In vivo gene transfer to the mouse eye using an HIV-based lentiviral vector; efficient long-term transduction of corneal endothelium and retinal pigment epithelium

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A comprehensive review of retinal gene therapy

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Regulation of PCNA and Cyclin D1 Expression and Epithelial Morphogenesis by the ZO-1-Regulated Transcription Factor ZONAB/DbpA

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Vector platforms for gene therapy of inherited retinopathies

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Mutation of a Single Residue Renders Human Tetherin Resistant to HIV-1 Vpu-Mediated Depletion

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Inhibiting primary effusion lymphoma by lentiviral vectors encoding short hairpin RNA

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Gene therapy progress and prospects: the eye

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All Three Variable Regions of the TRIM5α B30.2 Domain Can Contribute to the Specificity of Retrovirus Restriction

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The Tight Junction Associated Signalling Proteins ZO-1 and ZONAB Regulate Retinal Pigment Epithelium Homeostasis in Mice

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Structural basis of lentiviral subversion of a cellular protein degradation pathway

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Antiretroviral potential of human tripartite motif-5 and related proteins

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Long-term preservation of retinal function in the RCS rat model of retinitis pigmentosa following lentivirus-mediated gene therapy

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Gene delivery to mitotic and postmitotic photoreceptors Via compacted DNA nanoparticles results in improved phenotype in a mouse model of retinitis pigmentosa

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Lentiviral Gene Transfer of Rpe65 Rescues Survival and Function of Cones in a Mouse Model of Leber Congenital Amaurosis

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Gene therapy and transplantation in CNS repair: The visual system

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Phospho-dependent Regulation of SAMHD1 Oligomerisation Couples Catalysis and Restriction

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Ocular gene delivery using lentiviral vectors

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Selective Inhibition of the Mitochondrial Permeability Transition Pore Protects against Neurodegeneration in Experimental Multiple Sclerosis

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Hypermutation of an Ancient Human Retrovirus by APOBEC3G

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Gene therapy in the cornea

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HIV-1 capsid uncoating initiates after the first strand transfer of reverse transcription

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Corneal gene therapy

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Five Recombinant Simian Immunodeficiency Virus Pseudotypes Lead to Exclusive Transduction of Retinal Pigmented Epithelium in Rat

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Effect of Disrupting Seven-in-Absentia Homolog 2 Function on Lung Cancer Cell Growth

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Recent developments in ocular gene therapy

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An Active TRIM5 Protein in Rabbits Indicates a Common Antiviral Ancestor for Mammalian TRIM5 Proteins

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Inhibition of RAS-Mediated Transformation and Tumorigenesis by Targeting the Downstream E3 Ubiquitin Ligase Seven in Absentia Homologue

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Lentiviral vector-mediated gene transfer in adult mouse photoreceptors is impaired by the presence of a physical barrier

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Third-generation lentivirus vectors efficiently transduce and phenotypically modify vascular cells: implications for gene therapy

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Feline Tetherin Efficiently Restricts Release of Feline Immunodeficiency Virus but Not Spreading of Infection

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Corneal Gene Therapy: Basic Science and Translational Perspective

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Evasion of cGAS and TRIM5 defines pandemic HIV

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Gene supplementation therapy for recessive forms of inherited retinal dystrophies

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Truncation of TRIM5 in the Feliformia Explains the Absence of Retroviral Restriction in Cells of the Domestic Cat

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Retinal Ganglion Cell Gene Therapy and Visual System Repair

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EIAV vector-mediated delivery of endostatin or angiostatin inhibits angiogenesis and vascular hyperpermeability in experimental CNV

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The design of artificial retroviral restriction factors

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Novel insights into gene therapy in the cornea

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Retinal transduction profiles by high-capacity viral vectors

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Lentiviral Vector Integration Profiles Differ in Rodent Postmitotic Tissues

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Lentiviral-vector-mediated expression of murine IL-1 receptor antagonist or IL-10 reduces the severity of endotoxin-induced uveitis

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Immune responses to gene editing by viral and non-viral delivery vectors used in retinal gene therapy

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Challenges and strategies for the delivery of biologics to the cornea

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Prospects for gene therapy in corneal disease

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Gene-based antiangiogenic applications for corneal neovascularization

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Conformational Adaptation of Asian Macaque TRIMCyp Directs Lineage Specific Antiviral Activity

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Gene Therapy of Inherited Retinopathies: A Long and Successful Road from Viral Vectors to Patients

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Retinal cell type expression specificity of HIV-1-derived gene transfer vectors upon subretinal injection in the adult rat: influence of pseudotyping and promoter

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Gene therapy for ocular angiogenesis

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Promising and delivering gene therapies for vision loss

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HIV-1 requires capsid remodelling at the nuclear pore for nuclear entry and integration

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SARS-CoV-2 ORF6 disrupts innate immune signalling by inhibiting cellular mRNA export

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Early Antigen Presentation of Protective HIV-1 KF11Gag and KK10Gag Epitopes from Incoming Viral Particles Facilitates Rapid Recognition of Infected Cells by Specific CD8+T Cells

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Gene Therapy of Inherited Retinal Degenerations: Prospects and Challenges

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Comparison of HIV-1 and EIAV-based lentiviral vectors in corneal transduction

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Genetic manipulation for inherited neurodegenerative diseases: myth or reality?

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