stoye, J. P., & Groom, H. C. T. (2021) · Journal of Visualized Experiments · doi:10.3791/62502 · Cited by 3

Coevolved Multidrug-Resistant HIV-1 Protease and Reverse Transcriptase Influences Integrase Drug Susceptibility and Replication Fitness

Martin, S. A., Cane, P. A., Pillay, D., & Mbisa, J. L. (2021) · Pathogens · doi:10.3390/pathogens10091070 · Cited by 3

HIV-1-mediated delivery of a short hairpin RNA targeting vascular endothelial growth factor in human retinal pigment epithelium cells

Lombardi, G., Calistri, A., Curtarello, M., Giudice, G. L., Piermarocchi, S., Prosdocimo, G., Palù, G., & Parolin, C. (2009) · British Journal of Ophthalmology · doi:10.1136/bjo.2008.138388 · Cited by 3

Vascular Endothelial Growth Factors In Eye Diseases Pathophysiology and New Therapeutic Strategies for Retinal and Choroideal Angiogenesis

Kinnunen, K. (2009) · Cited by 3

Targeted AAV6 gene therapy restores corneal endothelial function in three hereditary corneal dystrophies

Zhang, B. N., Qi, B., Chen, S., Su, J., Li, G., Wang, X., Ren, Z., Zhang, H., Cheng, J., Qu, J., et al. (2026) · Cell Reports Medicine · doi:10.1016/j.xcrm.2026.102649 · Cited by 2

COVID-19 vaccination induces cross-neutralisation of sarbecoviruses related to SARS-CoV-2

West, G. E., Morse, R. B., Sievers, B. L., Abdullahi, A., Kamelian, K., Cheng, M. T. K., Bradley, J. R., Baker, S., Graves, B., Stark, H., et al. (2026) · npj Vaccines · doi:10.1038/s41541-026-01469-x · Cited by 2

Development of Viral Vectors with Optimal Transgene Expression for Ocular Gene Therapies

Hashimoto, T. (2007) · Advances in experimental medicine and biology · doi:10.1007/978-0-387-74904-4_12 · Cited by 3

Role of HIF1α and HIF2α in Cre Recombinase–Induced Retinal Pigment Epithelium Pathology and Its Secondary Effect on Choroidal Neovascularization

Cristante, E., Liyanage, S. E., Smith, A. J., Ali, R. R., & Bainbridge, J. W. (2023) · American Journal Of Pathology · doi:10.1016/j.ajpath.2023.05.017 · Cited by 2

Macrophage activation of cGAS and TRIM5 distinguish pandemic and non-pandemic HIVPreprint

Zuliani‐Alvarez, L., Govasli, M. L., Rasaiyaah, J., Monit, C., Perry, S. O., Sumner, R. P., McAlpine-Scott, S., Dickson, C. F., Faysal, K. M. R., Hilditch, L., et al. (2022) · bioRxiv (Cold Spring Harbor Laboratory) · doi:10.1101/2022.01.21.477263 · Cited by 2

HIV-1 Vpr causes separate cell cycle arrests in G2 and M that activate alternative DNA damage pathwaysPreprint

Hall, R., Ahern, L. M., Yap, M. W., Tsai, M.-H., Boucherit, V., Takaki, T., Boulton, S. J., & Bishop, K. N. (2024) · bioRxiv (Cold Spring Harbor Laboratory) · doi:10.1101/2024.04.02.587683 · Cited by 2

Mesenchymal and Adipose Stem Cell Strategies for Peripheral Nerve Regeneration

Schweizer, R., Ravuri, S. K., Plock, J. A., Marra, K. G., & Gorantla, V. S. (2015) · Stem cell biology and regenerative medicine · doi:10.1007/978-1-4939-2071-6_20 · Cited by 1

Endothelial Cell Isolation and Manipulation

Brostjan, C. (2019) · Learning materials in biosciences · doi:10.1007/978-3-030-12270-6_14 · Cited by 1

Ocular Gene Therapies

Michalakis, S., Gerhardt, M.-J., Priglinger, C., & Priglinger, S. G. (2021) · Springer eBooks · doi:10.1007/978-3-319-90495-5_150-1 · Cited by 1

Suppression of choroidal neovascularization in mice by subretinal delivery of multigenic lentiviral vectors encoding anti-angiogenic microRNAs

Askou, A. L., Benckendorff, J. N. E., Holmgaard, A., Storm, T., Aagaard, L., Bek, T., Mikkelsen, J. G., & Corydon, T. J. (2017) · Human Gene Therapy Methods · doi:10.1089/hum.2017.079 · Cited by 1

Ocular Gene Therapies

Michalakis, S., Gerhardt, M.-J., Priglinger, C., & Priglinger, S. G. (2022) · Springer eBooks · doi:10.1007/978-3-030-42634-7_150 · Cited by 1

Investigation of mesenchymal stem cells and the development of experimental strategies for rescuing glaucomatous eyes using a stem cell-based therapy

Ye, E. (2013) · doi:10.31274/etd-180810-713 · Cited by 1

Viral‐Mediated Delivery of shRNA and miRNA

Manfredsson, F. P. (2013) · Wiley eBooks · doi:10.1002/9781118610749.ch11 · Cited by 1

Combinations of gene therapy, tissue transplantation and pharmacotherapeutic techniques in visual system repair

Hellström, M. (2010) · UWA Profiles and Research Repository (University of Western Australia) · Cited by 1

Somatic Gene Therapy Using Viral Vectors: Theoretical and Clinical Implications in Relation to Treatment of Genetic Conditions in Humans

Askou, A. L., & Corydon, T. J. (2015) · Springer eBooks · doi:10.1007/978-1-4939-2389-2_3

Viral vector-mediated RNA interference in the retina

Georgiadis, A. (2010) · UCL Discovery (University College London)

Studies of Fv1 binding and restriction

Li, H. L. W. (2015) · UCL Discovery (University College London)

Gene therapy for corneal graft survival

Bárcia, R. N., & Kazlauskas, A. (2007) · Expert Review of Ophthalmology · doi:10.1586/17469899.2.3.409

Construction of lentivirus carrying novel human pancreatic cancer gene S100P and green fluorescent protein gene

Li, G., Jin, G., Zhou, X., Hu, X., Wang, J., & Li, T. (2009) · Academic Journal of Second Military Medical University · doi:10.3724/sp.j.1008.2008.01230

Development of a Ribozyme Gene Therapy Against Herpes Simplex Virus Type I (HSV-1) Infection

Liu, J., Bloom, D. C., Lewin, A. S., Tuli, S. S., Ghivizzani, S. C., & Schultz, G. S. (2007) · Investigative Ophthalmology & Visual Science

Produção de vetores lentivirais baseados em HIV-1 em linhagem de célula tronco mesenquimal murina

da Silva, F. H. (2005) · Americanae (AECID Library)

Reconstitution and Characterization of Human Endogenous Retrovirus-K

Lee, Y. N. (2025) · Digital Commons - RU (Rockefeller University) · doi:10.48496/38w4-yp24

THÉRAPIE GÉNIQUE : INTÉRÊT ET LIMITES DES OUTILS GENE THERAPY: RELEVANCE AND LIMITS OF VECTORS

Mallet, J. J. (2011)

Anti-Angiogenic Gene Therapy: Basic Science and Challenges for Translation into the Clinic

Lange, C., & Bainbridge, J. W. (2016) · Essentials in ophthalmology/Essentials ophthalmology · doi:10.1007/978-3-319-24097-8_11

Characteristics of a Block to Entry via an HIV-2 Envelope, MCRPreprint

Gray, E. R. (2017) · bioRxiv (Cold Spring Harbor Laboratory) · doi:10.1101/177808

Analysis of SAMHD1 Restriction by Flow Cytometry in Human Myeloid U937 Cells

Ordonez, P., Bishop, K. N., Stoye, J. P., & Groom, H. C. T. (2021) · Journal of Visualized Experiments · doi:10.3791/62502-v

Endothelial Cell Isolation and Manipulation

Brostjan, C. (2024) · Learning materials in biosciences · doi:10.1007/978-3-031-64591-4_15

A modified cyclosporine enhances lentivector transduction ex vivo and in vivo by degrading IFITM3

Annett, D., Critchley, B. J., Morling, K. L., Graham, B., Pingitore, V., Whittaker, T. E., Kurdi, N., Warne, J. M., Moula, S. E., León‐Rico, D., et al. (2026) · Molecular Therapy · doi:10.1016/j.ymthe.2026.07.056

Interactions between primate lentiviral capsids and heterologous cellular host factors

Mamede, J. I. (2012) · theses.fr (ABES) · doi:10.70675/e3f4366bzb31fz4382z8f0cz19483f12bfe7

Antagonism of HUSH restriction by lentiviral Vpx and Vpr proteins

Chougui, G. (2018) · theses.fr (ABES) · doi:10.70675/a8f60021z4ac1z485az94c1za6a503874720

A genome-wide CRISPR/Cas9 knock-out screen identifies the DEAD box RNA helicase DDX42 as a broad viral inhibitor

Bonaventure, B. (2020) · theses.fr (ABES) · doi:10.70675/768c3190z3177z4b25z88b9z9a029e425462

Rethinking nonsense suppression therapies in inherited retinal diseases

Ren, C., Hu, C., Hu, M., Yang, Y., & Lu, F. (2026) · Trends in Molecular Medicine · doi:10.1016/j.molmed.2026.09.017

Site-Specific Ocular Nucleic Acid Delivery

Shukla, R., & Cheng, K. (2013) · Advances in delivery science and technology · doi:10.1007/978-1-4614-9434-8_11

Lentiviral–Vector Mediated Expression of Murine IL–1 Receptor Antagonist Reduces the Severity of Endotoxin–Induced Uveitis

Trittibach, P. C., Barker, S. E., Broderick, C. A., Georgiadis, A., Durán, Y., Smith, A. J., & Ali, R. R. (2006) · Investigative Ophthalmology & Visual Science

Stable and efficient gene transfer into the retina using an HIV-based lentiviral vector

Miyoshi, H., Takahashi, M., Gage, F. H., & Verma, I. M. (1997) · Proceedings of the National Academy of Sciences · doi:10.1073/pnas.94.19.10319 · Cited by 497

Lentivirus-mediated gene transfer to the rat, ovine and human cornea

Parker, D. G., Kaufmann, C., Brereton, H. M., Anson, D. S., Francis-Staite, L., Jessup, C. F., Marshall, K., Tan, C., Koldej, R. M., Coster, D. J., et al. (2007) · Gene Therapy · doi:10.1038/sj.gt.3302921 · Cited by 35

Sustained Transduction of Ocular Cells with a Bovine Immunodeficiency Viral Vector

Takahashi, K., Luo, T., Saishin, Y., Saishin, Y., Sung, J., Hackett, S. F., Brazzell, R. K., Kaleko, M., & Campochiaro, P. A. (2002) · Human Gene Therapy · doi:10.1089/104303402760128531 · Cited by 40

Efficient and sustained transgene expression in human corneal cells mediated by a lentiviral vector

Wang, X.-Y., Appukuttan, B., Ott, S. H., Patel, R. J., Irvine, J. A., Song, J., Park, J.-H. C., Smith, R. R., & Stout, J. T. (2000) · Gene Therapy · doi:10.1038/sj.gt.3301075 · Cited by 94

New strategy for in vivo transgene expression in corneal epithelial progenitor cells

Igarashi, T., Miyake, K., Suzuki, N., Kato, K., Takahashi, H., Ohara, K., & Shimada, T. (2002) · Current Eye Research · doi:10.1076/ceyr.24.1.46.5436 · Cited by 19