PreprintCited by 18Genomics and Rare DiseasesCancer Genomics and DiagnosticsGenetic Associations and Epidemiology

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PRESCOTT: a population aware, epistatic and structural model accurately predicts missense effect

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Preprint — published as 10.1186/s13059-025-03581-y · Paper page

Abstract

Predicting the functional impact of point mutations is a complex yet vital task in genomics. PRESCOTT stands at the forefront of this challenge and reconstructs complete mutational landscapes of proteins, enables the identification of protein regions most vulnerable to mutations and assigns scores to individual mutations, assisting pathologists in evaluating the pathogenic potential of missense variants. PRESCOTT categorizes these variants into three distinct classes: Benign, Pathogenic, or Variants of Uncertain Significance (VUS). The model leverages protein sequences across millions of species, advanced protein structural models, and extensive genomic and exomic data from diverse human populations. By using only sequence and structural information, it significantly improves on current standards for predicting mutations in human proteins and matches AlphaMissense performance, which incorporates allele frequency data in its analysis. By including population-specific allele frequencies, PRESCOTT excels in genome-scale score separation of ClinVar benign and pathogenic variants and surpasses AlphaMissense in analyzing the ACMG reference human dataset and the over 1800 proteins from the Human Protein Dataset. Its efficacy is particularly notable in autoinflammatory diseases, accurately predicting pathogenic gain-of-function missense mutations, a task known for its difficulty. Efficiency and accessibility are key aspects of PRESCOTT. The user-friendly PRESCOTT webserver facilitates mutation effect calculations on any protein and protein variants. The server hosts a Comprehensive Human Protein Database for over 19,000 human proteins, based on sequences and structures, ready for a customized allele population analysis. Additionally, the tool provides open access to all intermediate scores, ensuring interpretability and transparency in variant analysis. PRESCOTT is a significant stride forward in the field of genomic medicine, offering unparalleled insights into protein mutational impacts.

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Metadata

Authors
Tekpinar, M., David, L., Henry, T., & Carbone, A.
Affiliations
  • Centre National de la Recherche Scientifique (FR)
  • Lyon 1 Université (FR)
Corresponding author
Carbone, Alessandra
Venue
Genome biology
Publisher
openRxiv
Published
2024-02-06
Volume
26
Issue
1
Pages
113-113
ISSN
1465-6906 (ISSN-L)
OpenAlex
W4410130203
Cited by
18
References
1
Citations by year
2026: 9 · 2025: 6 · 2024: 2
FWCI
8.77
Type
journal article
Language
en
Open access
Licence
cc-by
Locations
  • Genome biology (publishedVersion, cc-by)
  • medRxiv (acceptedVersion, cc-by-nc-nd)
  • Europe PMC (PubMed Central) (publishedVersion, cc-by)
  • PubMed Central (publishedVersion, cc-by)
  • PubMed (publishedVersion)
  • HAL (submittedVersion, cc-by)
  • DOAJ (DOAJ: Directory of Open Access Journals) (submittedVersion, cc-by-sa)
Funders
  • Agence Nationale de la Recherche (ANR-21-CE17-0046)
  • Grand Équipement National De Calcul Intensif
Topics
  • Life Sciences › Biochemistry, Genetics and Molecular Biology › Genetics › Genomics and Rare Diseases
  • Life Sciences › Biochemistry, Genetics and Molecular Biology › Cancer Research › Cancer Genomics and Diagnostics
  • Life Sciences › Biochemistry, Genetics and Molecular Biology › Genetics › Genetic Associations and Epidemiology
Keywords
point mutations, protein structure, epistasis, population allele frequencies, ClinVar variants, ACMG criteria, variants of uncertain significance, protein sequence analysis, online prediction server
MeSH terms
Epistasis, Genetic, Gene Frequency, Humans, Proteins, Software, Mutation, Missense

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